nusinersen has been researched along with Infant--Newborn--Diseases* in 1 studies
1 other study(ies) available for nusinersen and Infant--Newborn--Diseases
Article | Year |
---|---|
Gene therapy rescues newborns with spinal muscular atrophy.
Topics: Drug Approval; Genetic Therapy; Humans; Infant, Newborn; Infant, Newborn, Diseases; Muscular Atrophy, Spinal; Neonatal Screening; Oligonucleotides; United States; United States Food and Drug Administration | 2018 |