busulfan has been researched along with Mucopolysaccharidoses in 5 studies
Mucopolysaccharidoses: Group of lysosomal storage diseases each caused by an inherited deficiency of an enzyme involved in the degradation of glycosaminoglycans (mucopolysaccharides). The diseases are progressive and often display a wide spectrum of clinical severity within one enzyme deficiency.
| Excerpt | Relevance | Reference |
|---|---|---|
| "We successfully used a haploidentical transplantation protocol with posttransplant cyclophosphamide (CY) (50 mg/kg/d on days +3 and +4) for in vivo T-cell depletion in patients with mucopolysaccharidosis using reduced-intensive conditioning regimens, followed by a busulfan-based conditioning regimen, which included busulfan (12 to 16 mg/kg) and fludarabine(150 to 200 mg/m)+rabbit antihuman thymocyte globulin (7." | 3.88 | Posttransplant Cyclophosphamide for HLA-haploidentical Transplantation in Patients With Mucopolysaccharidosis. ( Feng, S; Li, J; Liu, R; Shi, X; Song, Z; Yue, Y, 2018) |
| Timeframe | Studies, this research(%) | All Research% |
|---|---|---|
| pre-1990 | 0 (0.00) | 18.7374 |
| 1990's | 0 (0.00) | 18.2507 |
| 2000's | 0 (0.00) | 29.6817 |
| 2010's | 3 (60.00) | 24.3611 |
| 2020's | 2 (40.00) | 2.80 |
| Authors | Studies |
|---|---|
| Jubert, C | 1 |
| De Berranger, E | 1 |
| Castelle, M | 1 |
| Dalle, JH | 1 |
| Ouachee-Chardin, M | 1 |
| Sevin, C | 1 |
| Yakoub-Agha, I | 1 |
| Brassier, A | 1 |
| Wang, J | 1 |
| Chen, J | 1 |
| Luo, C | 1 |
| Zhang, H | 1 |
| Gu, X | 1 |
| Zhang, W | 1 |
| Yue, Y | 1 |
| Song, Z | 1 |
| Li, J | 1 |
| Feng, S | 1 |
| Liu, R | 1 |
| Shi, X | 1 |
| Chen, Y | 1 |
| Xu, LP | 1 |
| Zhang, XH | 1 |
| Chen, H | 1 |
| Wang, FR | 1 |
| Liu, KY | 1 |
| Qin, J | 1 |
| Yang, YL | 1 |
| Huang, XJ | 1 |
| Aldenhoven, M | 1 |
| Jones, SA | 1 |
| Bonney, D | 1 |
| Borrill, RE | 1 |
| Coussons, M | 1 |
| Mercer, J | 1 |
| Bierings, MB | 1 |
| Versluys, B | 1 |
| van Hasselt, PM | 1 |
| Wijburg, FA | 1 |
| van der Ploeg, AT | 1 |
| Wynn, RF | 1 |
| Boelens, JJ | 1 |
| Trial | Phase | Enrollment | Study Type | Start Date | Status | ||
|---|---|---|---|---|---|---|---|
| The Use of Granulocyte Transfusions After Umbilical Cord Blood Transplant for Leukaemia: A Prospective, Non-randomised, Single-centre Study to Evaluate Safety and Immune Reconstitution[NCT05425043] | 20 participants (Anticipated) | Interventional | 2021-09-14 | Recruiting | |||
| Phase I/II Study Evaluating Safety and Efficacy of Autologous Hematopoietic Stem and Progenitor Cells Genetically Modified With IDUA Lentiviral Vector Encoding for the Human α-L-iduronidase Gene for the Treatment of Patients Affected by Mucopolysaccharido[NCT03488394] | Phase 1/Phase 2 | 8 participants (Actual) | Interventional | 2018-05-11 | Active, not recruiting | ||
| [information is prepared from clinicaltrials.gov, extracted Sep-2024] | |||||||
5 other studies available for busulfan and Mucopolysaccharidoses
| Article | Year |
|---|---|
[Inborn error of metabolism and allogenic hematopoietic cell transplantation: Guidelines from the SFGM-TC].
Topics: Busulfan; Hematopoietic Stem Cell Transplantation; Humans; Mucopolysaccharidoses; Neurodegenerative | 2023 |
[Long-term outcome of hematopoietic stem cell transplantation in two children with Mucopolysaccharidosis].
Topics: Busulfan; Child; Child, Preschool; China; Female; Graft vs Host Disease; Hematopoietic Stem Cell Tra | 2023 |
Posttransplant Cyclophosphamide for HLA-haploidentical Transplantation in Patients With Mucopolysaccharidosis.
Topics: Allografts; Antilymphocyte Serum; Busulfan; Child, Preschool; Cyclophosphamide; Disease-Free Surviva | 2018 |
Busulfan, Fludarabine, and Cyclophosphamide (BFC) conditioning allowed stable engraftment after haplo-identical allogeneic stem cell transplantation in children with adrenoleukodystrophy and mucopolysaccharidosis.
Topics: Adrenoleukodystrophy; Antineoplastic Combined Chemotherapy Protocols; Busulfan; Cyclophosphamide; Fe | 2018 |
Hematopoietic cell transplantation for mucopolysaccharidosis patients is safe and effective: results after implementation of international guidelines.
Topics: Acute Disease; Busulfan; Child; Child, Preschool; Chronic Disease; Cord Blood Stem Cell Transplantat | 2015 |
Hematopoietic cell transplantation for mucopolysaccharidosis patients is safe and effective: results after implementation of international guidelines.
Topics: Acute Disease; Busulfan; Child; Child, Preschool; Chronic Disease; Cord Blood Stem Cell Transplantat | 2015 |
Hematopoietic cell transplantation for mucopolysaccharidosis patients is safe and effective: results after implementation of international guidelines.
Topics: Acute Disease; Busulfan; Child; Child, Preschool; Chronic Disease; Cord Blood Stem Cell Transplantat | 2015 |
Hematopoietic cell transplantation for mucopolysaccharidosis patients is safe and effective: results after implementation of international guidelines.
Topics: Acute Disease; Busulfan; Child; Child, Preschool; Chronic Disease; Cord Blood Stem Cell Transplantat | 2015 |