Page last updated: 2024-08-21

pyrazines and Adult Spinal Muscular Atrophy

pyrazines has been researched along with Adult Spinal Muscular Atrophy in 1 studies

Research

Studies (1)

TimeframeStudies, this research(%)All Research%
pre-19900 (0.00)18.7374
1990's0 (0.00)18.2507
2000's0 (0.00)29.6817
2010's1 (100.00)24.3611
2020's0 (0.00)2.80

Authors

AuthorsStudies
Birkhoff, W; Bugawan, T; Czech, C; Dziadek, S; Fischer, D; Gerlach, I; Groeneveld, GJ; Günther, A; Heinig, K; Heuberger, J; Khwaja, O; Kinch, R; Kletzl, H; Lochmüller, H; Marquet, A; Mercuri, E; Tang, W; Wood, C1

Trials

1 trial(s) available for pyrazines and Adult Spinal Muscular Atrophy

ArticleYear
The oral splicing modifier RG7800 increases full length survival of motor neuron 2 mRNA and survival of motor neuron protein: Results from trials in healthy adults and patients with spinal muscular atrophy.
    Neuromuscular disorders : NMD, 2019, Volume: 29, Issue:1

    Topics: Administration, Oral; Adolescent; Adult; Alternative Splicing; Child; Child, Preschool; Double-Blind Method; Female; Humans; Infant; Male; Middle Aged; Muscular Atrophy, Spinal; Neuromuscular Agents; Pyrazines; Pyrimidines; RNA, Messenger; Survival of Motor Neuron 2 Protein; Young Adult

2019