Page last updated: 2024-08-21

benzoxazoles and Amyloid Neuropathy Type 1

benzoxazoles has been researched along with Amyloid Neuropathy Type 1 in 140 studies

Research

Studies (140)

TimeframeStudies, this research(%)All Research%
pre-19900 (0.00)18.7374
1990's0 (0.00)18.2507
2000's0 (0.00)29.6817
2010's80 (57.14)24.3611
2020's60 (42.86)2.80

Authors

AuthorsStudies
Barbarossa, A; Capucci, A; Casella, M; Ciliberti, G; Dello Russo, A; Falanga, U; Guerra, F; Principi, S; Silenzi, M; Stronati, G; Urbinati, A1
Damy, T; Grogan, M; Gundapaneni, B; Hanna, M; Maurer, MS; Stewart, M; Sultan, MB1
Drachman, BM; Ebede, B; Elliott, P; Gottlieb, SS; Gundapaneni, B; Hoffman, JE; Hummel, SL; Lenihan, DJ; Li, B; Shah, SJ; Sultan, MB2
Brogneaux, C; Grayet, D; Jackers, L; Lacremans, D; Legrand, D; Magnée, M; Nyssen, A; Pirotte, I1
Assmus, B; Bulinski, C; Discher, T; Krämer, HH; Rutsatz, W1
Bhambri, R; Nativi-Nicolau, J; Rozenbaum, MH; Tran, D1
Aguirre, MA; Calandra, CR; Carretero, M; Conti, E; Lautre, A; León-Cejas, L; Negro, A; Nucifora, EM; Posadas-Martínez, ML; Reisin, R; Rugiero, M; Sáez, MS; Salutto, V; Sorroche, P1
Aguirre, MA; Baratta, S; Belziti, CA; Carretero, M; Costabel, JP; Dumont, CA; Fernández, A; Higa, C; Negro, A; Nucifora, EM; Perez de Arenaza, D; Posadas-Martínez, ML; Quiroga, A; Rivas, C; Streitenberg, GM; Villanueva, E; Volberg, VI1
Bonderman, D; Rettl, R1
Baba, Y; Hamada, T; Hirota, T; Kitaoka, H; Kubo, T; Miyagawa, K; Noguchi, T; Ochi, Y; Sugiura, K; Yamasaki, N1
Gomez-Valencia, J; Malhotra, S; Mekritthikrai, R1
Elliott, P; Gundapaneni, B; Sultan, MB1
Baldovino, S; Costanzo, P; Roccatello, D1
Cuddy, SAM1
Casey, M; Li, H; Rozenbaum, M; Sultan, MB1
Mitchell, JD; Rater, M; Schiffer, W; Zaghlol, R1
Balasubramanian, SS; Gaznabi, S; Hussain, K; Iqbal, SH; Kwak, E; Macrinici, V; Minga, I; Pursnani, A; Sarswat, N; Wang, CH; Wathen, L1
Anselmo, J; Coelho, T; Fernandes, J; Kelly, JW; Mesgarzadeh, JS; Monteiro, C; Novais, M; Powers, DL; Powers, ET; Rodrigues, C1
Fukuda, D; Hara, T; Ise, T; Kadota, M; Kawabata, Y; Kusunose, K; Matsuura, T; Osaki, Y; Saijo, Y; Sata, M; Soeki, T; Tserensonom, M; Ueno, R; Wakatsuki, T; Yagi, S; Yamada, H; Yamaguchi, K; Yamazaki, H1
Bulawa, C; Fleming, J; Li, Z; Maurer, TS; Moody, AT; Tess, DA1
Coelho, T; Jaeger, M; Kelly, JW; Powers, ET; Tsai, FJ1
Adams, D; Algalarrondo, V; Benmalek, A; Cauquil, C; Echaniz-Laguna, A; Eliahou, L; Kounis, I; Piekarski, E; Rousseau, A; Rouzet, F; Samuel, D; Slama, MS; Socie, P1
Czepluch, F1
Cruz, MW1
Aschenbrenner, DS1
Chang, Y; Huang, SJ; Lin, KP; Liu, YT; Ricardo, F; Wu, PH; Yen, YJ; Yu, TY1
Gospodinova, M; Kirov, A; Nakov, R; Nakov, V; Sarafov, S; Todorov, T; Todorova, A; Tournev, I1
Ando, Y; Endo, J; Fukuda, K; Inomata, T; Isobe, M; Izumiya, Y; Kuwahara, K; Nakamura, K; Sano, M; Sekijima, Y; Tahara, N; Tsujita, K; Tsutsui, H; Ueda, M1
Murohara, T; Okumura, T1
Gurwitz, JH; Maurer, MS2
Björkenheim, A; Szabó, B; Sztaniszláv, ÁJ1
Paton, DM1
Maurer, MS; Rubin, J1
Amass, L; Cameron, C; Salvo, EM; Samjoo, IA; Stewart, M; Tran, D1
Arnold, SV; Baron, SJ; Bellows, BK; Cohen, DJ; Kazi, DS; Maurer, MS; Shah, SJ; Shen, C; Sperry, BW; Spertus, JA; Yeh, RW2
Le, VH; Lockwood, PA; O'Gorman, MT; Patterson, TA; Riley, S; Sultan, MB; Tankisheva, E; Wang, Q1
Cavallaro, T; Fabrizi, GM; Magrinelli, F; Manganelli, F; Santoro, L; Tamburin, S; Zanette, G1
Coyle, ML; Cuddy, SAM; Falk, RH1
Magomedov, MM; Nasonova, SN; Osmolovskaya, YF; Saidova, MA; Tereschenko, SN; Zhirov, IV1
Brum, M; Caetano, A; Casanova, I; Conceição, I; de Carvalho, M; Díaz, A1
Hale, C; Lin, H; Marantz, JL; Merkel, M1
Cristóbal Gutiérrez, H; Gómez Gómez, D; Martín Vega, MÁ; Pelayo-Negro, AL; Valero Domínguez, M1
Adams, D; Slama, M1
Ando, Y; Hirano, Y; Ishii, T; Matsumoto, N; Sekijima, Y; Takata, A; Ueda, M1
Kelly, JW; Nelson, LT; Paxman, RJ; Powers, ET; Webb, B; Xu, J1
Audia, S; Damy, T; Eicher, JC1
Dou, Y; Ge, S; Lo, GV; Yuan, S; Zhang, Q; Zhang, W; Zhou, S1
Almeida, AR; Azevedo, O; Bento, D; Correia, E; Cruz, I; Lopes, LR; Lourenço, C; Marques, N1
Kemner, J; Parasuraman, B; Rozenbaum, MH1
Damy, T; Garcia-Pavia, P; Gundapaneni, B; Hanna, M; Judge, DP; Merlini, G; Patterson, TA; Riley, S; Schwartz, JH; Sultan, MB; Witteles, R1
Abulizi, M; Audard, V; Bézard, M; Canoui-Poitrine, F; Damy, T; Deux, JF; El Karoui, K; Fanen, P; Funalot, B; Galat, A; Gendre, T; Guendouz, S; Itti, E; Kharoubi, M; Lefaucheur, JP; Moktefi, A; Oghina, S; Planté-Bordeneuve, V; Poullot, E; Teiger, E; Zaroui, A1
Damy, T; Grogan, M; Gundapaneni, B; Hanna, M; Maurer, MS; Patterson, TA; Schwartz, JH; Stewart, M; Sultan, MB1
Harnisch, L; Huh, Y; Nicholas, T; Riley, S1
Benbrahim, M; Hughes, D; Norman, K; Sanchorawala, V; Siddiqi, OK1
Gundapaneni, B; Januzzi, JL; López-Sendón, J; Miller, AB; O'Neill, BJ; Patterson, TA; Sultan, MB1
Galan, L; Gonzalez-Moreno, J; Lebeau, P; Mallaina, P; Martínez-Sesmero, JM; Muñoz-Beamud, F; Peral, C; Rozenbaum, MH; Santos-Rubio, MD; Stewart, M; Tarilonte, P; Tran, D1
Kittleson, MM; Stern, LK1
Boucher, M; Harnisch, LO; Riley, S; Vong, C1
Tian, Z; Zhang, SY1
Bhambri, R; Garcia, A; Grima, D; Heeg, B; Li, B; Masri, A; Postma, M; Rozenbaum, MH; Stewart, M; Tran, D1
Griffin, JM; Maurer, MS; Rosenblum, H1
DeLuca, A; Einstein, AJ; Elias, P; Griffin, JM; Johnson, LL; Kinkhabwala, M; Maurer, MS; Pandey, S; Poterucha, TJ; Ruberg, FL1
Katsuno, M; Koike, H1
Gamino, D; Goldsmith, J; Griffin, JM; Guadalupe, S; Helmke, S; Maurer, MS; Rosenblum, HR; Saith, SE; Santos, JL; Teruya, S1
Amass, L; Gundapaneni, B; Keohane, D; Schwartz, J; Stewart, M1
Clarke, A; Mendes, Á; Sequeiros, J; Sousa, L1
Ando, Y; Iijima, M; Ikeda, S; Ikeda, SI; Katsuno, M; Kawagashira, Y; Koike, H; Misumi, Y; Sobue, G; Takahashi, M1
Alves, C; Beirão, I; Cardoso, M; Coelho, T; Lobato, L; Rocha, A; Silva, A; Teles, P1
Cruz, MW; Elliott, P; Flynn, A; Gundapaneni, B; Hahn, C; Maurer, MS; Merlini, G; Rapezzi, C; Riley, S; Schwartz, J; Shah, SJ; Sultan, MB1
Amass, L; Barroso, FA; Ebede, B; Judge, DP; Li, H; Stewart, M; Sultan, MB1
Ahn, S; Choi, S; Hyun, HC; Jang, E; Jeong, JW; Joo, SH; Kim, S; Koo, TS; Lee, KR1
Matsushima, M; Sakakibara, M; Sasaki, H; Shimamura, T; Tsuda, M; Yabe, I1
Gundapaneni, BK; Keohane, DJ; Schwartz, JH; Sultan, MB1
Ando, Y; Ikeda, T; Masuda, T; Misumi, Y; Shinriki, S; Ueda, M; Yamashita, T1
Ando, Y; Ishii, T; Koike, H; Misawa, S; Sekijima, Y; Ueda, M1
Bianchi, A; Mascalchi, M; Pastorelli, F; Rapezzi, C; Salvi, F; Vella, A; Volpe, R1
Castro, J; Conceição, I; de Carvalho, M; Miranda, B1
Coelho, T; Ferreira, N; Kelly, JW; Martins da Silva, A; Mesgarzadeh, J; Monteiro, C; Novais, M1
Kristen, AV1
Barsdorf, AI; Damy, T; Drachman, BM; Elliott, PM; Grogan, M; Gundapaneni, B; Hanna, M; Huber, P; Judge, DP; Kristen, AV; Maurer, MS; Merlini, G; Patterson, TA; Rapezzi, C; Riley, S; Schumacher, J; Schwartz, JH; Shah, SJ; Stewart, M; Sultan, MB; Waddington-Cruz, M; Witteles, R1
Ando, Y; Ikeda, N; Kato, TS; Maurer, MS; Tanno, K1
Coelho, T; Conceição, I; Costa, J; de Carvalho, M; Inês, M; Soares, M1
Barreira, AA; Bulle, AS; França, MC; Freitas, MRG; Gondim, FAA; Marques, W; Marrone, CD; Nascimento, OJM; Pinto, MV; Pupe, C; Rotta, FT; Waddington-Cruz, M1
Amaki, M; Amano, M; Hamatani, Y; Hasegawa, T; Ishibashi-Ueda, H; Izumi, C; Kanzaki, H; Morita, Y; Ohta-Ogo, K; Okada, A; Sekijima, Y; Shimazaki, C; Shintani, Y; Takahama, H; Yasuda, S; Yazaki, M; Yoshinaga, T1
Agarwal, S; Betts, M; Chitnis, M; Fahrbach, K; Gollob, J; Lin, H; Planté-Bordeneuve, V; Polydefkis, M1
Ando, Y; Hashimoto, T; Hiroe, M; Kawamura, S; Yamamoto, H; Yamashita, T; Yokochi, T1
Maurer, MS; Rapezzi, C; Sultan, MB1
Manion, C; Sharma, UC1
Falk, RH1
Brannagan, T; Buades-Reinés, J; Buxbaum, JN; Cisneros, E; Conceicao, I; Imai, A; Kyriakides, T; Merlini, G; Obici, L; Plante-Bordeneuve, V; Rousseau, A; Sekijima, Y; Waddington Cruz, M; Yamada, M1
Elliott, PM; Lorenzini, M1
Castro, J; Conceição, I; Costa, J; de Castro, I1
Abate, E; Ali, M; Bigalke, B; de Vecchis, R; Mammadov, M; Matiakis, M; Mavrogeni, S; Melnyk, H; Noutsias, M; Rigopoulos, AG; Torky, AR; Vogt, A; Wohlgemuth, W1
Buxbaum, JN1
Hineno, A; Ichikawa, T; Ikeda, SI; Makino, M1
Deeks, ED; Lamb, YN1
Aimo, A; Barison, A; Castiglione, V; Emdin, M; Fontana, M; Giannoni, A; Merlini, G; Passino, C; Perfetto, F; Rapezzi, C; Seferović, PM; Vergaro, G1
Cameron, C; Salvo, EM; Samjoo, IA; Tran, D1
Agarwal, S; Betts, M; Chitnis, M; Fahrbach, K; Lin, H; Polydefkis, M1
Gagliardi, C; Milandri, A; Rapezzi, C1
Anselmo, J; Brighty, GJ; Coelho, T; Fernandes, J; Kelly, JW; Mesgazardeh, JS; Monteiro, C; Novais, M; Powers, DL; Powers, ET; Rodrigues, C1
Bokhari, S; Damy, T; Elliott, PM; Falk, RH; Fine, NM; Garcia-Pavia, P; Gospodinova, M; Obici, L; Rapezzi, C; Witteles, RM1
Autore, C; Canepa, M; Cappelli, F; Milandri, A; Mussinelli, R; Musumeci, B; Perfetto, F; Perlini, S; Rapezzi, C; Tini, G1
Merkies, IS1
Adams, D; Cauquil, C; Théaudin, M1
Adams, D; Ducot, B; Lacroix, C; Lozeron, P; Mincheva, Z; Théaudin, M1
Chan, J; Coelho, T; Conceiçao, I; Cruz, MW; da Silva, AM; Grogan, DR; Kelly, JW; Labaudinière, R; Maia, LF; Packman, J; Planté-Bordeneuve, V; Schmidt, HH; Suhr, OB; Trigo, P1
Nencetti, S; Orlandini, E; Rossello, A1
Grogan, DR; Judge, DP; Merlini, G; Obici, L; Packman, J; Perlini, S; Planté-Bordeneuve, V; Schmidt, H; Tripp, T1
Adams, D; Algalarrondo, V; Cauquil, C; Slama, M; Théaudin, M1
Sekijima, Y4
Scott, LJ1
Castaño, A; Drachman, BM; Judge, D; Maurer, MS1
Acker, T; Haverkamp, T; Kimmich, C; Krämer, HH; Röcken, C; Schänzer, A; Weidner, I1
Aarts, J; Berthet, K; Damy, T; Judge, DP; Kristen, AV; Li, H1
Aarts, J; Falk, RH; Grogan, DR; Judge, DP; Lombardo, I; Maurer, MS; Mundayat, R; Packman, J; Quyyumi, AA1
Ackermann, E; Dubrey, S; Gillmore, J1
Ando, Y; Baba, M; Honda, M; Inomata, Y; Kon, T; Misumi, Y; Nishijima, H; Obayashi, K; Suzuki, C; Tomiyama, M1
Baranczak, A; Cho, Y; Helmke, S; Horn, EM; Kelly, JW; Maurer, MS; Teruya, S1
Adams, D; Algalarrondo, V; Beaudonnet, G; Cauquil, C; Labeyrie, C; Théaudin, M1
Ando, Y; Ikeda, S; Machii, K; Misumi, Y; Morita, H; Obayashi, K; Ohta, M; Sekijima, Y; Takata, A; Ueda, M; Yamashita, T1
Bisogni, G; Calabrese, D; Cavallaro, T; Cortese, A; Fabrizi, GM; Gemelli, C; Gentile, L; Grandis, M; Lozza, A; Luigetti, M; Manganelli, F; Mauro, A; Mazzeo, A; Obici, L; Pareyson, D; Perlini, S; Piscosquito, G; Pradotto, LG; Russo, M; Sabatelli, M; Santoro, L; Schenone, A; Stancanelli, C; Vita, G1
Alvarez, R; Bettencourt, BR; Borland, TD; Butler, JS; Chan, A; Chen, Q; Costelha, S; Fishman, S; Fitzgerald, K; Foster, DJ; Gonçalves, P; Manoharan, M; Meyers, RE; Milstein, S; Nochur, SV; Qin, J; Rajeev, KG; Sah, DW; Saraiva, MJ; Willoughby, JL; Zimmermann, TS1
Bettini, M; Chaves, M; Cristiano, E; Marciano, S; Rugiero, M; Sáez, S1
Amass, L; Gundapaneni, B; Keohane, D; Li, H; Schwartz, J; Waddington Cruz, M1
Buxbaum, JN; Coelho, T; Gelbart, T; Kelly, JW; Kurian, SM; Novais, M; Salomon, DR; Whisenant, T1
Beirão, JM; Casal, I; Monteiro, S1
Ayache, SS; Azoulay, D; Damy, T; Feray, C; Gorram, F; Le Corvoisier, P; Lefaucheur, JP; Nordine, T; Planté-Bordeneuve, V; Salhi, H1
Miyazaki, Y1
Adams, D; Samuel, D; Slama, M1
de Lartigue, J1
Chalk, C1
Campistol, JM; Chan, J; Coelho, T; Conceição, IM; Grogan, DR; Kelly, JW; Labaudinière, R; Lozeron, P; Maia, LF; Martins da Silva, A; Packman, J; Planté-Bordeneuve, V; Schmidt, HH; Suhr, OB; Trigo, P; Waddington Cruz, M; Wilson, A1
de Carvalho, M1

Reviews

35 review(s) available for benzoxazoles and Amyloid Neuropathy Type 1

ArticleYear
[Diagnosis and treatment of cardiac transthyretin amyloidosis. Innovative therapy with tafamidis.]
    Revue medicale de Liege, 2022, Volume: 77, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Therapies, Investigational

2022
Impact of Tafamidis on Survival in a Real-World Community-Based Cohort.
    Current problems in cardiology, 2022, Volume: 47, Issue:12

    Topics: Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Female; Heart Failure; Humans; Male; Observational Studies as Topic; Prospective Studies

2022
Long-term survival in people with transthyretin amyloid cardiomyopathy who took tafamidis: A Plain Language Summary.
    Future cardiology, 2023, Volume: 19, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Prealbumin

2023
[Transthyretin amyloid cardiomyopathy].
    Innere Medizin (Heidelberg, Germany), 2023, Volume: 64, Issue:9

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Prealbumin; Stroke Volume; Tomography, X-Ray Computed

2023
Tafamidis for autonomic neuropathy in hereditary transthyretin (ATTR) amyloidosis: a review.
    Clinical autonomic research : official journal of the Clinical Autonomic Research Society, 2019, Volume: 29, Issue:Suppl 1

    Topics: Amyloid Neuropathies, Familial; Autonomic Nervous System Diseases; Benzoxazoles; Humans; Polyneuropathies

2019
Cardiac Amyloidosis: Overlooked, Underappreciated, and Treatable.
    Annual review of medicine, 2020, 01-27, Volume: 71

    Topics: Amyloid Neuropathies, Familial; Amyloidosis; Arrhythmias, Cardiac; Benzoates; Benzoxazoles; Biopsy; Cardiac Pacing, Artificial; Cardiomyopathies; Diflunisal; Disease Progression; Early Diagnosis; Early Medical Intervention; Echocardiography; Electrocardiography; Heart Failure; Humans; Immunoglobulin Light-chain Amyloidosis; Immunologic Factors; Magnetic Resonance Imaging; Oligonucleotides; Prealbumin; Prognosis; Proteasome Inhibitors; Pyrazoles; Radionuclide Imaging; RNA, Small Interfering

2020
The impact of clinical heterogeneity on conducting network meta-analyses in transthyretin amyloidosis with polyneuropathy.
    Current medical research and opinion, 2020, Volume: 36, Issue:5

    Topics: Adult; Amyloid Neuropathies, Familial; Bayes Theorem; Benzoxazoles; Female; Humans; Male; Middle Aged; Network Meta-Analysis; Oligonucleotides; Polyneuropathies; RNA, Small Interfering

2020
Pharmacological treatment for familial amyloid polyneuropathy.
    The Cochrane database of systematic reviews, 2020, Apr-20, Volume: 4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Disease Progression; Humans; Oligonucleotides; Patient Dropouts; Quality of Life; Randomized Controlled Trials as Topic; RNA, Small Interfering

2020
Overview of treatments used in transthyretin-related hereditary amyloidosis: a systematic review.
    European journal of hospital pharmacy : science and practice, 2020, Volume: 27, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Humans; Liver Transplantation; RNA, Small Interfering

2020
Hereditary transthyretin amyloidosis: current treatment.
    Current opinion in neurology, 2020, Volume: 33, Issue:5

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Biomarkers; Clinical Trials as Topic; Disease Progression; Humans; Oligonucleotides, Antisense; Quality of Life

2020
[Transthyretin cardiac amyloidosis].
    La Revue de medecine interne, 2020, Volume: 41, Issue:10

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Echocardiography; Electrocardiography; Humans

2020
Specific Therapy for Transthyretin Cardiac Amyloidosis: A Systematic Literature Review and Evidence-Based Recommendations.
    Journal of the American Heart Association, 2020, 10-20, Volume: 9, Issue:19

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Cardiovascular Agents; Genetic Therapy; Humans

2020
A Review of Novel Agents and Clinical Considerations in Patients With ATTR Cardiac Amyloidosis.
    Journal of cardiovascular pharmacology, 2021, 05-01, Volume: 77, Issue:5

    Topics: Amyloid Neuropathies, Familial; Animals; Benzoxazoles; Cardiomyopathies; Cardiovascular Agents; Diflunisal; Genetic Predisposition to Disease; Humans; Mutation; Oligonucleotides; Phenotype; Prealbumin; RNA, Small Interfering; Treatment Outcome

2021
Updates in Cardiac Amyloidosis Diagnosis and Treatment.
    Current oncology reports, 2021, 03-16, Volume: 23, Issue:4

    Topics: Amyloid Neuropathies, Familial; Amyloidosis; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Immunoglobulin Light-chain Amyloidosis

2021
Pathophysiology and Therapeutic Approaches to Cardiac Amyloidosis.
    Circulation research, 2021, 05-14, Volume: 128, Issue:10

    Topics: Aging; Alkylating Agents; Amyloid; Amyloid Neuropathies, Familial; Amyloidosis; Antibodies, Monoclonal; Benzoates; Benzoxazoles; Bridged Bicyclo Compounds, Heterocyclic; Cardiomyopathies; Catechol O-Methyltransferase Inhibitors; Heart Transplantation; Humans; Immunomodulating Agents; Oligonucleotides; Proteasome Inhibitors; Protein Folding; Pyrazoles; RNA, Small Interfering; Stem Cell Transplantation; Sulfonamides; Tolcapone

2021
The Ultrastructure of Tissue Damage by Amyloid Fibrils.
    Molecules (Basel, Switzerland), 2021, Jul-29, Volume: 26, Issue:15

    Topics: Alzheimer Disease; Amyloid; Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Humans; Immunoglobulin Light Chains; Immunoglobulin Light-chain Amyloidosis; Immunologic Factors; Myocardium; Neuroprotective Agents; Oligonucleotides; Peripheral Nerves; Prealbumin; Prion Diseases; RNA, Small Interfering

2021
Design and Rationale of the Phase 3 ATTR-ACT Clinical Trial (Tafamidis in Transthyretin Cardiomyopathy Clinical Trial).
    Circulation. Heart failure, 2017, Volume: 10, Issue:6

    Topics: Administration, Oral; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Clinical Trials, Phase III as Topic; Disease Management; Disease Progression; Humans; Randomized Controlled Trials as Topic

2017
Diagnosis and management of transthyretin familial amyloid polyneuropathy in Japan: red-flag symptom clusters and treatment algorithm.
    Orphanet journal of rare diseases, 2018, 01-17, Volume: 13, Issue:1

    Topics: Algorithms; Amyloid Neuropathies, Familial; Benzoxazoles; Carpal Tunnel Syndrome; Humans; Japan; Liver Transplantation; Methionine; Mutation; Valine

2018
An indirect treatment comparison of the efficacy of patisiran and tafamidis for the treatment of hereditary transthyretin-mediated amyloidosis with polyneuropathy.
    Expert opinion on pharmacotherapy, 2019, Volume: 20, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Polyneuropathies; Quality of Life; Randomized Controlled Trials as Topic; RNA, Small Interfering; Surveys and Questionnaires

2019
Tafamidis for the treatment of transthyretin amyloidosis.
    Future cardiology, 2019, Volume: 15, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Global Health; Heart Failure; Humans; Survival Rate

2019
Advances in the diagnosis and treatment of transthyretin amyloidosis with cardiac involvement.
    Heart failure reviews, 2019, Volume: 24, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Biomarkers; Cardiomyopathies; Diagnosis, Differential; Echocardiography; Electrocardiography; Humans; Magnetic Resonance Imaging; Oligonucleotides; Radionuclide Imaging; RNA, Small Interfering

2019
Treatment of hereditary and acquired forms of transthyretin amyloidosis in the era of personalized medicine: the role of randomized controlled trials.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2019, Volume: 26, Issue:2

    Topics: Amyloid Neuropathies; Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Female; Humans; Male; Oligonucleotides; Prealbumin; Precision Medicine; Randomized Controlled Trials as Topic; RNA, Small Interfering; Treatment Outcome

2019
Tafamidis: A Review in Transthyretin Amyloidosis with Polyneuropathy.
    Drugs, 2019, Volume: 79, Issue:8

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Clinical Trials as Topic; Disease Progression; Drug Approval; Humans; Mutation; Polyneuropathies; Prealbumin; Quality of Life

2019
Treatment of cardiac transthyretin amyloidosis: an update.
    European heart journal, 2019, 12-01, Volume: 40, Issue:45

    Topics: Amyloid; Amyloid Neuropathies; Amyloid Neuropathies, Familial; Benzoxazoles; Clinical Trials, Phase III as Topic; Combined Modality Therapy; Heart Failure; Heart Transplantation; Humans; Liver Transplantation; Mutation; Oligonucleotides; Prealbumin; RNA, Small Interfering; Stroke Volume

2019
Screening for Transthyretin Amyloid Cardiomyopathy in Everyday Practice.
    JACC. Heart failure, 2019, Volume: 7, Issue:8

    Topics: Age Factors; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Delayed Diagnosis; Diagnostic Errors; Early Diagnosis; Early Medical Intervention; Heart Failure; Humans; Stroke Volume

2019
[Familial amyloid polyneuropathies: therapeutic issues].
    Bulletin de l'Academie nationale de medecine, 2012, Volume: 196, Issue:7

    Topics: Amyloid Neuropathies, Familial; Antibodies, Monoclonal; Benzoxazoles; Clinical Trials as Topic; Diflunisal; Disease Progression; Doxycycline; Drug Therapy, Combination; Genetic Therapy; Heart Failure; Heart Transplantation; Humans; Kidney Failure, Chronic; Kidney Transplantation; Liver Transplantation; Myocardium; Oligonucleotides, Antisense; Renal Dialysis; RNA Interference; Serum Amyloid P-Component; Taurochenodeoxycholic Acid

2012
FAP neuropathy and emerging treatments.
    Current neurology and neuroscience reports, 2014, Volume: 14, Issue:3

    Topics: Amyloid Neuropathies, Familial; Animals; Benzoxazoles; Gene Silencing; Humans; Liver Transplantation; Mutation; Prealbumin

2014
Recent progress in the understanding and treatment of transthyretin amyloidosis.
    Journal of clinical pharmacy and therapeutics, 2014, Volume: 39, Issue:3

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Genetic Therapy; Humans; Liver Transplantation; Oligonucleotides, Antisense; Prealbumin; RNA, Small Interfering

2014
Tafamidis: a review of its use in familial amyloid polyneuropathy.
    Drugs, 2014, Volume: 74, Issue:12

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Humans

2014
Natural history and therapy of TTR-cardiac amyloidosis: emerging disease-modifying therapies from organ transplantation to stabilizer and silencer drugs.
    Heart failure reviews, 2015, Volume: 20, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Biomarkers; Cardiomyopathies; Cyclooxygenase Inhibitors; Defibrillators, Implantable; Diflunisal; Doxycycline; Heart Failure; Humans; Oligonucleotides, Antisense; Organ Transplantation; Pacemaker, Artificial; RNA, Small Interfering

2015
Transthyretin (ATTR) amyloidosis: clinical spectrum, molecular pathogenesis and disease-modifying treatments.
    Journal of neurology, neurosurgery, and psychiatry, 2015, Volume: 86, Issue:9

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Humans; Mutation; Prealbumin

2015
[Clinical diversity, diagnosis and treatment of hereditary amyloid neuropathy].
    Rinsho shinkeigaku = Clinical neurology, 2014, Volume: 54, Issue:12

    Topics: Adult; Age of Onset; Aged; Aged, 80 and over; Amyloid; Amyloid Neuropathies, Familial; Benzoxazoles; Diagnosis, Differential; Diflunisal; Early Diagnosis; Female; Genes, Dominant; Humans; Liver Transplantation; Male; Middle Aged; Mutation; Prealbumin

2014
The transthyretin amyloidoses: advances in therapy.
    Postgraduate medical journal, 2015, Volume: 91, Issue:1078

    Topics: Amyloid Neuropathies, Familial; Anti-Inflammatory Agents, Non-Steroidal; Benzoxazoles; Doxycycline; Echocardiography; Humans; Liver Transplantation; Molecular Targeted Therapy; Prealbumin; Prognosis; RNA, Small Interfering; Taurochenodeoxycholic Acid

2015
TTR kinetic stabilizers and TTR gene silencing: a new era in therapy for familial amyloidotic polyneuropathies.
    Expert opinion on pharmacotherapy, 2016, Volume: 17, Issue:6

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Clinical Trials, Phase III as Topic; Diflunisal; Disease Progression; Gene Silencing; Humans; Liver Transplantation; Prealbumin; Receptors, Albumin

2016
Tafamidis for transthyretin amyloidosis.
    Drugs of today (Barcelona, Spain : 1998), 2012, Volume: 48, Issue:5

    Topics: Amyloid Neuropathies, Familial; Animals; Benzoxazoles; Genotype; Humans; Mutation; Neuroprotective Agents; Prealbumin; Randomized Controlled Trials as Topic

2012

Trials

22 trial(s) available for benzoxazoles and Amyloid Neuropathy Type 1

ArticleYear
Annual Cardiovascular-Related Hospitalization Days Avoided with Tafamidis in Patients with Transthyretin Amyloid Cardiomyopathy.
    American journal of cardiovascular drugs : drugs, devices, and other interventions, 2022, Volume: 22, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Hospitalization; Humans; Prealbumin

2022
Estimating the Effect of Tafamidis on Cardiovascular-Related Hospitalization in NYHA Class III Patients with Transthyretin Amyloid Cardiomyopathy in the Presence of Death.
    Cardiology, 2022, Volume: 147, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Hospitalization; Humans; Prealbumin

2022
The Bioequivalence of Tafamidis 61-mg Free Acid Capsules and Tafamidis Meglumine 4 × 20-mg Capsules in Healthy Volunteers.
    Clinical pharmacology in drug development, 2020, Volume: 9, Issue:7

    Topics: Administration, Oral; Adult; Amyloid Neuropathies; Amyloid Neuropathies, Familial; Benzoxazoles; Brazil; Canada; Cardiomyopathies; Cross-Over Studies; Disease Progression; Dose-Response Relationship, Drug; Drug Administration Schedule; Drug Compounding; Fasting; Female; Healthy Volunteers; Humans; Japan; Male; Middle Aged; Prealbumin; Safety; Therapeutic Equivalency; United States

2020
Experience of patisiran with transthyretin stabilizers in patients with hereditary transthyretin-mediated amyloidosis.
    Neurodegenerative disease management, 2020, Volume: 10, Issue:5

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Female; Humans; Male; Middle Aged; Quality of Life; RNA, Small Interfering; Surveys and Questionnaires

2020
Efficacy and safety of tafamidis doses in the Tafamidis in Transthyretin Cardiomyopathy Clinical Trial (ATTR-ACT) and long-term extension study.
    European journal of heart failure, 2021, Volume: 23, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Prealbumin

2021
Impact of Tafamidis on Health-Related Quality of Life in Patients With Transthyretin Amyloid Cardiomyopathy (from the Tafamidis in Transthyretin Cardiomyopathy Clinical Trial).
    The American journal of cardiology, 2021, 02-15, Volume: 141

    Topics: Activities of Daily Living; Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Cost of Illness; Female; Humans; Male; Patient Reported Outcome Measures; Quality of Life; Self Efficacy; Social Participation

2021
Causes of Cardiovascular Hospitalization and Death in Patients With Transthyretin Amyloid Cardiomyopathy (from the Tafamidis in Transthyretin Cardiomyopathy Clinical Trial [ATTR-ACT]).
    The American journal of cardiology, 2021, 06-01, Volume: 148

    Topics: Aged; Amyloid Neuropathies, Familial; Amyloidosis; Arrhythmias, Cardiac; Benzoxazoles; Cardiomyopathies; Cardiovascular Diseases; Cause of Death; Death, Sudden, Cardiac; Double-Blind Method; Female; Heart Failure; Hospitalization; Humans; Ischemic Attack, Transient; Male; Myocardial Infarction; Prealbumin; Proportional Hazards Models; Stroke

2021
Health impact of tafamidis in transthyretin amyloid cardiomyopathy patients: an analysis from the Tafamidis in Transthyretin Cardiomyopathy Clinical Trial (ATTR-ACT) and the open-label long-term extension studies.
    European heart journal. Quality of care & clinical outcomes, 2022, 08-17, Volume: 8, Issue:5

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Prealbumin

2022
Tafamidis delays disease progression in patients with early stage transthyretin familial amyloid polyneuropathy: additional supportive analyses from the pivotal trial.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2017, Volume: 24, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Female; Humans; Male; Middle Aged; Polyneuropathies; Prealbumin; Treatment Outcome

2017
Transthyretin (ATTR) amyloidosis nephropathy: lessons from a TTR stabilizer molecule.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2017, Volume: 24, Issue:sup1

    Topics: Adult; Amyloid; Amyloid Neuropathies, Familial; Benzoxazoles; Biomarkers; Creatinine; Cystatin C; Drug Administration Schedule; Female; Gene Expression; Glomerular Filtration Rate; Humans; Kidney; Male; Middle Aged; Mutation; Nephritis; Prealbumin; Prospective Studies; Proteinuria

2017
Long-term safety and efficacy of tafamidis for the treatment of hereditary transthyretin amyloid polyneuropathy: results up to 6 years.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2017, Volume: 24, Issue:3

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Female; Humans; Longitudinal Studies; Male; Middle Aged; Quality of Life

2017
Tafamidis delays neurological progression comparably across Val30Met and non-Val30Met genotypes in transthyretin familial amyloid polyneuropathy.
    European journal of neurology, 2018, Volume: 25, Issue:3

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Double-Blind Method; Female; Genotype; Humans; Lower Extremity; Male; Middle Aged; Mutation; Treatment Outcome

2018
Tafamidis Treatment for Patients with Transthyretin Amyloid Cardiomyopathy.
    The New England journal of medicine, 2018, Sep-13, Volume: 379, Issue:11

    Topics: Administration, Oral; Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Disease Progression; Double-Blind Method; Female; Heart Failure; Hospitalization; Humans; Male; Middle Aged; Prealbumin; Quality of Life; Survival Analysis; Walk Test

2018
Tafamidis for transthyretin amyloid cardiomyopathy: the solution or just the beginning of the end?
    European heart journal, 2019, 03-21, Volume: 40, Issue:12

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Case-Control Studies; Echocardiography; Hospitalization; Humans; Mutation; Placebos; Prealbumin; Survival Analysis

2019
Effect on disability and safety of Tafamidis in late onset of Met30 transthyretin familial amyloid polyneuropathy.
    European journal of neurology, 2013, Volume: 20, Issue:12

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Humans; Middle Aged

2013
Long-term effects of tafamidis for the treatment of transthyretin familial amyloid polyneuropathy.
    Journal of neurology, 2013, Volume: 260, Issue:11

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Drug Administration Schedule; Female; Follow-Up Studies; Humans; International Cooperation; Male; Methionine; Middle Aged; Mutation; Prealbumin; Quality of Life; Time Factors; Valine; Young Adult

2013
Effects of tafamidis on transthyretin stabilization and clinical outcomes in patients with non-Val30Met transthyretin amyloidosis.
    Journal of cardiovascular translational research, 2013, Volume: 6, Issue:6

    Topics: Adult; Aged; Amyloid; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Europe; Female; Genetic Predisposition to Disease; Humans; Male; Middle Aged; Mutation; Phenotype; Prealbumin; Time Factors; Treatment Outcome; United States

2013
Cardiac findings and events observed in an open-label clinical trial of tafamidis in patients with non-Val30Met and non-Val122Ile hereditary transthyretin amyloidosis.
    Journal of cardiovascular translational research, 2015, Volume: 8, Issue:2

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Europe; Female; Fibrosis; Genetic Predisposition to Disease; Heart Failure; Humans; Male; Middle Aged; Mutation; Myocardium; Phenotype; Prealbumin; Risk Factors; Time Factors; Treatment Outcome; United States

2015
Tafamidis in transthyretin amyloid cardiomyopathy: effects on transthyretin stabilization and clinical outcomes.
    Circulation. Heart failure, 2015, Volume: 8, Issue:3

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Disease Progression; Drug Administration Schedule; Female; Humans; Male; Mutation; Myocardium; Prealbumin; Protein Folding; Protein Multimerization; Protein Stability; Protein Structure, Quaternary; Time Factors; Treatment Outcome; United States

2015
Effects of tafamidis treatment on transthyretin (TTR) stabilization, efficacy, and safety in Japanese patients with familial amyloid polyneuropathy (TTR-FAP) with Val30Met and non-Val30Met: A phase III, open-label study.
    Journal of the neurological sciences, 2016, Mar-15, Volume: 362

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Body Mass Index; Echocardiography; Female; Follow-Up Studies; Humans; Japan; Male; Methionine; Middle Aged; Pharmacogenetics; Prealbumin; Valine; Young Adult

2016
Early intervention with tafamidis provides long-term (5.5-year) delay of neurologic progression in transthyretin hereditary amyloid polyneuropathy.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2016, Volume: 23, Issue:3

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Anti-Inflammatory Agents, Non-Steroidal; Benzoxazoles; Double-Blind Method; Drug Administration Schedule; Female; Humans; Male; Middle Aged; Prospective Studies; Secondary Prevention

2016
Tafamidis for transthyretin familial amyloid polyneuropathy: a randomized, controlled trial.
    Neurology, 2012, Aug-21, Volume: 79, Issue:8

    Topics: Adolescent; Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Double-Blind Method; Humans; Male; Middle Aged; Neuroprotective Agents; Polymorphism, Single Nucleotide; Prealbumin; Quality of Life; Severity of Illness Index

2012

Other Studies

83 other study(ies) available for benzoxazoles and Amyloid Neuropathy Type 1

ArticleYear
Compassionate drug use for patients with transthyretin amyloid cardiomyopathy.
    Journal of cardiovascular medicine (Hagerstown, Md.), 2021, 10-01, Volume: 22, Issue:10

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathy, Restrictive; Compassionate Use Trials; Drug Approval; Drugs, Investigational; Heart Failure; Humans; Magnetic Resonance Imaging, Cine; Myocardial Perfusion Imaging; Treatment Outcome

2021
Tafamidis and quality of life in people with transthyretin amyloid cardiomyopathy in the study ATTR-ACT: A plain language summary.
    Future cardiology, 2022, Volume: 18, Issue:3

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Language; Prealbumin; Quality of Life

2022
Long-Term Survival With Tafamidis in Patients With Transthyretin Amyloid Cardiomyopathy.
    Circulation. Heart failure, 2022, Volume: 15, Issue:1

    Topics: Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Female; Heart Failure; Hospitalization; Humans; Male; Middle Aged; Prealbumin; Proportional Hazards Models; Time

2022
Clinical improvement after change of therapy from tafamidis to patisiran in progressive TTR amyloidosis post-liver transplantation.
    Journal of neurology, 2022, Volume: 269, Issue:7

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Liver Transplantation; Prealbumin; RNA, Small Interfering

2022
[Practice guideline for the treatment of familial amyloid polyneuropathy].
    Medicina, 2022, Volume: 82, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Prealbumin; Quality of Life; Treatment Outcome

2022
[Specific pharmacological treatment guide for transthyretin amyloid cardiomyopathy, 2021].
    Medicina, 2022, Volume: 82, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Diflunisal; Doxycycline; Humans; Prealbumin; Ursodeoxycholic Acid

2022
Tafamidis and its stabilizing effects on transthyretin tetramers, the heart and eventually, scientific evidence.
    European heart journal. Cardiovascular Imaging, 2022, 07-21, Volume: 23, Issue:8

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Myocardium; Prealbumin

2022
Early Experience of Tafamidis Treatment in Japanese Patients With Wild-Type Transthyretin Cardiac Amyloidosis From the Kochi Amyloidosis Cohort.
    Circulation journal : official journal of the Japanese Circulation Society, 2022, 06-24, Volume: 86, Issue:7

    Topics: Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Japan; Prealbumin; Stroke Volume; Ventricular Function, Left

2022
What is this image? 2022 image 1 result: radiologic improvement of transthyretin cardiac amyloidosis after treatment with tafamidis.
    Journal of nuclear cardiology : official publication of the American Society of Nuclear Cardiology, 2022, Volume: 29, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Prealbumin

2022
Response by Elliott et al to Letter Regarding Article, "Long-Term Survival With Tafamidis in Patients With Transthyretin Amyloid Cardiomyopathy".
    Circulation. Heart failure, 2022, Volume: 15, Issue:7

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Prealbumin

2022
Letter by Baldovino et al Regarding Article, "Long-Term Survival With Tafamidis in Patients With Transthyretin Amyloid Cardiomyopathy".
    Circulation. Heart failure, 2022, Volume: 15, Issue:7

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Prealbumin

2022
Understanding Changes in Functional Capacity After TTR Stabilization in Patients With Transthyretin Cardiac Amyloidosis.
    Circulation. Heart failure, 2022, Volume: 15, Issue:7

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Prealbumin

2022
Redefining Prognosis of Transthyretin Cardiomyopathy in the Tafamidis Era.
    Journal of cardiac failure, 2022, Volume: 28, Issue:10

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Prealbumin; Prognosis

2022
Tafamidis polyneuropathy amelioration requires modest increases in transthyretin stability even though increases in plasma native TTR and decreases in non-native TTR do not predict response.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2023, Volume: 30, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Male; Polyneuropathies; Prealbumin

2023
Regression of left ventricular hypertrophy after tafamidis therapy in a patient with transthyretin amyloidosis variant.
    The journal of medical investigation : JMI, 2022, Volume: 69, Issue:3.4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Hypertrophy, Left Ventricular; Prealbumin

2022
Relationship of binding-site occupancy, transthyretin stabilisation and disease modification in patients with tafamidis-treated transthyretin amyloid cardiomyopathy.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2023, Volume: 30, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Disease Progression; Humans; Prealbumin

2023
Tafamidis concentration required for transthyretin stabilisation in cerebrospinal fluid.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2023, Volume: 30, Issue:3

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Prealbumin

2023
Comparison between tafamidis and liver transplantation as first-line therapy for hereditary transthyretin amyloidosis.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2023, Volume: 30, Issue:3

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Liver Transplantation; Middle Aged; Prealbumin; Retrospective Studies

2023
New Drugs Treat Rare Heart Disease Caused by Transthyretin-Mediated Amyloidosis.
    The American journal of nursing, 2019, Volume: 119, Issue:9

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Heart Diseases; Humans

2019
Biophysical characterization and modulation of Transthyretin Ala97Ser.
    Annals of clinical and translational neurology, 2019, Volume: 6, Issue:10

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Binding Sites; Biophysical Phenomena; Calorimetry; Humans; Magnetic Resonance Spectroscopy; Mutation; Prealbumin

2019
Transthyretin Amyloidosis with Gastrointestinal Manifestation: a Case Report.
    Journal of gastrointestinal and liver diseases : JGLD, 2019, Sep-01, Volume: 28, Issue:3

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Chronic Disease; Diagnosis, Differential; Diarrhea; DNA Mutational Analysis; Genetic Predisposition to Disease; Humans; Male; Middle Aged; Mutation; Prealbumin; Predictive Value of Tests

2019
A Statement on the Appropriate Administration of Tafamidis in Patients With Transthyretin Cardiac Amyloidosis.
    Circulation journal : official journal of the Japanese Circulation Society, 2019, 12-25, Volume: 84, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans

2019
Advantages and Emerging Problems of Novel Treatments for Transthyretin Cardiac Amyloidosis.
    Circulation journal : official journal of the Japanese Circulation Society, 2019, 12-25, Volume: 84, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Prealbumin

2019
Tafamidis-A Pricey Therapy for a Not-So-Rare Condition.
    JAMA cardiology, 2020, 03-01, Volume: 5, Issue:3

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cost-Benefit Analysis; Drug Approval; Health Policy; Humans; Randomized Controlled Trials as Topic; United States

2020
Hereditary transthyretin amyloidosis caused by the rare Phe33Leu mutation.
    BMJ case reports, 2020, Jan-12, Volume: 13, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Combined Modality Therapy; Diagnosis, Differential; Heart Transplantation; Humans; Leucine; Male; Middle Aged; Mutation; Phenylalanine; Prealbumin

2020
Tafamidis: a selective transthyretin stabilizer to treat wild-type ATTR amyloidosis and hereditary ATTR amyloidosis with cardiomyopathy.
    Drugs of today (Barcelona, Spain : 1998), 2019, Volume: 55, Issue:12

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Prealbumin

2019
Cost-Effectiveness of Tafamidis Therapy for Transthyretin Amyloid Cardiomyopathy.
    Circulation, 2020, 04-14, Volume: 141, Issue:15

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Cost-Benefit Analysis; Female; Humans; Male; Quality of Life

2020
Initial Monthly Cost of Tafamidis-the Real Price for Patients.
    JAMA cardiology, 2020, 07-01, Volume: 5, Issue:7

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans

2020
Initial Monthly Cost of Tafamidis-the Real Price for Patients-Reply.
    JAMA cardiology, 2020, 07-01, Volume: 5, Issue:7

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans

2020
[Experience with tafamidis in a patient with transthyretin amyloidosis].
    Kardiologiia, 2020, Jan-20, Volume: 60, Issue:3

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Prealbumin

2020
Motor excitability measurements in early stage familial amyloid polyneuropathy: The influence of tafamidis treatment.
    Neurophysiologie clinique = Clinical neurophysiology, 2020, Volume: 50, Issue:3

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Female; Humans; Male; Median Nerve; Nerve Fibers; Neural Conduction; Neuroprotective Agents; Treatment Outcome

2020
Characteristics of Patients with Hereditary Transthyretin Amyloidosis and an Evaluation of the Safety of Tafamidis Meglumine in Japan: An Interim Analysis of an All-case Postmarketing Surveillance.
    Clinical therapeutics, 2020, Volume: 42, Issue:9

    Topics: Adolescent; Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Female; Humans; Japan; Male; Middle Aged; Young Adult

2020
Blinded potency comparison of transthyretin kinetic stabilisers by subunit exchange in human plasma.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2021, Volume: 28, Issue:1

    Topics: Amyloid; Amyloid Neuropathies, Familial; Benzoates; Benzoxazoles; Cardiomyopathies; Diflunisal; Humans; Kinetics; Prealbumin; Protein Aggregates; Protein Binding; Protein Multimerization; Protein Subunits; Pyrazoles; Tolcapone

2021
Conventional Molecular Dynamics and Metadynamics Simulation Studies of the Binding and Unbinding Mechanism of TTR Stabilizers AG10 and Tafamidis.
    ACS chemical neuroscience, 2020, 10-07, Volume: 11, Issue:19

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Molecular Dynamics Simulation; Prealbumin

2020
Response by Kazi et al to Letter Regarding Article, "Cost-Effectiveness of Tafamidis Therapy for Transthyretin Amyloid Cardiomyopathy".
    Circulation, 2020, 10-13, Volume: 142, Issue:15

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Cost-Benefit Analysis; Humans; Prealbumin

2020
Letter by Rozenbaum et al Regarding Article, "Cost-Effectiveness of Tafamidis Therapy for Transthyretin Amyloid Cardiomyopathy".
    Circulation, 2020, 10-13, Volume: 142, Issue:15

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Cost-Benefit Analysis; Humans; Prealbumin

2020
Natural history and impact of treatment with tafamidis on major cardiovascular outcome-free survival time in a cohort of patients with transthyretin amyloidosis.
    European journal of heart failure, 2021, Volume: 23, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; France; Heart Failure; Humans

2021
Population pharmacokinetic modelling and simulation of tafamidis in healthy subjects and patients with transthyretin amyloidosis.
    British journal of clinical pharmacology, 2021, Volume: 87, Issue:9

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Healthy Volunteers; Humans

2021
Estimating the annual economic burden for the management of patients with transthyretin amyloid polyneuropathy in Spain.
    Expert review of pharmacoeconomics & outcomes research, 2021, Volume: 21, Issue:5

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cost of Illness; Drug Costs; Health Care Costs; Hospitalization; Humans; Oligonucleotides; RNA, Small Interfering; Spain

2021
Modeling of Survival and Frequency of Cardiovascular-Related Hospitalization in Patients with Transthyretin Amyloid Cardiomyopathy Treated with Tafamidis.
    American journal of cardiovascular drugs : drugs, devices, and other interventions, 2021, Volume: 21, Issue:5

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Hospitalization; Humans; Models, Statistical; Survival Analysis

2021
[Update of tafamidis for the treatment of transthyretin cardiac amyloidosis].
    Zhonghua xin xue guan bing za zhi, 2021, Apr-24, Volume: 49, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Prealbumin

2021
False Positive 99mTc-Pyrophosphate Scanning Leading to Inappropriate Tafamidis Prescriptions.
    JACC. Cardiovascular imaging, 2021, Volume: 14, Issue:10

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Predictive Value of Tests; Prescriptions; Technetium Tc 99m Pyrophosphate

2021
Factors associated with changes in serum transthyretin after treatment with tafamidis and outcomes in transthyretin cardiac amyloidosis.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2021, Volume: 28, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Prealbumin

2021
Discredited legacy: Stigma and familial amyloid polyneuropathy in Northwestern Portugal.
    Social science & medicine (1982), 2017, Volume: 182

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Female; Genetic Diseases, Inborn; Humans; Male; Middle Aged; Portugal; Qualitative Research; Reproductive Behavior; Social Stigma; Surveys and Questionnaires

2017
Disruption of blood-nerve barriers in hereditary transthyretin (ATTR) amyloidosis.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2017, Volume: 24, Issue:sup1

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Cell Survival; Female; Humans; Male; Middle Aged; Mutation; Plasma

2017
Pharmacokinetics of tafamidis, a transthyretin amyloidosis drug, in rats.
    Xenobiotica; the fate of foreign compounds in biological systems, 2018, Volume: 48, Issue:8

    Topics: Amyloid Neuropathies, Familial; Animals; Benzoxazoles; Brain; Caco-2 Cells; Humans; Liver; Male; Microsomes, Liver; Organ Specificity; Rats; Rats, Sprague-Dawley

2018
Amyloid Polyneuropathy and Myocardial Amyloidosis 10 Years after Domino Liver Transplantation from a Patient with a Transthyretin Ser50Arg Mutation.
    Internal medicine (Tokyo, Japan), 2017, Dec-01, Volume: 56, Issue:23

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cysts; Humans; Liver Diseases; Liver Transplantation; Male; Middle Aged; Mutation; Prealbumin; Treatment Outcome

2017
Unwanted road to anaemia in transthyretin familial amyloid polyneuropathy may continue irrespective of tafamidis treatment.
    Annals of clinical biochemistry, 2018, Volume: 55, Issue:5

    Topics: Amyloid Neuropathies, Familial; Anemia; Benzoxazoles; Blood Chemical Analysis; Disease Progression; Female; Humans; Longitudinal Studies; Male; Middle Aged; Retrospective Studies

2018
Failure of Tafamidis to Halt Progression of Ala36Pro TTR Oculomeningovascular Amyloidosis.
    Journal of stroke and cerebrovascular diseases : the official journal of National Stroke Association, 2018, Volume: 27, Issue:9

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Blindness; Brain Ischemia; Cerebrovascular Disorders; Disease Progression; Eye Diseases; Female; Genetic Predisposition to Disease; Humans; Intracranial Hemorrhages; Magnetic Resonance Imaging; Mutation; Phenotype; Prealbumin; Siderosis; Treatment Failure; Ultrasonography

2018
Hereditary amyloidosis related to transthyretin V30M: disease progression in treated and untreated patients.
    European journal of neurology, 2018, Volume: 25, Issue:11

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Female; Humans; Liver Transplantation; Male; Middle Aged; Neural Conduction; Polyneuropathies; Time Factors; Treatment Outcome

2018
Cerebrospinal fluid and vitreous body exposure to orally administered tafamidis in hereditary ATTRV30M (p.TTRV50M) amyloidosis patients.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2018, Volume: 25, Issue:2

    Topics: Administration, Oral; Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Cerebrospinal Fluid; Chromatography, High Pressure Liquid; Female; Humans; Liver Transplantation; Male; Mutation; Prealbumin; Vitreous Body

2018
[What gnaws at the heart and gets on the nerves].
    Der Internist, 2018, Volume: 59, Issue:11

    Topics: Aged; Amyloid; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Drug Approval; Humans; Middle Aged; Mutation; Polyneuropathies; Prealbumin; Quality of Life

2018
Transthyretin Stabilizer Is Associated With Expanding Apical Sparing Area and Improving Global Cardiac Function in a Patient With Wild-Type Cardiac Amyloidosis.
    Circulation journal : official journal of the Japanese Circulation Society, 2019, 02-25, Volume: 83, Issue:3

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart; Humans; Magnetic Resonance Angiography; Male; Treatment Outcome

2019
Natural history and survival in stage 1 Val30Met transthyretin familial amyloid polyneuropathy.
    Neurology, 2018, 11-20, Volume: 91, Issue:21

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Female; Follow-Up Studies; Humans; Liver Transplantation; Male; Middle Aged

2018
Brazilian consensus for diagnosis, management and treatment of transthyretin familial amyloid polyneuropathy.
    Arquivos de neuro-psiquiatria, 2018, Volume: 76, Issue:9

    Topics: Amyloid Neuropathies, Familial; Animals; Benzoxazoles; Brazil; Cardiomyopathies; Diagnosis, Differential; Humans; Oligonucleotides; Randomized Controlled Trials as Topic; RNA, Small Interfering

2018
Monitoring treatment response to tafamidis by serial native T1 and extracellular volume in transthyretin amyloid cardiomyopathy.
    ESC heart failure, 2019, Volume: 6, Issue:1

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Biopsy; Cardiomyopathies; Electrocardiography; Follow-Up Studies; Humans; Magnetic Resonance Imaging, Cine; Male; Myocardium

2019
Hereditary cardiac amyloidosis associated with Pro24Ser transthyretin mutation: a case report.
    Journal of medical case reports, 2018, Dec-16, Volume: 12, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Diuretics; Echocardiography; Genes, Dominant; Humans; Male; Middle Aged; Mutation; Prealbumin; Radionuclide Imaging; Treatment Outcome

2018
Tafamidis for Transthyretin Amyloid Cardiomyopathy.
    The New England journal of medicine, 2019, 01-10, Volume: 380, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Prealbumin

2019
Tafamidis for Transthyretin Amyloid Cardiomyopathy.
    The New England journal of medicine, 2019, 01-10, Volume: 380, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Prealbumin

2019
Transthyretin deposition in the eye in the era of effective therapy for hereditary ATTRV30M amyloidosis.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2019, Volume: 26, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Eye Diseases; Humans; Mutation, Missense; Prealbumin; Protein Aggregation, Pathological

2019
Electrochemical skin conductance in hereditary amyloidosis related to transthyretin V30M - a promising tool to assess treatment efficacy?
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2018, Volume: 25, Issue:4

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Case-Control Studies; Electrochemical Techniques; Female; Follow-Up Studies; Galvanic Skin Response; Humans; Male; Middle Aged; Mutation; Neural Conduction; Prealbumin; Prognosis; Prospective Studies

2018
Tafamidis dramatically improved severe proteinuria in a patient with TTR V30M hereditary ATTR amyloidosis.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2019, Volume: 26, Issue:2

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Male; Middle Aged; Mutation, Missense; Prealbumin; Proteinuria; Treatment Outcome

2019
Letter to the editor concerning the article: "An indirect treatment comparison of the efficacy of patisiran and tafamidis for the treatment of hereditary transthyretin-mediated amyloidosis with polyneuropathy".
    Expert opinion on pharmacotherapy, 2019, Volume: 20, Issue:12

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Polyneuropathies; Prealbumin; RNA, Small Interfering

2019
Response to the letter to the editor on "an indirect treatment comparison of the efficacy of patisiran and tafamidis for the treatment of hereditary transthyretin-mediated amyloidosis with polyneuropathy".
    Expert opinion on pharmacotherapy, 2019, Volume: 20, Issue:12

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Polyneuropathies; Prealbumin; RNA, Small Interfering

2019
[The ATTR-ACT trial].
    Giornale italiano di cardiologia (2006), 2019, Volume: 20, Issue:6

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Multicenter Studies as Topic; Randomized Controlled Trials as Topic

2019
Predictive model of response to tafamidis in hereditary ATTR polyneuropathy.
    JCI insight, 2019, 06-20, Volume: 4, Issue:12

    Topics: Adult; Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Biomarkers; Cohort Studies; Demography; Female; Humans; Longitudinal Studies; Male; Middle Aged; Models, Biological; Prealbumin; Sex Factors; Treatment Outcome; Young Adult

2019
Real-world versus trial patients with transthyretin amyloid cardiomyopathy.
    European journal of heart failure, 2019, Volume: 21, Issue:11

    Topics: Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Angiotensin-Converting Enzyme Inhibitors; Benzoxazoles; Cardiomyopathies; Cardiovascular Agents; Clinical Trials as Topic; Diuretics; Female; Humans; Male; Rare Diseases

2019
Tafamidis for transthyretin familial amyloid polyneuropathy: a randomized, controlled trial.
    Neurology, 2013, Apr-09, Volume: 80, Issue:15

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Male; Neuroprotective Agents; Prealbumin

2013
Tafamidis (Vyndaqel): a light for FAP patients.
    ChemMedChem, 2013, Volume: 8, Issue:10

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Binding Sites; Drug Design; Humans; Mutation; Prealbumin; Protein Binding; Protein Structure, Tertiary

2013
[Newly developed drug therapies for familial amyloid polyneuropathy: diflunisal and tafamidis].
    Brain and nerve = Shinkei kenkyu no shinpo, 2014, Volume: 66, Issue:7

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Humans; Liver Transplantation; Molecular Targeted Therapy; Prealbumin; Protein Multimerization

2014
A woman with a rare p.Glu74Gly transthyretin mutation presenting exclusively with a rapidly progressive neuropathy: a case report.
    Journal of medical case reports, 2014, Dec-04, Volume: 8

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Fatal Outcome; Female; Genetic Linkage; Glutamic Acid; Glycine; Humans; Liver Transplantation; Mutation, Missense; Pedigree; Prealbumin

2014
Effects of liver transplantation and tafamidis in hereditary transthyretin amyloidosis caused by transthyretin Leu55Pro mutation: a case report.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2015, Volume: 22, Issue:3

    Topics: Adult; Amino Acid Substitution; Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Hypesthesia; Liver Transplantation; Male; Muscle Weakness; Mutation; Neuroprotective Agents; Prealbumin

2015
Personalized medicine approach for optimizing the dose of tafamidis to potentially ameliorate wild-type transthyretin amyloidosis (cardiomyopathy).
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2015, Volume: 22, Issue:3

    Topics: Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Drug Dosage Calculations; Drug Monitoring; Escherichia coli; Gene Expression; Humans; Kinetics; Male; Neuroprotective Agents; Prealbumin; Precision Medicine; Protein Stability; Recombinant Proteins

2015
Monitoring effectiveness and safety of Tafamidis in transthyretin amyloidosis in Italy: a longitudinal multicenter study in a non-endemic area.
    Journal of neurology, 2016, Volume: 263, Issue:5

    Topics: Adult; Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Female; Follow-Up Studies; Humans; Italy; Longitudinal Studies; Male; Middle Aged; Mutation; Prealbumin; Prognosis; Severity of Illness Index; Treatment Outcome

2016
Preclinical evaluation of RNAi as a treatment for transthyretin-mediated amyloidosis.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2016, Volume: 23, Issue:2

    Topics: Amyloid Neuropathies, Familial; Animals; Anti-Inflammatory Agents, Non-Steroidal; Benzoxazoles; Disease Models, Animal; Drug Evaluation, Preclinical; Female; Gene Expression; Humans; Liver; Macaca fascicularis; Male; Mice; Mice, Transgenic; Prealbumin; RNA Interference; RNA, Messenger; RNA, Small Interfering

2016
[Presentations of transthyretin associated familial amyloid polyneuropathy in Argentina].
    Medicina, 2016, Volume: 76, Issue:2

    Topics: Adult; Amyloid Neuropathies, Familial; Argentina; Benzoxazoles; Fatal Outcome; Female; Humans; Liver Transplantation; Male; Middle Aged; Mutation; Prealbumin; Retrospective Studies

2016
Peripheral Blood Cell Gene Expression Diagnostic for Identifying Symptomatic Transthyretin Amyloidosis Patients: Male and Female Specific Signatures.
    Theranostics, 2016, Volume: 6, Issue:11

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Biomarkers; Blood Cells; Cohort Studies; Female; Gene Expression; Gene Expression Profiling; Heterozygote; Humans; Inflammation; Male; Prealbumin; RNA; Sex Characteristics

2016
Tafamidis in hereditary ATTR amyloidosis - our experience on monitoring the ocular manifestations.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2016, Volume: 23, Issue:4

    Topics: Amyloid; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Female; Humans; Iris; Male; Middle Aged; Optic Disk; Prealbumin; Protein Aggregates; Retinal Pigment Epithelium; Vitreous Body

2016
Long-term treatment of transthyretin familial amyloid polyneuropathy with tafamidis: a clinical and neurophysiological study.
    Journal of neurology, 2017, Volume: 264, Issue:2

    Topics: Adult; Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Body Mass Index; Disease Progression; Female; Follow-Up Studies; Hematologic Agents; Humans; Male; Middle Aged; Neural Conduction; Time Factors; Treatment Outcome

2017
Treatment of transthyretin familial amyloid polyneuropathy with tafamidis: a case report.
    Nihon Ronen Igakkai zasshi. Japanese journal of geriatrics, 2017, Volume: 54, Issue:1

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Male

2017
[Treatment of familial amyloid polyneuropathy].
    Presse medicale (Paris, France : 1983), 2012, Volume: 41, Issue:9 Pt 1

    Topics: Amyloid; Amyloid Neuropathies, Familial; Arrhythmias, Cardiac; Benzoxazoles; Early Diagnosis; Follow-Up Studies; Heart Transplantation; Humans; Kidney Transplantation; Liver Transplantation; Mutation; Prealbumin; Quality of Life; RNA Interference; RNA, Small Interfering

2012
A designer drug for amyloid polyneuropathy.
    Neurology, 2012, Aug-21, Volume: 79, Issue:8

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Male; Neuroprotective Agents; Prealbumin

2012
Is it better than it seems or just good enough? The tafamidis saga.
    Muscle & nerve, 2012, Volume: 46, Issue:6

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Mutation; Neuroprotective Agents; Prealbumin

2012