Page last updated: 2024-08-23

miglustat and Mucopolysaccharidosis III

miglustat has been researched along with Mucopolysaccharidosis III in 3 studies

Research

Studies (3)

TimeframeStudies, this research(%)All Research%
pre-19900 (0.00)18.7374
1990's0 (0.00)18.2507
2000's1 (33.33)29.6817
2010's2 (66.67)24.3611
2020's0 (0.00)2.80

Authors

AuthorsStudies
Byers, S; Derrick-Roberts, A; Fletcher, J; Kaidonis, X; Ranieri, E; Sharp, P1
Bin-Dorel, S; Decullier, E; Fouilhoux, A; Guffon, N; Guitton, J; Paillet, C1
Jakóbkiewicz-Banecka, J; Wegrzyn, A; Wegrzyn, G1

Reviews

1 review(s) available for miglustat and Mucopolysaccharidosis III

ArticleYear
Substrate deprivation therapy: a new hope for patients suffering from neuronopathic forms of inherited lysosomal storage diseases.
    Journal of applied genetics, 2007, Volume: 48, Issue:4

    Topics: 1-Deoxynojirimycin; Animals; Enzyme Inhibitors; Gaucher Disease; Genistein; Humans; Lysosomal Storage Diseases; Lysosomes; Mucopolysaccharidosis III; Niemann-Pick Diseases; Sandhoff Disease; Tay-Sachs Disease

2007

Trials

1 trial(s) available for miglustat and Mucopolysaccharidosis III

ArticleYear
Evaluation of miglustat treatment in patients with type III mucopolysaccharidosis: a randomized, double-blind, placebo-controlled study.
    The Journal of pediatrics, 2011, Volume: 159, Issue:5

    Topics: 1-Deoxynojirimycin; alpha-Glucosidases; Brain; Child; Child, Preschool; Cognition; Double-Blind Method; Enzyme Inhibitors; Female; Glycoside Hydrolase Inhibitors; Humans; Magnetic Resonance Imaging; Male; Mucopolysaccharidosis III; Neuropsychological Tests; Sleep Wake Disorders

2011

Other Studies

1 other study(ies) available for miglustat and Mucopolysaccharidosis III

ArticleYear
N-butyldeoxynojirimycin treatment restores the innate fear response and improves learning in mucopolysaccharidosis IIIA mice.
    Molecular genetics and metabolism, 2016, Volume: 118, Issue:2

    Topics: 1-Deoxynojirimycin; Analysis of Variance; Animals; Brain; Chemokine CCL3; Disease Models, Animal; Fear; Gangliosides; Glucosyltransferases; Glycoside Hydrolase Inhibitors; Interleukin-1beta; Maze Learning; Mice; Mucopolysaccharidosis III

2016