Page last updated: 2024-09-05

deflazacort and Becker Muscular Dystrophy

deflazacort has been researched along with Becker Muscular Dystrophy in 82 studies

Research

Studies (82)

TimeframeStudies, this research(%)All Research%
pre-19900 (0.00)18.7374
1990's0 (0.00)18.2507
2000's22 (26.83)29.6817
2010's49 (59.76)24.3611
2020's11 (13.41)2.80

Authors

AuthorsStudies
Akour, A; Al-Tammemi, AB; AlMuhaissen, SA; Alrawashdeh, MN; An, H; Anastasia, L; Apkon, S; Armstrong, WS; Ayala Izurieta, JE; Barnett, K; Bhowmick, S; Biniskos, N; Booka, E; Brown, JC; Buchanan, SW; Campbell, C; Camporeale, A; Cantos, VD; Cao, Z; Chakraborty, RD; Chaturvedi, V; Chen, C; Chen, G; Chen, Y; Chou, PT; Ciconte, G; Colasanti, JA; Collins, LF; Darras, BT; de Carvalho, RM; De Morais, DC; Delegido, J; Dodd, J; Doki, Y; Dunfield, K; Elfring, G; Feng, B; Ferry, VE; Galaviz, KI; García, VJ; Greven, M; Guo, J; Gutierrez, M; Hameed, S; Hippler, M; Huang, JW; Isaac, ME; Ishihara, R; Ishikawa, H; Ito, Y; Jacobson, A; Jalouqa, S; James, TD; Jara Santillán, CA; Jiang, K; Jordan, R; Kampf, JW; Kato, H; Kato, K; Katzmarzyk, PT; Kaviani, A; Kawachi, H; Kawakubo, H; Khansari Nejad, N; Kitagawa, Y; Kojima, T; Kono, K; Koplowitz, B; Kubo, Y; Kuribayashi, S; Lahiri, CD; Lei, H; Leighton, C; Li, J; Liu, G; Lombardi, M; Lu, Y; Luo, Y; Ma, P; Mafa-Attoye, T; Mahmoud, NN; Makhlina, M; Makino, T; Manguso, F; Mano, M; Manso, AP; Marconi, VC; Márquez, CO; Matsubara, H; Matsuda, S; McDonald, CM; Mecarocci, V; Metcalfe, GD; Micaglio, E; Miele, L; Mire, EF; Miyazaki, T; Moi, CT; Moore, CM; Moran, CA; Muto, M; Nemoto, K; Nguyen, ML; Nusair, MB; Ochoa, A; Owen, G; Oyama, T; Palma-Dibb, RG; Pappone, C; Parsons, JA; Pasqualotto, N; Peltz, SW; Pesco Koplowitz, L; Pica, S; Postiglione, WM; Qureshi, M; Rhodes, J; Saeki, H; Sakai, M; Santinelli, V; Santos, C; Shah, NS; Shanahan, JP; Shieh, PB; Sisti, JM; Smith, TW; Sohda, M; Song, Y; Spana, C; Sturla, F; Su, BK; Sumitani, J; Szabo, B; Szymczak, NK; Tabiś, W; Takeuchi, H; Tang, X; Thevathasan, NV; Toh, Y; Tondi, L; Trifillis, P; Tsushima, T; Van Wittenberghe, S; Vicedomini, G; Wang, H; Wang, K; Wang, S; Wang, W; Wang, X; Wang, Y; Wu, F; Wu, X; Yamaji, T; Yamamoto, K; Yamatsuji, T; Yang, L; Yang, S; Yang, WH; Yang, Y; Yoshida, M; Yu, B; Yuan, L; Zabaleta, J; Zhang, C; Zhang, H; Zhang, L; Zhang, X; Zhang, Z; Zheng, WQ; Zheng, YX; Zhou, H; Zhou, J; Zhou, N; Zhu, W1
Bhattacharjee, S; Kumar, A; Patil, AN; Reddy, C; Sahu, JK; Saini, AG; Sankhyan, N; Saxena, S; Sirari, T; Suthar, R1
Cook, T; Miller, H; Wong, BL1
Biggar, WD; McDonald, CM; Skalsky, A1
Cox, DA; Darras, BT; Elfring, G; Landry, J; McDonald, CM; McDonnell, E; Peltz, SW; Sajeev, G; Shieh, PB; Signorovitch, J; Souza, M; Yao, Z1
Thangarajh, M1
Freimark, J; Marden, JR; Signorovitch, J; Tian, C; Wong, BL; Yao, Z1
Bach, JR; Brahmsteadt, AE; Cespedes, L; Pierucci, P; Pishdad, R1
Agboola, F; Fluetsch, N; Lin, GA; Pearson, SD; Rind, DM; Walton, SM1
Brandsema, JF1
Belosludtsev, KN; Belosludtseva, NV; Dubinin, MV; Starinets, VS; Talanov, EY; Tenkov, KS1
Cecconi, I; Cordelli, DM; Dormi, A; Merlini, L; Parmeggiani, A1
Baranello, G; Barohn, RJ; Brown, MW; Bryan Burnette, W; Bushby, K; Butterfield, RJ; Campbell, C; Childs, AM; Ciafaloni, E; Darras, BT; Eagle, M; Finkel, RS; Flanigan, KM; Griggs, RC; Guglieri, M; Hart, KA; Herr, BE; Hirtz, D; Horrocks, I; Howard, JF; Hughes, I; King, WM; Kirschner, J; Kuntz, NL; Mah, JK; Manzur, AY; Martens, WB; McColl, E; McDermott, MP; McDonald, CM; McMillan, HJ; Mongini, T; Morrison, L; Pegoraro, E; Roper, H; Schara, U; Shieh, PB; Spinty, S; Straub, V; Tawil, R; Thangarajh, M; Vita, G; von der Hagen, M; Wicklund, M; Wilichowski, E; Wilkinson, J; Willis, T1
Aschenbrenner, DS1
Hayes, A; Rybalka, E; Timpani, CA1
Illum, NO; Jensen, L; Jørgensen, LH; Laugaard-Jacobsen, HC; Petersson, SJ; Schrøder, HD; Thelle, T1
Glemser, PA; Jaeger, H; Jurkat-Rott, K; Lehmann-Horn, F; Nagel, AM; Schlemmer, HP; Simons, D; Weber, MA; Ziegler, AE1
Giannakopoulou, A; Karanasios, E; Kolovou, G; Markousis-Mavrogenis, G; Mavrogeni, S; Noutsias, M; Papadopoulos, G; Papavasiliou, A; Pons, R1
Marques, MJ; Mauricio, AF; Neto, HS; Pereira, JA1
Chrzanowski, SM; Poudyal, R1
de Carvalho, SC; Marques, MJ; Matsumura, CY; Santo Neto, H1
Horn, PS; Rice, ML; Wong, B; Yang, MB1
Darras, BT; Elfring, G; Jin, F; Mcdonald, CM; Mcintosh, J; Narayanan, S; Peltz, SW; Shieh, PB; Souza, M; Trifillis, P1
Abutaleb, ARA; Anderson, AS; Carr, JC; Khan, SS; McNally, EM; Wilcox, JE1
Ahmed, SF; Bushby, K; Guglieri, M; Horrocks, I; Joseph, S; Straub, V; Wang, C; Wong, SC1
Amaddeo, A; Amin, R; Burrows, C; Darmahkasih, A; Fauroux, B; Gurbani, N; Horn, PS; Khirani, S; Pascoe, J; Rutter, MM; Rybalsky, I; Sawnani, H; Shellenbarger, KC; Simakajornboon, N; Tian, C; Wong, B1
Mayer, OH1
Flanigan, KM; Waldrop, MA1
Alman, BA; Biggar, WD; Corston, JA; Lebel, DE; McAdam, LC1
Bridwell, KH; Connolly, AM; Kim, HJ1
Bobbitt, SA; Cummings, EA; Dooley, JM1
Campbell, K; Flanigan, KM; Gomez, AM; Mendell, JR; Viollet, L; Walker, CM; Wang, W1
Apolinário, LM; Carvalho, SC; Marques, MJ; Matheus, SM; Santo Neto, H1
Campbell, KA; Fox, DJ; Kim, S; Matthews, DJ; Valdez, R1
Benson, DW; Fleck, RJ; Gao, Z; Hor, KN; Jefferies, JL; Mazur, W; Sticka, JJ; Tandon, A; Taylor, MD; Towbin, JA; Villa, CR; Wong, BL1
Marques, MJ; Pereira, JA; Santo Neto, H1
Bello, L; Cnaan, A; Duong, T; Gordish-Dressman, H; Henricson, EK; Hoffman, EP; McDonald, CM; Morgenroth, LP1
Ashwal, S; Gloss, D; Moxley, RT; Oskoui, M1
Ciafaloni, E; DiGuiseppi, C; James, K; Lamb, MM; Ouyang, L; Pandya, S; Weitzenkamp, D; West, NA; Yang, M1
Brassington, R; Jichi, F; Kuntzer, T; Manzur, AY; Matthews, E1
Reilly, CW; Schaeffer, EK; Singh, A1
Goldstein, SL; Jefferies, JL; Kaddourah, A; Mathew, J; Ryan, TD; Villa, CR; Wong, BL1
Cwik, V; Dubow, JS; Fehlings, DL; Florence, JM; Greenberg, CR; Griggs, RC; King, W; Kissel, JT; Mendell, JR; Meyer, JM; Miller, JP; Moxley, RT; Pandya, S; Pestronk, A; Vanasse, M1
Jefferies, JL; McMahon, MA; Rutter, MM; Rybalsky, I; Sawnani, H; Shellenbarger, KC; Tian, C; Wong, BL1
Ander, BP; Apperson, M; Liao, I; Lit, L; Liu, DZ; Sharp, FR; Walker, WL; Wong, B; Xu, H1
Campbell, K; Ciafaloni, E; Fox, DJ; Moxley, RT; Pandya, S1
Carvalho, MS; Marie, SK; Parreira, SL; Reed, UC; Resende, MB; Zanoteli, E1
Dooley, JM; Esser, MJ; Gordon, KE; MacSween, J; Sheppard, KM1
Battini, R; Bello, L; Berardinelli, A; Bertini, E; Bianco, F; Bonfiglio, S; Bruno, C; Cavallaro, F; Comi, G; D'Amico, A; De Sanctis, R; Doglio, L; Donati, MA; Frosini, S; Gasperini, S; Martinelli, D; Mazzone, E; Mercuri, E; Messina, S; Mongini, T; Motta, MC; Napolitano, S; Pane, M; Pegoraro, E; Pini, A; Politano, L; Previtali, S; Rossi, F; Sacco, A; Scutifero, M; Sormani, MP; Torrente, Y; Vasco, G; Vita, G; Zucchini, E1
Machado, DL; Reed, UC; Resende, MB; Silva, EC; Silva, RF; Zanoteli, E1
Armaroli, A; Cecconi, I; Cicognani, A; Ferlini, A; Franzoni, E; Gennari, M; Gnudi, S; Malaspina, E; Merlini, L; Talim, B1
Beytía, Mde L; Kirschner, J; Vry, J1
Alman, BA; Biggar, WD; Mayo, AL; McAdam, LC1
Angelini, C; Peterle, E1
Biggar, WD; Craven, BC; Mayo, AL; McAdam, LC1
Carvalho, CR; Machado, DL; Reed, UC; Resende, MB; Silva, EC; Zanoteli, E1
Collins, J; Cripe, LH; Hor, KN; Rose, SR; Rutter, MM; Sawnani, H; Sucharew, H; Wong, BL; Woo, JG1
Cripe, L; King, E; Kinnett, K; Pratt, J; Sage, J; Spicer, R; Uzark, K; Varni, JW; Wong, B1
Bushby, K; Connor, EM; Damsker, J; Hoffman, EP; McCall, JM; Nagaraju, K; Reeves, E1
Battini, R; Bello, L; Berardinelli, A; Bertini, E; Bianco, F; Bonfiglio, S; Bruno, C; Cavallaro, F; Comi, GP; D'Ambrosio, P; D'Amico, A; De Sanctis, R; Doglio, L; Donati, MA; Frosini, S; Magri, F; Mazzone, ES; Mercuri, E; Messina, S; Mongini, T; Motta, MC; Napolitano, S; Pane, M; Pegoraro, E; Pini, A; Politano, L; Previtali, S; Rolle, E; Rossi, F; Sacchini, M; Scalise, R; Sormani, MP; Torrente, Y; Vasco, G; Viggiano, E; Vita, G1
Biggar, DW; Harris, VA; Silversides, CK; Webb, GD1
Campbell, C; Jacob, P1
Alman, BA; Biggar, WD; Raza, SN1
Kuntzer, T; Manzur, AY; Pike, M; Swan, A1
Biggar, D; Doherty, TJ; Mahoney, DJ; Rodriguez, C; Roy, BD; Tarnopolsky, MA; Vajsar, J1
Alman, B; Biggar, WD; Comi, LI; Harris, VA; Nigro, G; Palladino, A; Passamano, L; Politano, L; Vajsar, J1
Chakkalakal, JV; Jasmin, BJ; Knudson, JC; Kolodziejczyk, SM; Megeney, LA; St-Pierre, SJ1
Ashwal, S; Baumbach, L; Connolly, A; Florence, J; Mathews, K; McDonald, C; Moxley, RT; Pandya, S; Sussman, M; Wade, C1
Biggar, WD; Chase, CC; Fielding, LJ; Harris, VA; Hawker, GA; Ridout, R1
Balaban, B; Carry, T; Clayton, GH; Matthews, DJ1
Alman, B; Biggar, WD; Eliasoph, L; Harris, VA1
Angelini, C; Bonifati, DM; Ermani, M; Hoffman, EP; Pegoraro, E; Witchel, SF1
Carvalho, MS; Della Corte Peduto, M; Marie, SK; Parreira, SL; Reed, UC; Resende, MB1
Comi, LI; De Luca, F; Nigro, G; Palladino, A; Passamano, L; Politano, L1
Bérubé, D; Brousseau, Y; D'Arcy, S; Dubé, J; Filiatrault, M; Fournier, A; Houde, S; Lapierre, G; Vanasse, M1
Cokkinos, DV; Douskou, M; Kolovou, G; Mavrogeni, S; Papadopoulou, E; Papavasiliou, A1
Angelini, C; Berardinelli, A; Bonifati, MD; Bonometto, P; Gorni, K; Lanzi, G; Orcesi, S; Ruzza, G1
Biggar, WD; Fehlings, DL; Gingras, M; Harris, VA; Steele, CA1
Gnudi, S; Malaguti, C; Merlini, L; Politano, L; Talim, B1
Escolar, DM; Scacheri, CG1
Christopher, C; Wong, BL1

Reviews

20 review(s) available for deflazacort and Becker Muscular Dystrophy

ArticleYear
    Biomaterial investigations in dentistry, 2021, Volume: 8, Issue:1

    Topics: Adult; Alcohol Drinking; Ammonia; Animals; Anti-Inflammatory Agents; Area Under Curve; B-Lymphocytes; Black or African American; Bleaching Agents; Body Mass Index; Brugada Syndrome; Carbon; China; Climate Models; Codon, Nonsense; Cohort Studies; Colitis; Colon; COVID-19; Cytokines; Dental Enamel; Dextran Sulfate; Disease Models, Animal; Disease Outbreaks; Dogs; Electrocardiography; Escherichia coli; Esophageal Neoplasms; Female; Follow-Up Studies; Forests; Georgia; Glucosides; Healthy Volunteers; Heart Ventricles; Hesperidin; HIV Infections; Humans; Humidity; Hydrogen Peroxide; Incidence; Influenza, Human; Longitudinal Studies; Magnetic Resonance Imaging, Cine; Male; Melanocortins; Mice; Mice, Inbred C57BL; Microscopy, Electron, Scanning; Middle Aged; Muscular Dystrophy, Duchenne; Naphthol AS D Esterase; Naphthols; Neoplasms; Nitrates; Nitrites; Nitrous Oxide; Obesity; Pandemics; Patient Outcome Assessment; Patient Satisfaction; Plants; Prednisolone; Prednisone; Pregnenediones; Proportional Hazards Models; Prospective Studies; Pulmonary Disease, Chronic Obstructive; Rats; Receptor, Melanocortin, Type 1; Retrospective Studies; Risk Factors; SARS-CoV-2; Seasons; Soil; Stroke Volume; T-Lymphocytes; Telemedicine; Temperature; Tetralogy of Fallot; Tooth Bleaching; Tooth Bleaching Agents; Trees; Urea; White People

2021
Prednisone and deflazacort in Duchenne muscular dystrophy: a patient perspective and plain language summary publication of the Cincinnati study.
    Journal of comparative effectiveness research, 2022, Volume: 11, Issue:11

    Topics: Child; Humans; Inflammation; Language; Male; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Scoliosis

2022
Comparing Deflazacort and Prednisone in Duchenne Muscular Dystrophy.
    Journal of neuromuscular diseases, 2022, Volume: 9, Issue:4

    Topics: Humans; Muscular Dystrophy, Duchenne; Prednisolone; Prednisone; Pregnenediones; Prospective Studies

2022
Deflazacort vs prednisone treatment for Duchenne muscular dystrophy: A meta-analysis of disease progression rates in recent multicenter clinical trials.
    Muscle & nerve, 2020, Volume: 61, Issue:1

    Topics: Anti-Inflammatory Agents; Child; Disease Progression; Humans; Male; Multicenter Studies as Topic; Muscular Dystrophy, Duchenne; Prednisolone; Prednisone; Pregnenediones; Randomized Controlled Trials as Topic; Treatment Outcome; Walking

2020
The Dystrophinopathies.
    Continuum (Minneapolis, Minn.), 2019, Volume: 25, Issue:6

    Topics: Adrenal Cortex Hormones; Child; Child, Preschool; Humans; Immunologic Factors; Male; Morpholinos; Muscular Dystrophy, Duchenne; Pregnenediones

2019
The Effectiveness and Value of Deflazacort and Exon-Skipping Therapies for the Management of Duchenne Muscular Dystrophy.
    Journal of managed care & specialty pharmacy, 2020, Volume: 26, Issue:4

    Topics: Cost-Benefit Analysis; Dystrophin; Exons; Humans; Immunosuppressive Agents; Models, Economic; Morpholinos; Muscular Dystrophy, Duchenne; Oligonucleotides; Oligonucleotides, Antisense; Prednisone; Pregnenediones; Randomized Controlled Trials as Topic; Treatment Outcome

2020
Evaluating a Stone of Hope: ICER's 2019 Review of Treatments for Duchenne Muscular Dystrophy.
    Journal of managed care & specialty pharmacy, 2020, Volume: 26, Issue:4

    Topics: Cost-Benefit Analysis; Humans; Insurance Coverage; Insurance, Pharmaceutical Services; Morpholinos; Muscular Dystrophy, Duchenne; Oligonucleotides; Pregnenediones; United States; United States Food and Drug Administration

2020
Therapeutic strategies to address neuronal nitric oxide synthase deficiency and the loss of nitric oxide bioavailability in Duchenne Muscular Dystrophy.
    Orphanet journal of rare diseases, 2017, 05-25, Volume: 12, Issue:1

    Topics: Animals; Biological Availability; Clinical Trials as Topic; Drug Therapy, Combination; Humans; Muscular Dystrophy, Duchenne; Nitric Oxide; Nitric Oxide Donors; Nitric Oxide Synthase Type I; Pregnenediones

2017
Pulmonary function and clinical correlation in DMD.
    Paediatric respiratory reviews, 2019, Volume: 30

    Topics: Disease Progression; Glucocorticoids; Humans; Morpholinos; Muscular Dystrophy, Duchenne; Oxadiazoles; Prednisone; Pregnenediones; Respiratory Function Tests; Respiratory Insufficiency

2019
Update in Duchenne and Becker muscular dystrophy.
    Current opinion in neurology, 2019, Volume: 32, Issue:5

    Topics: Adrenal Cortex Hormones; Dystrophin; Exons; Genetic Therapy; Humans; Male; Muscular Dystrophy, Duchenne; Mutation; Prednisone; Pregnenediones

2019
Practice guideline update summary: Corticosteroid treatment of Duchenne muscular dystrophy: Report of the Guideline Development Subcommittee of the American Academy of Neurology.
    Neurology, 2016, Feb-02, Volume: 86, Issue:5

    Topics: Academies and Institutes; Adrenal Cortex Hormones; Humans; Muscular Dystrophy, Duchenne; Neurology; Practice Guidelines as Topic; Pregnenediones; Research Report; Treatment Outcome; United States

2016
Corticosteroids for the treatment of Duchenne muscular dystrophy.
    The Cochrane database of systematic reviews, 2016, May-05, Issue:5

    Topics: Adrenal Cortex Hormones; Glucocorticoids; Humans; Male; Muscle Strength; Muscular Dystrophy, Duchenne; Prednisolone; Prednisone; Pregnenediones; Quality of Life; Randomized Controlled Trials as Topic; Walking

2016
Change in natural history of Duchenne muscular dystrophy with long-term corticosteroid treatment: implications for management.
    Journal of child neurology, 2010, Volume: 25, Issue:9

    Topics: Child; Disease Progression; Drug Administration Schedule; Humans; Male; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Time Factors; Treatment Outcome

2010
Drug treatment of Duchenne muscular dystrophy: available evidence and perspectives.
    Acta myologica : myopathies and cardiomyopathies : official journal of the Mediterranean Society of Myology, 2012, Volume: 31, Issue:1

    Topics: Aminoglycosides; Genetic Therapy; Glucocorticoids; Humans; Immunosuppressive Agents; Muscular Dystrophy, Duchenne; Myostatin; Oxadiazoles; Prednisone; Pregnenediones; Utrophin

2012
Old and new therapeutic developments in steroid treatment in Duchenne muscular dystrophy.
    Acta myologica : myopathies and cardiomyopathies : official journal of the Mediterranean Society of Myology, 2012, Volume: 31, Issue:1

    Topics: Exercise Test; Glucocorticoids; Humans; Immunosuppressive Agents; Muscle Strength; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones

2012
Novel approaches to corticosteroid treatment in Duchenne muscular dystrophy.
    Physical medicine and rehabilitation clinics of North America, 2012, Volume: 23, Issue:4

    Topics: Drug Discovery; Glucocorticoids; Humans; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones

2012
Deflazacort for the treatment of Duchenne Dystrophy: a systematic review.
    BMC neurology, 2003, Sep-08, Volume: 3

    Topics: Adolescent; Anti-Inflammatory Agents; Child; Child, Preschool; Humans; Immunosuppressive Agents; Male; Muscle Contraction; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Randomized Controlled Trials as Topic; Treatment Outcome; Weight Gain

2003
Glucocorticoid corticosteroids for Duchenne muscular dystrophy.
    The Cochrane database of systematic reviews, 2004, Issue:2

    Topics: Adrenal Cortex Hormones; Glucocorticoids; Humans; Male; Muscular Dystrophy, Duchenne; Prednisolone; Prednisone; Pregnenediones; Randomized Controlled Trials as Topic; Walking

2004
Pharmacologic and genetic therapy for childhood muscular dystrophies.
    Current neurology and neuroscience reports, 2001, Volume: 1, Issue:2

    Topics: Animals; Cell Transplantation; Child; Child, Preschool; Clinical Trials as Topic; Creatine; Cytoskeletal Proteins; Drug Administration Schedule; Dystrophin; Female; Gene Expression Regulation; Genetic Therapy; Genetic Vectors; Humans; Male; Membrane Proteins; Mice; Mice, Inbred mdx; Muscle, Skeletal; Muscular Dystrophies; Muscular Dystrophy, Animal; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Protein Biosynthesis; Sarcolemma; Utrophin

2001
Corticosteroids in Duchenne muscular dystrophy: a reappraisal.
    Journal of child neurology, 2002, Volume: 17, Issue:3

    Topics: Adolescent; Anti-Inflammatory Agents; Child; Child, Preschool; Cushing Syndrome; Evidence-Based Medicine; Humans; Male; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Randomized Controlled Trials as Topic

2002

Trials

13 trial(s) available for deflazacort and Becker Muscular Dystrophy

ArticleYear
Deflazacort dose optimization and safety evaluation in Duchenne muscular dystrophy (DOSE): A randomized, double-blind non-inferiority trial.
    European journal of paediatric neurology : EJPN : official journal of the European Paediatric Neurology Society, 2022, Volume: 38

    Topics: Child; Double-Blind Method; Humans; Male; Muscular Dystrophy, Duchenne; Pregnenediones; Treatment Outcome; Walking

2022
Developing standardized corticosteroid treatment for Duchenne muscular dystrophy.
    Contemporary clinical trials, 2017, Volume: 58

    Topics: Child; Child, Preschool; Disability Evaluation; Double-Blind Method; Drug Administration Schedule; Heart Function Tests; Humans; Immunosuppressive Agents; Male; Muscle Strength; Muscular Dystrophy, Duchenne; Patient Satisfaction; Prednisone; Pregnenediones; Range of Motion, Articular; Research Design; Vital Capacity

2017
Muscular response to the first three months of deflazacort treatment in boys with Duchenne muscular dystrophy.
    Journal of musculoskeletal & neuronal interactions, 2017, 06-01, Volume: 17, Issue:2

    Topics: Anti-Inflammatory Agents; Biopsy; Child; Humans; Male; Muscle, Skeletal; Muscular Dystrophy, Duchenne; Pregnenediones; Transcriptome

2017
Deflazacort versus prednisone/prednisolone for maintaining motor function and delaying loss of ambulation: A post HOC analysis from the ACT DMD trial.
    Muscle & nerve, 2018, Volume: 58, Issue:5

    Topics: Adolescent; Age Factors; Anti-Inflammatory Agents; Child; Double-Blind Method; Dystrophin; Female; Humans; Male; Muscular Dystrophy, Duchenne; Prednisolone; Prednisone; Pregnenediones; Walk Test; Walking

2018
Prednisone/prednisolone and deflazacort regimens in the CINRG Duchenne Natural History Study.
    Neurology, 2015, Sep-22, Volume: 85, Issue:12

    Topics: Adolescent; Adult; Anti-Inflammatory Agents; Child; Child, Preschool; Follow-Up Studies; Glucocorticoids; Humans; Internationality; Male; Muscular Dystrophy, Duchenne; Prednisolone; Prednisone; Pregnenediones; Young Adult

2015
Efficacy and safety of deflazacort vs prednisone and placebo for Duchenne muscular dystrophy.
    Neurology, 2016, Nov-15, Volume: 87, Issue:20

    Topics: Adolescent; Anti-Inflammatory Agents; Body Weight; Child; Child, Preschool; Double-Blind Method; Humans; Least-Squares Analysis; Male; Motor Activity; Muscle Strength; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Treatment Outcome

2016
Effects of deflazacort on left ventricular function in patients with Duchenne muscular dystrophy.
    The American journal of cardiology, 2003, Mar-15, Volume: 91, Issue:6

    Topics: Adolescent; Anti-Inflammatory Agents; Child; Cohort Studies; Echocardiography; Electrocardiography; Follow-Up Studies; Humans; Male; Muscle, Skeletal; Muscular Dystrophy, Duchenne; Pregnenediones; Retrospective Studies; Ventricular Dysfunction, Left; Ventricular Function, Left

2003
Steroid treatment and the development of scoliosis in males with duchenne muscular dystrophy.
    The Journal of bone and joint surgery. American volume, 2004, Volume: 86, Issue:3

    Topics: Activities of Daily Living; Adolescent; Anti-Inflammatory Agents; Child; Disease Progression; Follow-Up Studies; Humans; Male; Muscle Weakness; Muscular Dystrophy, Duchenne; Predictive Value of Tests; Pregnenediones; Prevalence; Proportional Hazards Models; Risk Factors; Scoliosis; Spinal Fusion; Survival Analysis; Time Factors; Treatment Outcome; Vital Capacity; Walking

2004
Creatine monohydrate enhances strength and body composition in Duchenne muscular dystrophy.
    Neurology, 2004, May-25, Volume: 62, Issue:10

    Topics: 8-Hydroxy-2'-Deoxyguanosine; Adolescent; Body Composition; Child; Collagen; Collagen Type I; Creatine; Creatinine; Cross-Over Studies; Deoxyguanosine; Drug Therapy, Combination; Hand Strength; Humans; Male; Methylhistidines; Muscle, Skeletal; Muscular Dystrophy, Duchenne; Organ Size; Peptides; Prednisone; Pregnenediones; Respiratory Muscles; Spirometry; Treatment Outcome

2004
Deflazacort in Duchenne muscular dystrophy: a comparison of two different protocols.
    Neuromuscular disorders : NMD, 2004, Volume: 14, Issue:8-9

    Topics: Adolescent; Body Height; Body Weight; Calcium; Case-Control Studies; Cataract; Child; Clinical Protocols; Dietary Supplements; Drug Administration Schedule; Follow-Up Studies; Fractures, Bone; Humans; Immunosuppressive Agents; Male; Motor Activity; Muscular Dystrophy, Duchenne; Pregnenediones; Psychomotor Performance; Scoliosis; Treatment Outcome; Vitamin D

2004
Deflazacort use in Duchenne muscular dystrophy: an 8-year follow-up.
    Pediatric neurology, 2008, Volume: 38, Issue:3

    Topics: Adolescent; Adult; Anti-Inflammatory Agents; Body Height; Body Weight; Bone Density; Cataract; Fractures, Bone; Humans; Longitudinal Studies; Male; Muscular Dystrophy, Duchenne; Pregnenediones; Scoliosis; Treatment Outcome

2008
Effect of deflazacort on cardiac and sternocleidomastoid muscles in Duchenne muscular dystrophy: a magnetic resonance imaging study.
    European journal of paediatric neurology : EJPN : official journal of the European Paediatric Neurology Society, 2009, Volume: 13, Issue:1

    Topics: Adolescent; Anti-Inflammatory Agents; Child; Electrocardiography; Humans; Image Interpretation, Computer-Assisted; Magnetic Resonance Imaging; Male; Muscle, Skeletal; Muscular Dystrophy, Duchenne; Pregnenediones; Prospective Studies; Time Factors; Treatment Outcome; Ventricular Function, Left; Young Adult

2009
A multicenter, double-blind, randomized trial of deflazacort versus prednisone in Duchenne muscular dystrophy.
    Muscle & nerve, 2000, Volume: 23, Issue:9

    Topics: Adolescent; Child; Child, Preschool; Double-Blind Method; Humans; Male; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones

2000

Other Studies

49 other study(ies) available for deflazacort and Becker Muscular Dystrophy

ArticleYear
Real-world outcomes of long-term prednisone and deflazacort use in patients with Duchenne muscular dystrophy: experience at a single, large care center.
    Journal of comparative effectiveness research, 2020, Volume: 9, Issue:3

    Topics: Adolescent; Bone Density; Child; Child, Preschool; Humans; Male; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Retrospective Studies; Stroke Volume; Ventricular Function, Left; Walking

2020
Glucocorticoid-Associated Demise of a Patient With Duchenne Muscular Dystrophy.
    American journal of physical medicine & rehabilitation, 2020, Volume: 99, Issue:12

    Topics: Adult; Anti-Inflammatory Agents; Disease Progression; Drug Administration Schedule; Glucocorticoids; Humans; Long Term Adverse Effects; Male; Muscular Dystrophy, Duchenne; Pregnenediones

2020
The Effect of Deflazacort Treatment on the Functioning of Skeletal Muscle Mitochondria in Duchenne Muscular Dystrophy.
    International journal of molecular sciences, 2020, Nov-19, Volume: 21, Issue:22

    Topics: Adenine Nucleotide Translocator 2; Adenosine Triphosphate; Animals; Calcium; Calcium Channels; Electron Transport Complex III; Electron Transport Complex IV; Gene Expression Regulation; Male; Mice; Mice, Inbred C57BL; Mice, Inbred mdx; Mitochondria, Muscle; Mitochondrial Proton-Translocating ATPases; Muscle, Skeletal; Muscular Dystrophy, Duchenne; Peptidyl-Prolyl Isomerase F; Pregnenediones

2020
Quadriceps muscle strength in Duchenne muscular dystrophy and effect of corticosteroid treatment.
    Acta myologica : myopathies and cardiomyopathies : official journal of the Mediterranean Society of Myology, 2020, Volume: 39, Issue:4

    Topics: Adolescent; Age Factors; Anti-Inflammatory Agents; Child; Child, Preschool; Drug Administration Schedule; Glucocorticoids; Humans; Male; Muscle Strength; Muscle Strength Dynamometer; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Quadriceps Muscle; Walking; Young Adult

2020
New Treatment for Duchenne Muscular Dystrophy.
    The American journal of nursing, 2017, Volume: 117, Issue:6

    Topics: Anti-Inflammatory Agents; Child; Drug Approval; Humans; Immunosuppressive Agents; Muscular Dystrophy, Duchenne; Pregnenediones

2017
    Acta myologica : myopathies and cardiomyopathies : official journal of the Mediterranean Society of Myology, 2017, Volume: 36, Issue:1

    Topics: Adipose Tissue; Child; Diuretics; Edema; Elasticity; Eplerenone; Glucocorticoids; Humans; Hydrogen; Imaging, Three-Dimensional; Magnetic Resonance Imaging; Male; Muscle, Skeletal; Muscular Dystrophy, Duchenne; Pilot Projects; Pregnenediones; Sodium Radioisotopes; Spironolactone

2017
Cardiac profile of asymptomatic children with Becker and Duchenne muscular dystrophy under treatment with steroids and with/without perindopril.
    BMC cardiovascular disorders, 2017, 07-24, Volume: 17, Issue:1

    Topics: Adolescent; Angiotensin-Converting Enzyme Inhibitors; Asymptomatic Diseases; Case-Control Studies; Child; Contrast Media; Cross-Sectional Studies; Echocardiography; Electrocardiography; Gadolinium DTPA; Heart Diseases; Humans; Magnetic Resonance Imaging; Male; Muscular Dystrophy, Duchenne; Perindopril; Pregnenediones; Protective Agents; Time Factors; Treatment Outcome; Ventricular Function, Left; Ventricular Function, Right

2017
Dual Therapy Deflazacort/Doxycyclyne Is Better Than Deflazacort Monotherapy to Alleviate Cardiomyopathy in Dystrophin-Deficient mdx Mice.
    Journal of cardiovascular pharmacology and therapeutics, 2017, Volume: 22, Issue:5

    Topics: Animals; Cardiomyopathies; Doxycycline; Drug Therapy, Combination; Dystrophin; Electrocardiography; Female; Male; Mice; Mice, Inbred C57BL; Muscular Dystrophy, Duchenne; Pregnenediones

2017
Deflazacort (Emflaza) for Duchenne muscular dystrophy.
    The Medical letter on drugs and therapeutics, 2017, 09-11, Volume: 59, Issue:1529

    Topics: Adrenal Cortex Hormones; Humans; Muscular Dystrophy, Duchenne; Pregnenediones; Treatment Outcome

2017
Deflazacort-New Costs of an Old Medicine.
    JAMA neurology, 2018, Feb-01, Volume: 75, Issue:2

    Topics: Anti-Inflammatory Agents; Humans; Muscular Dystrophy, Duchenne; Pregnenediones

2018
Identification of plasma interleukins as biomarkers for deflazacort and omega-3 based Duchenne muscular dystrophy therapy.
    Cytokine, 2018, Volume: 102

    Topics: Animals; Anti-Inflammatory Agents; Biomarkers; Disease Progression; Fatty Acids, Omega-3; Interferon-gamma; Interleukins; Mice; Muscular Dystrophy, Duchenne; Pregnenediones; Transforming Growth Factor beta; Tumor Necrosis Factor-alpha

2018
Cataract development associated with long-term glucocorticoid therapy in Duchenne muscular dystrophy patients.
    Journal of AAPOS : the official publication of the American Association for Pediatric Ophthalmology and Strabismus, 2018, Volume: 22, Issue:3

    Topics: Adolescent; Cataract; Cataract Extraction; Child; Female; Glucocorticoids; Humans; Immunosuppressive Agents; Intraocular Pressure; Male; Muscular Dystrophy, Duchenne; Ocular Hypertension; Prednisone; Pregnenediones; Prevalence; Retrospective Studies; Time Factors; Tonometry, Ocular; Young Adult

2018
Myocarditis in Duchenne Muscular Dystrophy After Changing Steroids.
    JAMA cardiology, 2018, 10-01, Volume: 3, Issue:10

    Topics: Adolescent; Drug Substitution; Emergency Service, Hospital; Humans; Male; Muscular Dystrophy, Duchenne; Myocarditis; Prednisone; Pregnenediones; Steroids

2018
Fractures and Linear Growth in a Nationwide Cohort of Boys With Duchenne Muscular Dystrophy With and Without Glucocorticoid Treatment: Results From the UK NorthStar Database.
    JAMA neurology, 2019, 06-01, Volume: 76, Issue:6

    Topics: Adolescent; Back Pain; Body Height; Bone Density Conservation Agents; Case-Control Studies; Child; Cohort Studies; Diphosphonates; Fractures, Bone; Glucocorticoids; Growth Disorders; Humans; Incidence; Male; Muscular Dystrophy, Duchenne; Osteoporosis; Osteoporotic Fractures; Pregnenediones; Proportional Hazards Models; Retrospective Studies; Risk Factors; Spinal Fractures; United Kingdom

2019
Comparison of Pulmonary Function Decline in Steroid-Treated and Steroid-Naïve Patients with Duchenne Muscular Dystrophy.
    The Journal of pediatrics, 2019, Volume: 210

    Topics: Adolescent; Child; Disease Progression; Glucocorticoids; Humans; Male; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Respiratory Function Tests; Retrospective Studies

2019
Glucocorticoid treatment for the prevention of scoliosis in children with Duchenne muscular dystrophy: long-term follow-up.
    The Journal of bone and joint surgery. American volume, 2013, Jun-19, Volume: 95, Issue:12

    Topics: Child; Follow-Up Studies; Glucocorticoids; Humans; Kaplan-Meier Estimate; Long-Term Care; Male; Muscular Dystrophy, Duchenne; Pregnenediones; Scoliosis; Treatment Outcome

2013
Corticosteroids can reduce the severity of scoliosis in Duchenne muscular dystrophy.
    The Journal of bone and joint surgery. American volume, 2013, Jun-19, Volume: 95, Issue:12

    Topics: Glucocorticoids; Humans; Male; Muscular Dystrophy, Duchenne; Pregnenediones; Scoliosis

2013
The impact of deflazacort on puberty in Duchenne muscular dystrophy.
    Pediatric neurology, 2013, Volume: 49, Issue:4

    Topics: Adolescent; Humans; Immunosuppressive Agents; Male; Muscular Dystrophy, Duchenne; Nova Scotia; Pilot Projects; Pregnenediones; Puberty, Delayed; Treatment Outcome

2013
Anti-dystrophin T cell responses in Duchenne muscular dystrophy: prevalence and a glucocorticoid treatment effect.
    Human gene therapy, 2013, Volume: 24, Issue:9

    Topics: Age Factors; CD4-Positive T-Lymphocytes; CD8-Positive T-Lymphocytes; Dependovirus; Dystrophin; Genetic Therapy; Glucocorticoids; Humans; Immunosuppressive Agents; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones

2013
EPA protects against muscle damage in the mdx mouse model of Duchenne muscular dystrophy by promoting a shift from the M1 to M2 macrophage phenotype.
    Journal of neuroimmunology, 2013, Nov-15, Volume: 264, Issue:1-2

    Topics: Analysis of Variance; Animals; Antigens, Differentiation; Creatine Kinase; Disease Models, Animal; Eicosapentaenoic Acid; Enzyme-Linked Immunosorbent Assay; Female; Interferon-gamma; Interleukin-10; Lectins, C-Type; Macrophages; Male; Mannose Receptor; Mannose-Binding Lectins; Mice; Mice, Inbred C57BL; Mice, Inbred mdx; Muscles; Muscular Dystrophy, Duchenne; Nitric Oxide Synthase Type II; Phenotype; Pregnenediones; Receptors, Cell Surface

2013
Corticosteroid Treatments in Males With Duchenne Muscular Dystrophy: Treatment Duration and Time to Loss of Ambulation.
    Journal of child neurology, 2015, Volume: 30, Issue:10

    Topics: Adrenal Cortex Hormones; Age of Onset; Child; Disease Progression; Follow-Up Studies; Humans; Longitudinal Studies; Male; Muscular Dystrophy, Duchenne; Neuromuscular Agents; Prednisone; Pregnenediones; Proportional Hazards Models; Time Factors; United States; Walking

2015
Myocardial fibrosis burden predicts left ventricular ejection fraction and is associated with age and steroid treatment duration in duchenne muscular dystrophy.
    Journal of the American Heart Association, 2015, Mar-26, Volume: 4, Issue:4

    Topics: Adolescent; Adult; Age Factors; Child; Disease Progression; Fibrosis; Glucocorticoids; Heart; Humans; Magnetic Resonance Imaging; Male; Muscular Dystrophy, Duchenne; Myocardium; Prednisone; Pregnenediones; Retrospective Studies; Stroke Volume; Young Adult

2015
Co-administration of deflazacort and doxycycline: a potential pharmacotherapy for Duchenne muscular dystrophy.
    Clinical and experimental pharmacology & physiology, 2015, Volume: 42, Issue:7

    Topics: Animals; Doxycycline; Drug Combinations; Female; Male; Mice; Mice, Inbred mdx; Muscle Fatigue; Muscle Strength; Muscular Dystrophy, Duchenne; Phenotype; Pregnenediones; Treatment Outcome

2015
Corticosteroid Treatment and Growth Patterns in Ambulatory Males with Duchenne Muscular Dystrophy.
    The Journal of pediatrics, 2016, Volume: 173

    Topics: Adolescent; Body Height; Body Mass Index; Body Weight; Case-Control Studies; Child; Child, Preschool; Dose-Response Relationship, Drug; Glucocorticoids; Humans; Male; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones

2016
Vertebral Fractures in Duchenne Muscular Dystrophy Patients Managed With Deflazacort.
    Journal of pediatric orthopedics, 2018, Volume: 38, Issue:6

    Topics: Adolescent; Adrenal Cortex Hormones; Bone Density; Bone Density Conservation Agents; Child; Diphosphonates; Glucocorticoids; Humans; Immunosuppressive Agents; Male; Muscular Dystrophy, Duchenne; Osteoporosis; Osteoporotic Fractures; Pamidronate; Pregnenediones; Quality of Life; Retrospective Studies; Risk Factors; Spinal Fractures; Time Factors; Walking

2018
Identifying evidence of cardio-renal syndrome in patients with Duchenne muscular dystrophy using cystatin C.
    Neuromuscular disorders : NMD, 2016, Volume: 26, Issue:10

    Topics: Adolescent; Adult; Anti-Inflammatory Agents; Biomarkers; Cardio-Renal Syndrome; Child; Cross-Sectional Studies; Cystatin C; Echocardiography; Glomerular Filtration Rate; Glucocorticoids; Humans; Magnetic Resonance Imaging; Male; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Retrospective Studies; Ventricular Function, Left; Young Adult

2016
Long-Term Outcome of Interdisciplinary Management of Patients with Duchenne Muscular Dystrophy Receiving Daily Glucocorticoid Treatment.
    The Journal of pediatrics, 2017, Volume: 182

    Topics: Adolescent; Age Factors; Child; Cohort Studies; Dose-Response Relationship, Drug; Drug Administration Schedule; Exercise Therapy; Follow-Up Studies; Fractures, Bone; Glucocorticoids; Humans; Insulin Resistance; Long-Term Care; Male; Muscular Dystrophy, Duchenne; Osteoporosis; Patient Care Team; Prednisone; Pregnenediones; Retrospective Studies; Risk Assessment; Severity of Illness Index; Treatment Outcome; Weight Gain

2017
Corticosteroid effects on blood gene expression in Duchenne muscular dystrophy.
    The pharmacogenomics journal, 2009, Volume: 9, Issue:6

    Topics: Adipose Tissue; Adolescent; Case-Control Studies; Child; Child, Preschool; Chondroitin Sulfates; Gene Expression; Gene Expression Profiling; Humans; Iron; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Retrospective Studies; RNA, Messenger

2009
Comparison of motor strength and function in patients with Duchenne muscular dystrophy with or without steroid therapy.
    Arquivos de neuro-psiquiatria, 2010, Volume: 68, Issue:5

    Topics: Age Factors; Anti-Inflammatory Agents; Child; Child, Preschool; Disease Progression; Female; Glucocorticoids; Humans; Male; Motor Activity; Muscle Strength; Muscle, Skeletal; Muscular Dystrophy, Duchenne; Prednisolone; Pregnenediones

2010
Impact of bisphosphonates on survival for patients with Duchenne muscular dystrophy.
    Pediatrics, 2011, Volume: 127, Issue:2

    Topics: Adolescent; Adult; Child; Cohort Studies; Diphosphonates; Drug Therapy, Combination; Follow-Up Studies; Humans; Male; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Retrospective Studies; Survival Analysis; Young Adult

2011
Functional changes in Duchenne muscular dystrophy: a 12-month longitudinal cohort study.
    Neurology, 2011, Jul-19, Volume: 77, Issue:3

    Topics: Adolescent; Anti-Inflammatory Agents; Child; Child, Preschool; Cohort Studies; Cross-Sectional Studies; Disease Progression; Female; Humans; Male; Muscular Dystrophy, Duchenne; Prednisolone; Pregnenediones; Reproducibility of Results; Severity of Illness Index; Statistics as Topic; Walking

2011
Motor function measure scale, steroid therapy and patients with Duchenne muscular dystrophy.
    Arquivos de neuro-psiquiatria, 2012, Volume: 70, Issue:3

    Topics: Adolescent; Child; Disability Evaluation; Disease Progression; Glucocorticoids; Humans; Motor Activity; Muscular Dystrophy, Duchenne; Prednisolone; Pregnenediones

2012
Early corticosteroid treatment in 4 Duchenne muscular dystrophy patients: 14-year follow-up.
    Muscle & nerve, 2012, Volume: 45, Issue:6

    Topics: Adolescent; Adrenal Cortex Hormones; Follow-Up Studies; Humans; Longitudinal Studies; Male; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Prospective Studies; Puberty, Delayed; Stroke Volume; Treatment Outcome; Walking

2012
The Canadian experience with long-term deflazacort treatment in Duchenne muscular dystrophy.
    Acta myologica : myopathies and cardiomyopathies : official journal of the Mediterranean Society of Myology, 2012, Volume: 31, Issue:1

    Topics: Adolescent; Adrenal Cortex Hormones; Body Height; Bone Density; Canada; Cataract; Child; Fractures, Bone; Humans; Immunosuppressive Agents; Male; Muscle Strength; Muscular Dystrophy, Duchenne; Pregnenediones; Spinal Injuries; Spine; Walking; Weight Gain

2012
Bone health in boys with Duchenne Muscular Dystrophy on long-term daily deflazacort therapy.
    Neuromuscular disorders : NMD, 2012, Volume: 22, Issue:12

    Topics: Adolescent; Anti-Inflammatory Agents; Body Height; Bone and Bones; Bone Density; Child; Fractures, Bone; Humans; Male; Muscular Dystrophy, Duchenne; Pregnenediones; Quality of Life; Risk Factors; Time Factors

2012
Lung function monitoring in patients with duchenne muscular dystrophy on steroid therapy.
    BMC research notes, 2012, Aug-13, Volume: 5

    Topics: Adolescent; Analysis of Variance; Anti-Inflammatory Agents; Child; Child, Preschool; Forced Expiratory Volume; Humans; Lung; Male; Muscular Dystrophy, Duchenne; Prednisolone; Pregnenediones; Respiratory Function Tests; Treatment Outcome; Vital Capacity; Young Adult

2012
Growth hormone treatment in boys with Duchenne muscular dystrophy and glucocorticoid-induced growth failure.
    Neuromuscular disorders : NMD, 2012, Volume: 22, Issue:12

    Topics: Body Height; Body Weight; Child; Glucocorticoids; Growth Disorders; Human Growth Hormone; Humans; Male; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Treatment Outcome

2012
Health-related quality of life in children and adolescents with Duchenne muscular dystrophy.
    Pediatrics, 2012, Volume: 130, Issue:6

    Topics: Activities of Daily Living; Adolescent; Age Factors; Anti-Inflammatory Agents; Child; Child, Preschool; Disability Evaluation; Disease Progression; Humans; Male; Muscular Dystrophy, Duchenne; Needs Assessment; Prednisone; Pregnenediones; Quality of Life; Reference Values; Sick Role; Social Adjustment; Surveys and Questionnaires; Wheelchairs

2012
24 month longitudinal data in ambulant boys with Duchenne muscular dystrophy.
    PloS one, 2013, Volume: 8, Issue:1

    Topics: Adolescent; Analysis of Variance; Anti-Inflammatory Agents; Child; Child, Preschool; Exercise Test; Glucocorticoids; Humans; Logistic Models; Longitudinal Studies; Male; Muscular Dystrophy, Duchenne; Outcome Assessment, Health Care; Prednisone; Pregnenediones; Risk Assessment; Risk Factors; Time Factors; Walking

2013
Glucocorticoid treatment alleviates dystrophic myofiber pathology by activation of the calcineurin/NF-AT pathway.
    FASEB journal : official publication of the Federation of American Societies for Experimental Biology, 2004, Volume: 18, Issue:15

    Topics: Active Transport, Cell Nucleus; Animals; Calcineurin; Cell Nucleus; DNA-Binding Proteins; Enzyme Activation; Mice; Mice, Inbred mdx; Mitogen-Activated Protein Kinase 8; Muscle Fibers, Skeletal; Muscle, Skeletal; Muscular Dystrophy, Duchenne; NFATC Transcription Factors; Nuclear Proteins; Pregnenediones; Signal Transduction; Transcription Factors; Transcriptional Activation; Utrophin

2004
Practice parameter: corticosteroid treatment of Duchenne dystrophy: report of the Quality Standards Subcommittee of the American Academy of Neurology and the Practice Committee of the Child Neurology Society.
    Neurology, 2005, Jan-11, Volume: 64, Issue:1

    Topics: Adolescent; Child; Child, Preschool; Creatinine; Dose-Response Relationship, Drug; Drug Administration Schedule; Humans; Male; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Risk Assessment; Time; Weight Gain

2005
Alendronate in the treatment of low bone mass in steroid-treated boys with Duchennes muscular dystrophy.
    Archives of physical medicine and rehabilitation, 2005, Volume: 86, Issue:2

    Topics: Alendronate; Bone and Bones; Bone Density; Child; Glucocorticoids; Humans; Male; Muscular Dystrophy, Duchenne; Pregnenediones

2005
Corticosteroid treatment and functional improvement in Duchenne muscular dystrophy: long-term effect.
    American journal of physical medicine & rehabilitation, 2005, Volume: 84, Issue:11

    Topics: Adolescent; Anti-Inflammatory Agents; Body Height; Body Weight; Disease Progression; Dose-Response Relationship, Drug; Follow-Up Studies; Glucocorticoids; Humans; Male; Motor Activity; Motor Skills; Muscle Weakness; Muscular Dystrophy, Duchenne; Prednisone; Pregnenediones; Retrospective Studies; Statistics, Nonparametric

2005
Long-term benefits of deflazacort treatment for boys with Duchenne muscular dystrophy in their second decade.
    Neuromuscular disorders : NMD, 2006, Volume: 16, Issue:4

    Topics: Adolescent; Body Height; Body Weight; Cataract; Child; Humans; Immunosuppressive Agents; Lung; Male; Motor Activity; Muscular Dystrophy, Duchenne; Posture; Pregnenediones; Quality of Life; Respiratory Function Tests; Retrospective Studies; Stroke Volume; Treatment Outcome; Walking

2006
The glucocorticoid receptor N363S polymorphism and steroid response in Duchenne dystrophy.
    Journal of neurology, neurosurgery, and psychiatry, 2006, Volume: 77, Issue:10

    Topics: Anti-Inflammatory Agents; Child; Child, Preschool; Cohort Studies; Female; Humans; Male; Muscular Dystrophy, Duchenne; Polymerase Chain Reaction; Polymorphism, Genetic; Prednisone; Pregnenediones; Receptors, Glucocorticoid; Steroids

2006
Quantification of muscle strength and motor ability in patients with Duchenne muscular dystrophy on steroid therapy.
    Arquivos de neuro-psiquiatria, 2007, Volume: 65, Issue:2A

    Topics: Anti-Inflammatory Agents; Child; Child, Preschool; Female; Follow-Up Studies; Glucocorticoids; Humans; Male; Motor Activity; Muscle Strength; Muscle, Skeletal; Muscular Dystrophy, Duchenne; Prednisolone; Prednisone; Pregnenediones; Surveys and Questionnaires

2007
Cardiac treatment in neuro-muscular diseases.
    Acta myologica : myopathies and cardiomyopathies : official journal of the Mediterranean Society of Myology, 2006, Volume: 25, Issue:3

    Topics: Angiotensin-Converting Enzyme Inhibitors; Anti-Inflammatory Agents; Cardiac Output, Low; Case-Control Studies; Disease Progression; Fosinopril; Furosemide; Humans; Muscular Dystrophies, Limb-Girdle; Muscular Dystrophy, Duchenne; Myotonic Dystrophy; Pregnenediones; Prognosis; Retrospective Studies; Severity of Illness Index; Sodium Potassium Chloride Symporter Inhibitors

2006
Deflazacort treatment of Duchenne muscular dystrophy.
    The Journal of pediatrics, 2001, Volume: 138, Issue:1

    Topics: Activities of Daily Living; Adolescent; Anti-Inflammatory Agents; Body Height; Body Weight; Cataract; Child; Humans; Male; Motor Skills; Muscular Dystrophy, Duchenne; Pregnenediones; Retrospective Studies; Treatment Outcome; Vital Capacity; Walking

2001
Vertebral compression in Duchenne muscular dystrophy following deflazacort.
    Neuromuscular disorders : NMD, 2002, Volume: 12, Issue:3

    Topics: Adolescent; Humans; Immunosuppressive Agents; Lumbar Vertebrae; Male; Muscular Dystrophy, Duchenne; Pregnenediones; Spinal Fractures; Thoracic Vertebrae

2002