nusinersen has been researched along with Genetic-Diseases--Inborn* in 1 studies
1 other study(ies) available for nusinersen and Genetic-Diseases--Inborn
Article | Year |
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News Feature: Gene therapy successes point to better therapies.
Topics: Genetic Diseases, Inborn; Genetic Therapy; Humans; Muscular Atrophy, Spinal; Neuronal Ceroid-Lipofuscinoses; Oligonucleotides; Oligonucleotides, Antisense; United States; United States Food and Drug Administration | 2019 |