miglustat has been researched along with Classical Niemann-Pick Disease in 2 studies
Timeframe | Studies, this research(%) | All Research% |
---|---|---|
pre-1990 | 0 (0.00) | 18.7374 |
1990's | 0 (0.00) | 18.2507 |
2000's | 0 (0.00) | 29.6817 |
2010's | 1 (50.00) | 24.3611 |
2020's | 1 (50.00) | 2.80 |
Authors | Studies |
---|---|
Agrawal, N; Berry-Kravis, E; Bianconi, S; Bielekova, B; Do, AD; Farhat, NY; Masvekar, R; Porter, FD; Sinaii, N; Solomon, B; Xiao, C | 1 |
Döme, P; Faludi, G; Gonda, X | 1 |
1 review(s) available for miglustat and Classical Niemann-Pick Disease
Article | Year |
---|---|
[Adult psychiatric aspects of Niemann-Pick disease].
Topics: 1-Deoxynojirimycin; Age of Onset; Cataplexy; Cognition Disorders; Enzyme Inhibitors; Humans; Niemann-Pick Disease, Type A; Niemann-Pick Disease, Type B; Niemann-Pick Disease, Type C; Niemann-Pick Diseases; Sphingolipids; Sphingomyelin Phosphodiesterase | 2013 |
1 other study(ies) available for miglustat and Classical Niemann-Pick Disease
Article | Year |
---|---|
Neurofilament light chain in cerebrospinal fluid as a novel biomarker in evaluating both clinical severity and therapeutic response in Niemann-Pick disease type C1.
Topics: 2-Hydroxypropyl-beta-cyclodextrin; Biomarkers; Cross-Sectional Studies; Humans; Intermediate Filaments; Niemann-Pick Disease, Type A; Niemann-Pick Disease, Type C | 2023 |