defibrotide has been researched along with Leukodystrophy--Metachromatic* in 1 studies
1 other study(ies) available for defibrotide and Leukodystrophy--Metachromatic
Article | Year |
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Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy.
Topics: Genetic Therapy; Hematopoietic Stem Cell Transplantation; Humans; Leukodystrophy, Metachromatic; Male; Platelet Aggregation Inhibitors; Polydeoxyribonucleotides; Transplantation Conditioning; Twins | 2018 |