nusinersen and Neuronal-Ceroid-Lipofuscinoses

nusinersen has been researched along with Neuronal-Ceroid-Lipofuscinoses* in 1 studies

Other Studies

1 other study(ies) available for nusinersen and Neuronal-Ceroid-Lipofuscinoses

ArticleYear
News Feature: Gene therapy successes point to better therapies.
    Proceedings of the National Academy of Sciences of the United States of America, 2019, 11-26, Volume: 116, Issue:48

    Topics: Genetic Diseases, Inborn; Genetic Therapy; Humans; Muscular Atrophy, Spinal; Neuronal Ceroid-Lipofuscinoses; Oligonucleotides; Oligonucleotides, Antisense; United States; United States Food and Drug Administration

2019