sirolimus has been researched along with Thalassemia* in 1 studies
1 other study(ies) available for sirolimus and Thalassemia
Article | Year |
---|---|
Co-Treatment of Erythroid Cells from β-Thalassemia Patients with CRISPR-Cas9-Based β
Gene editing (GE) is an efficient strategy for correcting genetic mutations in monogenic hereditary diseases, including β-thalassemia. We have elsewhere reported that CRISPR-Cas9-based gene editing can be employed for the efficient correction of the β Topics: Adult; beta-Thalassemia; CRISPR-Cas Systems; Erythroid Cells; Fetal Hemoglobin; Gene Editing; Humans; Sirolimus; Thalassemia | 2022 |