Page last updated: 2024-08-21

benzoxazoles and Amyloid Neuropathies, Familial

benzoxazoles has been researched along with Amyloid Neuropathies, Familial in 140 studies

Research

Studies (140)

TimeframeStudies, this research(%)All Research%
pre-19900 (0.00)18.7374
1990's0 (0.00)18.2507
2000's0 (0.00)29.6817
2010's80 (57.14)24.3611
2020's60 (42.86)2.80

Authors

AuthorsStudies
Barbarossa, A; Capucci, A; Casella, M; Ciliberti, G; Dello Russo, A; Falanga, U; Guerra, F; Principi, S; Silenzi, M; Stronati, G; Urbinati, A1
Damy, T; Grogan, M; Gundapaneni, B; Hanna, M; Maurer, MS; Stewart, M; Sultan, MB1
Drachman, BM; Ebede, B; Elliott, P; Gottlieb, SS; Gundapaneni, B; Hoffman, JE; Hummel, SL; Lenihan, DJ; Li, B; Shah, SJ; Sultan, MB2
Brogneaux, C; Grayet, D; Jackers, L; Lacremans, D; Legrand, D; Magnée, M; Nyssen, A; Pirotte, I1
Assmus, B; Bulinski, C; Discher, T; Krämer, HH; Rutsatz, W1
Bhambri, R; Nativi-Nicolau, J; Rozenbaum, MH; Tran, D1
Aguirre, MA; Calandra, CR; Carretero, M; Conti, E; Lautre, A; León-Cejas, L; Negro, A; Nucifora, EM; Posadas-Martínez, ML; Reisin, R; Rugiero, M; Sáez, MS; Salutto, V; Sorroche, P1
Aguirre, MA; Baratta, S; Belziti, CA; Carretero, M; Costabel, JP; Dumont, CA; Fernández, A; Higa, C; Negro, A; Nucifora, EM; Perez de Arenaza, D; Posadas-Martínez, ML; Quiroga, A; Rivas, C; Streitenberg, GM; Villanueva, E; Volberg, VI1
Bonderman, D; Rettl, R1
Baba, Y; Hamada, T; Hirota, T; Kitaoka, H; Kubo, T; Miyagawa, K; Noguchi, T; Ochi, Y; Sugiura, K; Yamasaki, N1
Gomez-Valencia, J; Malhotra, S; Mekritthikrai, R1
Elliott, P; Gundapaneni, B; Sultan, MB1
Baldovino, S; Costanzo, P; Roccatello, D1
Cuddy, SAM1
Casey, M; Li, H; Rozenbaum, M; Sultan, MB1
Mitchell, JD; Rater, M; Schiffer, W; Zaghlol, R1
Balasubramanian, SS; Gaznabi, S; Hussain, K; Iqbal, SH; Kwak, E; Macrinici, V; Minga, I; Pursnani, A; Sarswat, N; Wang, CH; Wathen, L1
Anselmo, J; Coelho, T; Fernandes, J; Kelly, JW; Mesgarzadeh, JS; Monteiro, C; Novais, M; Powers, DL; Powers, ET; Rodrigues, C1
Fukuda, D; Hara, T; Ise, T; Kadota, M; Kawabata, Y; Kusunose, K; Matsuura, T; Osaki, Y; Saijo, Y; Sata, M; Soeki, T; Tserensonom, M; Ueno, R; Wakatsuki, T; Yagi, S; Yamada, H; Yamaguchi, K; Yamazaki, H1
Bulawa, C; Fleming, J; Li, Z; Maurer, TS; Moody, AT; Tess, DA1
Coelho, T; Jaeger, M; Kelly, JW; Powers, ET; Tsai, FJ1
Adams, D; Algalarrondo, V; Benmalek, A; Cauquil, C; Echaniz-Laguna, A; Eliahou, L; Kounis, I; Piekarski, E; Rousseau, A; Rouzet, F; Samuel, D; Slama, MS; Socie, P1
Czepluch, F1
Cruz, MW1
Aschenbrenner, DS1
Chang, Y; Huang, SJ; Lin, KP; Liu, YT; Ricardo, F; Wu, PH; Yen, YJ; Yu, TY1
Gospodinova, M; Kirov, A; Nakov, R; Nakov, V; Sarafov, S; Todorov, T; Todorova, A; Tournev, I1
Ando, Y; Endo, J; Fukuda, K; Inomata, T; Isobe, M; Izumiya, Y; Kuwahara, K; Nakamura, K; Sano, M; Sekijima, Y; Tahara, N; Tsujita, K; Tsutsui, H; Ueda, M1
Murohara, T; Okumura, T1
Gurwitz, JH; Maurer, MS2
Björkenheim, A; Szabó, B; Sztaniszláv, ÁJ1
Paton, DM1
Maurer, MS; Rubin, J1
Amass, L; Cameron, C; Salvo, EM; Samjoo, IA; Stewart, M; Tran, D1
Arnold, SV; Baron, SJ; Bellows, BK; Cohen, DJ; Kazi, DS; Maurer, MS; Shah, SJ; Shen, C; Sperry, BW; Spertus, JA; Yeh, RW2
Le, VH; Lockwood, PA; O'Gorman, MT; Patterson, TA; Riley, S; Sultan, MB; Tankisheva, E; Wang, Q1
Cavallaro, T; Fabrizi, GM; Magrinelli, F; Manganelli, F; Santoro, L; Tamburin, S; Zanette, G1
Coyle, ML; Cuddy, SAM; Falk, RH1
Magomedov, MM; Nasonova, SN; Osmolovskaya, YF; Saidova, MA; Tereschenko, SN; Zhirov, IV1
Brum, M; Caetano, A; Casanova, I; Conceição, I; de Carvalho, M; Díaz, A1
Hale, C; Lin, H; Marantz, JL; Merkel, M1
Cristóbal Gutiérrez, H; Gómez Gómez, D; Martín Vega, MÁ; Pelayo-Negro, AL; Valero Domínguez, M1
Adams, D; Slama, M1
Ando, Y; Hirano, Y; Ishii, T; Matsumoto, N; Sekijima, Y; Takata, A; Ueda, M1
Kelly, JW; Nelson, LT; Paxman, RJ; Powers, ET; Webb, B; Xu, J1
Audia, S; Damy, T; Eicher, JC1
Dou, Y; Ge, S; Lo, GV; Yuan, S; Zhang, Q; Zhang, W; Zhou, S1
Almeida, AR; Azevedo, O; Bento, D; Correia, E; Cruz, I; Lopes, LR; Lourenço, C; Marques, N1
Kemner, J; Parasuraman, B; Rozenbaum, MH1
Damy, T; Garcia-Pavia, P; Gundapaneni, B; Hanna, M; Judge, DP; Merlini, G; Patterson, TA; Riley, S; Schwartz, JH; Sultan, MB; Witteles, R1
Abulizi, M; Audard, V; Bézard, M; Canoui-Poitrine, F; Damy, T; Deux, JF; El Karoui, K; Fanen, P; Funalot, B; Galat, A; Gendre, T; Guendouz, S; Itti, E; Kharoubi, M; Lefaucheur, JP; Moktefi, A; Oghina, S; Planté-Bordeneuve, V; Poullot, E; Teiger, E; Zaroui, A1
Damy, T; Grogan, M; Gundapaneni, B; Hanna, M; Maurer, MS; Patterson, TA; Schwartz, JH; Stewart, M; Sultan, MB1
Harnisch, L; Huh, Y; Nicholas, T; Riley, S1
Benbrahim, M; Hughes, D; Norman, K; Sanchorawala, V; Siddiqi, OK1
Gundapaneni, B; Januzzi, JL; López-Sendón, J; Miller, AB; O'Neill, BJ; Patterson, TA; Sultan, MB1
Galan, L; Gonzalez-Moreno, J; Lebeau, P; Mallaina, P; Martínez-Sesmero, JM; Muñoz-Beamud, F; Peral, C; Rozenbaum, MH; Santos-Rubio, MD; Stewart, M; Tarilonte, P; Tran, D1
Kittleson, MM; Stern, LK1
Boucher, M; Harnisch, LO; Riley, S; Vong, C1
Tian, Z; Zhang, SY1
Bhambri, R; Garcia, A; Grima, D; Heeg, B; Li, B; Masri, A; Postma, M; Rozenbaum, MH; Stewart, M; Tran, D1
Griffin, JM; Maurer, MS; Rosenblum, H1
DeLuca, A; Einstein, AJ; Elias, P; Griffin, JM; Johnson, LL; Kinkhabwala, M; Maurer, MS; Pandey, S; Poterucha, TJ; Ruberg, FL1
Katsuno, M; Koike, H1
Gamino, D; Goldsmith, J; Griffin, JM; Guadalupe, S; Helmke, S; Maurer, MS; Rosenblum, HR; Saith, SE; Santos, JL; Teruya, S1
Amass, L; Gundapaneni, B; Keohane, D; Schwartz, J; Stewart, M1
Clarke, A; Mendes, Á; Sequeiros, J; Sousa, L1
Ando, Y; Iijima, M; Ikeda, S; Ikeda, SI; Katsuno, M; Kawagashira, Y; Koike, H; Misumi, Y; Sobue, G; Takahashi, M1
Alves, C; Beirão, I; Cardoso, M; Coelho, T; Lobato, L; Rocha, A; Silva, A; Teles, P1
Cruz, MW; Elliott, P; Flynn, A; Gundapaneni, B; Hahn, C; Maurer, MS; Merlini, G; Rapezzi, C; Riley, S; Schwartz, J; Shah, SJ; Sultan, MB1
Amass, L; Barroso, FA; Ebede, B; Judge, DP; Li, H; Stewart, M; Sultan, MB1
Ahn, S; Choi, S; Hyun, HC; Jang, E; Jeong, JW; Joo, SH; Kim, S; Koo, TS; Lee, KR1
Matsushima, M; Sakakibara, M; Sasaki, H; Shimamura, T; Tsuda, M; Yabe, I1
Gundapaneni, BK; Keohane, DJ; Schwartz, JH; Sultan, MB1
Ando, Y; Ikeda, T; Masuda, T; Misumi, Y; Shinriki, S; Ueda, M; Yamashita, T1
Ando, Y; Ishii, T; Koike, H; Misawa, S; Sekijima, Y; Ueda, M1
Bianchi, A; Mascalchi, M; Pastorelli, F; Rapezzi, C; Salvi, F; Vella, A; Volpe, R1
Castro, J; Conceição, I; de Carvalho, M; Miranda, B1
Coelho, T; Ferreira, N; Kelly, JW; Martins da Silva, A; Mesgarzadeh, J; Monteiro, C; Novais, M1
Kristen, AV1
Barsdorf, AI; Damy, T; Drachman, BM; Elliott, PM; Grogan, M; Gundapaneni, B; Hanna, M; Huber, P; Judge, DP; Kristen, AV; Maurer, MS; Merlini, G; Patterson, TA; Rapezzi, C; Riley, S; Schumacher, J; Schwartz, JH; Shah, SJ; Stewart, M; Sultan, MB; Waddington-Cruz, M; Witteles, R1
Ando, Y; Ikeda, N; Kato, TS; Maurer, MS; Tanno, K1
Coelho, T; Conceição, I; Costa, J; de Carvalho, M; Inês, M; Soares, M1
Barreira, AA; Bulle, AS; França, MC; Freitas, MRG; Gondim, FAA; Marques, W; Marrone, CD; Nascimento, OJM; Pinto, MV; Pupe, C; Rotta, FT; Waddington-Cruz, M1
Amaki, M; Amano, M; Hamatani, Y; Hasegawa, T; Ishibashi-Ueda, H; Izumi, C; Kanzaki, H; Morita, Y; Ohta-Ogo, K; Okada, A; Sekijima, Y; Shimazaki, C; Shintani, Y; Takahama, H; Yasuda, S; Yazaki, M; Yoshinaga, T1
Agarwal, S; Betts, M; Chitnis, M; Fahrbach, K; Gollob, J; Lin, H; Planté-Bordeneuve, V; Polydefkis, M1
Ando, Y; Hashimoto, T; Hiroe, M; Kawamura, S; Yamamoto, H; Yamashita, T; Yokochi, T1
Maurer, MS; Rapezzi, C; Sultan, MB1
Manion, C; Sharma, UC1
Falk, RH1
Brannagan, T; Buades-Reinés, J; Buxbaum, JN; Cisneros, E; Conceicao, I; Imai, A; Kyriakides, T; Merlini, G; Obici, L; Plante-Bordeneuve, V; Rousseau, A; Sekijima, Y; Waddington Cruz, M; Yamada, M1
Elliott, PM; Lorenzini, M1
Castro, J; Conceição, I; Costa, J; de Castro, I1
Abate, E; Ali, M; Bigalke, B; de Vecchis, R; Mammadov, M; Matiakis, M; Mavrogeni, S; Melnyk, H; Noutsias, M; Rigopoulos, AG; Torky, AR; Vogt, A; Wohlgemuth, W1
Buxbaum, JN1
Hineno, A; Ichikawa, T; Ikeda, SI; Makino, M1
Deeks, ED; Lamb, YN1
Aimo, A; Barison, A; Castiglione, V; Emdin, M; Fontana, M; Giannoni, A; Merlini, G; Passino, C; Perfetto, F; Rapezzi, C; Seferović, PM; Vergaro, G1
Cameron, C; Salvo, EM; Samjoo, IA; Tran, D1
Agarwal, S; Betts, M; Chitnis, M; Fahrbach, K; Lin, H; Polydefkis, M1
Gagliardi, C; Milandri, A; Rapezzi, C1
Anselmo, J; Brighty, GJ; Coelho, T; Fernandes, J; Kelly, JW; Mesgazardeh, JS; Monteiro, C; Novais, M; Powers, DL; Powers, ET; Rodrigues, C1
Bokhari, S; Damy, T; Elliott, PM; Falk, RH; Fine, NM; Garcia-Pavia, P; Gospodinova, M; Obici, L; Rapezzi, C; Witteles, RM1
Autore, C; Canepa, M; Cappelli, F; Milandri, A; Mussinelli, R; Musumeci, B; Perfetto, F; Perlini, S; Rapezzi, C; Tini, G1
Merkies, IS1
Adams, D; Cauquil, C; Théaudin, M1
Adams, D; Ducot, B; Lacroix, C; Lozeron, P; Mincheva, Z; Théaudin, M1
Chan, J; Coelho, T; Conceiçao, I; Cruz, MW; da Silva, AM; Grogan, DR; Kelly, JW; Labaudinière, R; Maia, LF; Packman, J; Planté-Bordeneuve, V; Schmidt, HH; Suhr, OB; Trigo, P1
Nencetti, S; Orlandini, E; Rossello, A1
Grogan, DR; Judge, DP; Merlini, G; Obici, L; Packman, J; Perlini, S; Planté-Bordeneuve, V; Schmidt, H; Tripp, T1
Adams, D; Algalarrondo, V; Cauquil, C; Slama, M; Théaudin, M1
Sekijima, Y4
Scott, LJ1
Castaño, A; Drachman, BM; Judge, D; Maurer, MS1
Acker, T; Haverkamp, T; Kimmich, C; Krämer, HH; Röcken, C; Schänzer, A; Weidner, I1
Aarts, J; Berthet, K; Damy, T; Judge, DP; Kristen, AV; Li, H1
Aarts, J; Falk, RH; Grogan, DR; Judge, DP; Lombardo, I; Maurer, MS; Mundayat, R; Packman, J; Quyyumi, AA1
Ackermann, E; Dubrey, S; Gillmore, J1
Ando, Y; Baba, M; Honda, M; Inomata, Y; Kon, T; Misumi, Y; Nishijima, H; Obayashi, K; Suzuki, C; Tomiyama, M1
Baranczak, A; Cho, Y; Helmke, S; Horn, EM; Kelly, JW; Maurer, MS; Teruya, S1
Adams, D; Algalarrondo, V; Beaudonnet, G; Cauquil, C; Labeyrie, C; Théaudin, M1
Ando, Y; Ikeda, S; Machii, K; Misumi, Y; Morita, H; Obayashi, K; Ohta, M; Sekijima, Y; Takata, A; Ueda, M; Yamashita, T1
Bisogni, G; Calabrese, D; Cavallaro, T; Cortese, A; Fabrizi, GM; Gemelli, C; Gentile, L; Grandis, M; Lozza, A; Luigetti, M; Manganelli, F; Mauro, A; Mazzeo, A; Obici, L; Pareyson, D; Perlini, S; Piscosquito, G; Pradotto, LG; Russo, M; Sabatelli, M; Santoro, L; Schenone, A; Stancanelli, C; Vita, G1
Alvarez, R; Bettencourt, BR; Borland, TD; Butler, JS; Chan, A; Chen, Q; Costelha, S; Fishman, S; Fitzgerald, K; Foster, DJ; Gonçalves, P; Manoharan, M; Meyers, RE; Milstein, S; Nochur, SV; Qin, J; Rajeev, KG; Sah, DW; Saraiva, MJ; Willoughby, JL; Zimmermann, TS1
Bettini, M; Chaves, M; Cristiano, E; Marciano, S; Rugiero, M; Sáez, S1
Amass, L; Gundapaneni, B; Keohane, D; Li, H; Schwartz, J; Waddington Cruz, M1
Buxbaum, JN; Coelho, T; Gelbart, T; Kelly, JW; Kurian, SM; Novais, M; Salomon, DR; Whisenant, T1
Beirão, JM; Casal, I; Monteiro, S1
Ayache, SS; Azoulay, D; Damy, T; Feray, C; Gorram, F; Le Corvoisier, P; Lefaucheur, JP; Nordine, T; Planté-Bordeneuve, V; Salhi, H1
Miyazaki, Y1
Adams, D; Samuel, D; Slama, M1
de Lartigue, J1
Chalk, C1
Campistol, JM; Chan, J; Coelho, T; Conceição, IM; Grogan, DR; Kelly, JW; Labaudinière, R; Lozeron, P; Maia, LF; Martins da Silva, A; Packman, J; Planté-Bordeneuve, V; Schmidt, HH; Suhr, OB; Trigo, P; Waddington Cruz, M; Wilson, A1
de Carvalho, M1

Reviews

35 review(s) available for benzoxazoles and Amyloid Neuropathies, Familial

ArticleYear
[Diagnosis and treatment of cardiac transthyretin amyloidosis. Innovative therapy with tafamidis.]
    Revue medicale de Liege, 2022, Volume: 77, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Therapies, Investigational

2022
Impact of Tafamidis on Survival in a Real-World Community-Based Cohort.
    Current problems in cardiology, 2022, Volume: 47, Issue:12

    Topics: Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Female; Heart Failure; Humans; Male; Observational Studies as Topic; Prospective Studies

2022
Long-term survival in people with transthyretin amyloid cardiomyopathy who took tafamidis: A Plain Language Summary.
    Future cardiology, 2023, Volume: 19, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Prealbumin

2023
[Transthyretin amyloid cardiomyopathy].
    Innere Medizin (Heidelberg, Germany), 2023, Volume: 64, Issue:9

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Prealbumin; Stroke Volume; Tomography, X-Ray Computed

2023
Tafamidis for autonomic neuropathy in hereditary transthyretin (ATTR) amyloidosis: a review.
    Clinical autonomic research : official journal of the Clinical Autonomic Research Society, 2019, Volume: 29, Issue:Suppl 1

    Topics: Amyloid Neuropathies, Familial; Autonomic Nervous System Diseases; Benzoxazoles; Humans; Polyneuropathies

2019
Cardiac Amyloidosis: Overlooked, Underappreciated, and Treatable.
    Annual review of medicine, 2020, 01-27, Volume: 71

    Topics: Amyloid Neuropathies, Familial; Amyloidosis; Arrhythmias, Cardiac; Benzoates; Benzoxazoles; Biopsy; Cardiac Pacing, Artificial; Cardiomyopathies; Diflunisal; Disease Progression; Early Diagnosis; Early Medical Intervention; Echocardiography; Electrocardiography; Heart Failure; Humans; Immunoglobulin Light-chain Amyloidosis; Immunologic Factors; Magnetic Resonance Imaging; Oligonucleotides; Prealbumin; Prognosis; Proteasome Inhibitors; Pyrazoles; Radionuclide Imaging; RNA, Small Interfering

2020
The impact of clinical heterogeneity on conducting network meta-analyses in transthyretin amyloidosis with polyneuropathy.
    Current medical research and opinion, 2020, Volume: 36, Issue:5

    Topics: Adult; Amyloid Neuropathies, Familial; Bayes Theorem; Benzoxazoles; Female; Humans; Male; Middle Aged; Network Meta-Analysis; Oligonucleotides; Polyneuropathies; RNA, Small Interfering

2020
Pharmacological treatment for familial amyloid polyneuropathy.
    The Cochrane database of systematic reviews, 2020, Apr-20, Volume: 4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Disease Progression; Humans; Oligonucleotides; Patient Dropouts; Quality of Life; Randomized Controlled Trials as Topic; RNA, Small Interfering

2020
Overview of treatments used in transthyretin-related hereditary amyloidosis: a systematic review.
    European journal of hospital pharmacy : science and practice, 2020, Volume: 27, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Humans; Liver Transplantation; RNA, Small Interfering

2020
Hereditary transthyretin amyloidosis: current treatment.
    Current opinion in neurology, 2020, Volume: 33, Issue:5

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Biomarkers; Clinical Trials as Topic; Disease Progression; Humans; Oligonucleotides, Antisense; Quality of Life

2020
[Transthyretin cardiac amyloidosis].
    La Revue de medecine interne, 2020, Volume: 41, Issue:10

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Echocardiography; Electrocardiography; Humans

2020
Specific Therapy for Transthyretin Cardiac Amyloidosis: A Systematic Literature Review and Evidence-Based Recommendations.
    Journal of the American Heart Association, 2020, 10-20, Volume: 9, Issue:19

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Cardiovascular Agents; Genetic Therapy; Humans

2020
A Review of Novel Agents and Clinical Considerations in Patients With ATTR Cardiac Amyloidosis.
    Journal of cardiovascular pharmacology, 2021, 05-01, Volume: 77, Issue:5

    Topics: Amyloid Neuropathies, Familial; Animals; Benzoxazoles; Cardiomyopathies; Cardiovascular Agents; Diflunisal; Genetic Predisposition to Disease; Humans; Mutation; Oligonucleotides; Phenotype; Prealbumin; RNA, Small Interfering; Treatment Outcome

2021
Updates in Cardiac Amyloidosis Diagnosis and Treatment.
    Current oncology reports, 2021, 03-16, Volume: 23, Issue:4

    Topics: Amyloid Neuropathies, Familial; Amyloidosis; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Immunoglobulin Light-chain Amyloidosis

2021
Pathophysiology and Therapeutic Approaches to Cardiac Amyloidosis.
    Circulation research, 2021, 05-14, Volume: 128, Issue:10

    Topics: Aging; Alkylating Agents; Amyloid; Amyloid Neuropathies, Familial; Amyloidosis; Antibodies, Monoclonal; Benzoates; Benzoxazoles; Bridged Bicyclo Compounds, Heterocyclic; Cardiomyopathies; Catechol O-Methyltransferase Inhibitors; Heart Transplantation; Humans; Immunomodulating Agents; Oligonucleotides; Proteasome Inhibitors; Protein Folding; Pyrazoles; RNA, Small Interfering; Stem Cell Transplantation; Sulfonamides; Tolcapone

2021
The Ultrastructure of Tissue Damage by Amyloid Fibrils.
    Molecules (Basel, Switzerland), 2021, Jul-29, Volume: 26, Issue:15

    Topics: Alzheimer Disease; Amyloid; Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Humans; Immunoglobulin Light Chains; Immunoglobulin Light-chain Amyloidosis; Immunologic Factors; Myocardium; Neuroprotective Agents; Oligonucleotides; Peripheral Nerves; Prealbumin; Prion Diseases; RNA, Small Interfering

2021
Design and Rationale of the Phase 3 ATTR-ACT Clinical Trial (Tafamidis in Transthyretin Cardiomyopathy Clinical Trial).
    Circulation. Heart failure, 2017, Volume: 10, Issue:6

    Topics: Administration, Oral; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Clinical Trials, Phase III as Topic; Disease Management; Disease Progression; Humans; Randomized Controlled Trials as Topic

2017
Diagnosis and management of transthyretin familial amyloid polyneuropathy in Japan: red-flag symptom clusters and treatment algorithm.
    Orphanet journal of rare diseases, 2018, 01-17, Volume: 13, Issue:1

    Topics: Algorithms; Amyloid Neuropathies, Familial; Benzoxazoles; Carpal Tunnel Syndrome; Humans; Japan; Liver Transplantation; Methionine; Mutation; Valine

2018
An indirect treatment comparison of the efficacy of patisiran and tafamidis for the treatment of hereditary transthyretin-mediated amyloidosis with polyneuropathy.
    Expert opinion on pharmacotherapy, 2019, Volume: 20, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Polyneuropathies; Quality of Life; Randomized Controlled Trials as Topic; RNA, Small Interfering; Surveys and Questionnaires

2019
Tafamidis for the treatment of transthyretin amyloidosis.
    Future cardiology, 2019, Volume: 15, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Global Health; Heart Failure; Humans; Survival Rate

2019
Advances in the diagnosis and treatment of transthyretin amyloidosis with cardiac involvement.
    Heart failure reviews, 2019, Volume: 24, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Biomarkers; Cardiomyopathies; Diagnosis, Differential; Echocardiography; Electrocardiography; Humans; Magnetic Resonance Imaging; Oligonucleotides; Radionuclide Imaging; RNA, Small Interfering

2019
Treatment of hereditary and acquired forms of transthyretin amyloidosis in the era of personalized medicine: the role of randomized controlled trials.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2019, Volume: 26, Issue:2

    Topics: Amyloid Neuropathies; Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Female; Humans; Male; Oligonucleotides; Prealbumin; Precision Medicine; Randomized Controlled Trials as Topic; RNA, Small Interfering; Treatment Outcome

2019
Tafamidis: A Review in Transthyretin Amyloidosis with Polyneuropathy.
    Drugs, 2019, Volume: 79, Issue:8

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Clinical Trials as Topic; Disease Progression; Drug Approval; Humans; Mutation; Polyneuropathies; Prealbumin; Quality of Life

2019
Treatment of cardiac transthyretin amyloidosis: an update.
    European heart journal, 2019, 12-01, Volume: 40, Issue:45

    Topics: Amyloid; Amyloid Neuropathies; Amyloid Neuropathies, Familial; Benzoxazoles; Clinical Trials, Phase III as Topic; Combined Modality Therapy; Heart Failure; Heart Transplantation; Humans; Liver Transplantation; Mutation; Oligonucleotides; Prealbumin; RNA, Small Interfering; Stroke Volume

2019
Screening for Transthyretin Amyloid Cardiomyopathy in Everyday Practice.
    JACC. Heart failure, 2019, Volume: 7, Issue:8

    Topics: Age Factors; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Delayed Diagnosis; Diagnostic Errors; Early Diagnosis; Early Medical Intervention; Heart Failure; Humans; Stroke Volume

2019
[Familial amyloid polyneuropathies: therapeutic issues].
    Bulletin de l'Academie nationale de medecine, 2012, Volume: 196, Issue:7

    Topics: Amyloid Neuropathies, Familial; Antibodies, Monoclonal; Benzoxazoles; Clinical Trials as Topic; Diflunisal; Disease Progression; Doxycycline; Drug Therapy, Combination; Genetic Therapy; Heart Failure; Heart Transplantation; Humans; Kidney Failure, Chronic; Kidney Transplantation; Liver Transplantation; Myocardium; Oligonucleotides, Antisense; Renal Dialysis; RNA Interference; Serum Amyloid P-Component; Taurochenodeoxycholic Acid

2012
FAP neuropathy and emerging treatments.
    Current neurology and neuroscience reports, 2014, Volume: 14, Issue:3

    Topics: Amyloid Neuropathies, Familial; Animals; Benzoxazoles; Gene Silencing; Humans; Liver Transplantation; Mutation; Prealbumin

2014
Recent progress in the understanding and treatment of transthyretin amyloidosis.
    Journal of clinical pharmacy and therapeutics, 2014, Volume: 39, Issue:3

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Genetic Therapy; Humans; Liver Transplantation; Oligonucleotides, Antisense; Prealbumin; RNA, Small Interfering

2014
Tafamidis: a review of its use in familial amyloid polyneuropathy.
    Drugs, 2014, Volume: 74, Issue:12

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Humans

2014
Natural history and therapy of TTR-cardiac amyloidosis: emerging disease-modifying therapies from organ transplantation to stabilizer and silencer drugs.
    Heart failure reviews, 2015, Volume: 20, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Biomarkers; Cardiomyopathies; Cyclooxygenase Inhibitors; Defibrillators, Implantable; Diflunisal; Doxycycline; Heart Failure; Humans; Oligonucleotides, Antisense; Organ Transplantation; Pacemaker, Artificial; RNA, Small Interfering

2015
Transthyretin (ATTR) amyloidosis: clinical spectrum, molecular pathogenesis and disease-modifying treatments.
    Journal of neurology, neurosurgery, and psychiatry, 2015, Volume: 86, Issue:9

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Humans; Mutation; Prealbumin

2015
[Clinical diversity, diagnosis and treatment of hereditary amyloid neuropathy].
    Rinsho shinkeigaku = Clinical neurology, 2014, Volume: 54, Issue:12

    Topics: Adult; Age of Onset; Aged; Aged, 80 and over; Amyloid; Amyloid Neuropathies, Familial; Benzoxazoles; Diagnosis, Differential; Diflunisal; Early Diagnosis; Female; Genes, Dominant; Humans; Liver Transplantation; Male; Middle Aged; Mutation; Prealbumin

2014
The transthyretin amyloidoses: advances in therapy.
    Postgraduate medical journal, 2015, Volume: 91, Issue:1078

    Topics: Amyloid Neuropathies, Familial; Anti-Inflammatory Agents, Non-Steroidal; Benzoxazoles; Doxycycline; Echocardiography; Humans; Liver Transplantation; Molecular Targeted Therapy; Prealbumin; Prognosis; RNA, Small Interfering; Taurochenodeoxycholic Acid

2015
TTR kinetic stabilizers and TTR gene silencing: a new era in therapy for familial amyloidotic polyneuropathies.
    Expert opinion on pharmacotherapy, 2016, Volume: 17, Issue:6

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Clinical Trials, Phase III as Topic; Diflunisal; Disease Progression; Gene Silencing; Humans; Liver Transplantation; Prealbumin; Receptors, Albumin

2016
Tafamidis for transthyretin amyloidosis.
    Drugs of today (Barcelona, Spain : 1998), 2012, Volume: 48, Issue:5

    Topics: Amyloid Neuropathies, Familial; Animals; Benzoxazoles; Genotype; Humans; Mutation; Neuroprotective Agents; Prealbumin; Randomized Controlled Trials as Topic

2012

Trials

22 trial(s) available for benzoxazoles and Amyloid Neuropathies, Familial

ArticleYear
Annual Cardiovascular-Related Hospitalization Days Avoided with Tafamidis in Patients with Transthyretin Amyloid Cardiomyopathy.
    American journal of cardiovascular drugs : drugs, devices, and other interventions, 2022, Volume: 22, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Hospitalization; Humans; Prealbumin

2022
Estimating the Effect of Tafamidis on Cardiovascular-Related Hospitalization in NYHA Class III Patients with Transthyretin Amyloid Cardiomyopathy in the Presence of Death.
    Cardiology, 2022, Volume: 147, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Hospitalization; Humans; Prealbumin

2022
The Bioequivalence of Tafamidis 61-mg Free Acid Capsules and Tafamidis Meglumine 4 × 20-mg Capsules in Healthy Volunteers.
    Clinical pharmacology in drug development, 2020, Volume: 9, Issue:7

    Topics: Administration, Oral; Adult; Amyloid Neuropathies; Amyloid Neuropathies, Familial; Benzoxazoles; Brazil; Canada; Cardiomyopathies; Cross-Over Studies; Disease Progression; Dose-Response Relationship, Drug; Drug Administration Schedule; Drug Compounding; Fasting; Female; Healthy Volunteers; Humans; Japan; Male; Middle Aged; Prealbumin; Safety; Therapeutic Equivalency; United States

2020
Experience of patisiran with transthyretin stabilizers in patients with hereditary transthyretin-mediated amyloidosis.
    Neurodegenerative disease management, 2020, Volume: 10, Issue:5

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Female; Humans; Male; Middle Aged; Quality of Life; RNA, Small Interfering; Surveys and Questionnaires

2020
Efficacy and safety of tafamidis doses in the Tafamidis in Transthyretin Cardiomyopathy Clinical Trial (ATTR-ACT) and long-term extension study.
    European journal of heart failure, 2021, Volume: 23, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Prealbumin

2021
Impact of Tafamidis on Health-Related Quality of Life in Patients With Transthyretin Amyloid Cardiomyopathy (from the Tafamidis in Transthyretin Cardiomyopathy Clinical Trial).
    The American journal of cardiology, 2021, 02-15, Volume: 141

    Topics: Activities of Daily Living; Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Cost of Illness; Female; Humans; Male; Patient Reported Outcome Measures; Quality of Life; Self Efficacy; Social Participation

2021
Causes of Cardiovascular Hospitalization and Death in Patients With Transthyretin Amyloid Cardiomyopathy (from the Tafamidis in Transthyretin Cardiomyopathy Clinical Trial [ATTR-ACT]).
    The American journal of cardiology, 2021, 06-01, Volume: 148

    Topics: Aged; Amyloid Neuropathies, Familial; Amyloidosis; Arrhythmias, Cardiac; Benzoxazoles; Cardiomyopathies; Cardiovascular Diseases; Cause of Death; Death, Sudden, Cardiac; Double-Blind Method; Female; Heart Failure; Hospitalization; Humans; Ischemic Attack, Transient; Male; Myocardial Infarction; Prealbumin; Proportional Hazards Models; Stroke

2021
Health impact of tafamidis in transthyretin amyloid cardiomyopathy patients: an analysis from the Tafamidis in Transthyretin Cardiomyopathy Clinical Trial (ATTR-ACT) and the open-label long-term extension studies.
    European heart journal. Quality of care & clinical outcomes, 2022, 08-17, Volume: 8, Issue:5

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Prealbumin

2022
Tafamidis delays disease progression in patients with early stage transthyretin familial amyloid polyneuropathy: additional supportive analyses from the pivotal trial.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2017, Volume: 24, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Female; Humans; Male; Middle Aged; Polyneuropathies; Prealbumin; Treatment Outcome

2017
Transthyretin (ATTR) amyloidosis nephropathy: lessons from a TTR stabilizer molecule.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2017, Volume: 24, Issue:sup1

    Topics: Adult; Amyloid; Amyloid Neuropathies, Familial; Benzoxazoles; Biomarkers; Creatinine; Cystatin C; Drug Administration Schedule; Female; Gene Expression; Glomerular Filtration Rate; Humans; Kidney; Male; Middle Aged; Mutation; Nephritis; Prealbumin; Prospective Studies; Proteinuria

2017
Long-term safety and efficacy of tafamidis for the treatment of hereditary transthyretin amyloid polyneuropathy: results up to 6 years.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2017, Volume: 24, Issue:3

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Female; Humans; Longitudinal Studies; Male; Middle Aged; Quality of Life

2017
Tafamidis delays neurological progression comparably across Val30Met and non-Val30Met genotypes in transthyretin familial amyloid polyneuropathy.
    European journal of neurology, 2018, Volume: 25, Issue:3

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Double-Blind Method; Female; Genotype; Humans; Lower Extremity; Male; Middle Aged; Mutation; Treatment Outcome

2018
Tafamidis Treatment for Patients with Transthyretin Amyloid Cardiomyopathy.
    The New England journal of medicine, 2018, Sep-13, Volume: 379, Issue:11

    Topics: Administration, Oral; Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Disease Progression; Double-Blind Method; Female; Heart Failure; Hospitalization; Humans; Male; Middle Aged; Prealbumin; Quality of Life; Survival Analysis; Walk Test

2018
Tafamidis for transthyretin amyloid cardiomyopathy: the solution or just the beginning of the end?
    European heart journal, 2019, 03-21, Volume: 40, Issue:12

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Case-Control Studies; Echocardiography; Hospitalization; Humans; Mutation; Placebos; Prealbumin; Survival Analysis

2019
Effect on disability and safety of Tafamidis in late onset of Met30 transthyretin familial amyloid polyneuropathy.
    European journal of neurology, 2013, Volume: 20, Issue:12

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Humans; Middle Aged

2013
Long-term effects of tafamidis for the treatment of transthyretin familial amyloid polyneuropathy.
    Journal of neurology, 2013, Volume: 260, Issue:11

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Drug Administration Schedule; Female; Follow-Up Studies; Humans; International Cooperation; Male; Methionine; Middle Aged; Mutation; Prealbumin; Quality of Life; Time Factors; Valine; Young Adult

2013
Effects of tafamidis on transthyretin stabilization and clinical outcomes in patients with non-Val30Met transthyretin amyloidosis.
    Journal of cardiovascular translational research, 2013, Volume: 6, Issue:6

    Topics: Adult; Aged; Amyloid; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Europe; Female; Genetic Predisposition to Disease; Humans; Male; Middle Aged; Mutation; Phenotype; Prealbumin; Time Factors; Treatment Outcome; United States

2013
Cardiac findings and events observed in an open-label clinical trial of tafamidis in patients with non-Val30Met and non-Val122Ile hereditary transthyretin amyloidosis.
    Journal of cardiovascular translational research, 2015, Volume: 8, Issue:2

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Europe; Female; Fibrosis; Genetic Predisposition to Disease; Heart Failure; Humans; Male; Middle Aged; Mutation; Myocardium; Phenotype; Prealbumin; Risk Factors; Time Factors; Treatment Outcome; United States

2015
Tafamidis in transthyretin amyloid cardiomyopathy: effects on transthyretin stabilization and clinical outcomes.
    Circulation. Heart failure, 2015, Volume: 8, Issue:3

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Disease Progression; Drug Administration Schedule; Female; Humans; Male; Mutation; Myocardium; Prealbumin; Protein Folding; Protein Multimerization; Protein Stability; Protein Structure, Quaternary; Time Factors; Treatment Outcome; United States

2015
Effects of tafamidis treatment on transthyretin (TTR) stabilization, efficacy, and safety in Japanese patients with familial amyloid polyneuropathy (TTR-FAP) with Val30Met and non-Val30Met: A phase III, open-label study.
    Journal of the neurological sciences, 2016, Mar-15, Volume: 362

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Body Mass Index; Echocardiography; Female; Follow-Up Studies; Humans; Japan; Male; Methionine; Middle Aged; Pharmacogenetics; Prealbumin; Valine; Young Adult

2016
Early intervention with tafamidis provides long-term (5.5-year) delay of neurologic progression in transthyretin hereditary amyloid polyneuropathy.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2016, Volume: 23, Issue:3

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Anti-Inflammatory Agents, Non-Steroidal; Benzoxazoles; Double-Blind Method; Drug Administration Schedule; Female; Humans; Male; Middle Aged; Prospective Studies; Secondary Prevention

2016
Tafamidis for transthyretin familial amyloid polyneuropathy: a randomized, controlled trial.
    Neurology, 2012, Aug-21, Volume: 79, Issue:8

    Topics: Adolescent; Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Double-Blind Method; Humans; Male; Middle Aged; Neuroprotective Agents; Polymorphism, Single Nucleotide; Prealbumin; Quality of Life; Severity of Illness Index

2012

Other Studies

83 other study(ies) available for benzoxazoles and Amyloid Neuropathies, Familial

ArticleYear
Compassionate drug use for patients with transthyretin amyloid cardiomyopathy.
    Journal of cardiovascular medicine (Hagerstown, Md.), 2021, 10-01, Volume: 22, Issue:10

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathy, Restrictive; Compassionate Use Trials; Drug Approval; Drugs, Investigational; Heart Failure; Humans; Magnetic Resonance Imaging, Cine; Myocardial Perfusion Imaging; Treatment Outcome

2021
Tafamidis and quality of life in people with transthyretin amyloid cardiomyopathy in the study ATTR-ACT: A plain language summary.
    Future cardiology, 2022, Volume: 18, Issue:3

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Language; Prealbumin; Quality of Life

2022
Long-Term Survival With Tafamidis in Patients With Transthyretin Amyloid Cardiomyopathy.
    Circulation. Heart failure, 2022, Volume: 15, Issue:1

    Topics: Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Female; Heart Failure; Hospitalization; Humans; Male; Middle Aged; Prealbumin; Proportional Hazards Models; Time

2022
Clinical improvement after change of therapy from tafamidis to patisiran in progressive TTR amyloidosis post-liver transplantation.
    Journal of neurology, 2022, Volume: 269, Issue:7

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Liver Transplantation; Prealbumin; RNA, Small Interfering

2022
[Practice guideline for the treatment of familial amyloid polyneuropathy].
    Medicina, 2022, Volume: 82, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Prealbumin; Quality of Life; Treatment Outcome

2022
[Specific pharmacological treatment guide for transthyretin amyloid cardiomyopathy, 2021].
    Medicina, 2022, Volume: 82, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Diflunisal; Doxycycline; Humans; Prealbumin; Ursodeoxycholic Acid

2022
Tafamidis and its stabilizing effects on transthyretin tetramers, the heart and eventually, scientific evidence.
    European heart journal. Cardiovascular Imaging, 2022, 07-21, Volume: 23, Issue:8

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Myocardium; Prealbumin

2022
Early Experience of Tafamidis Treatment in Japanese Patients With Wild-Type Transthyretin Cardiac Amyloidosis From the Kochi Amyloidosis Cohort.
    Circulation journal : official journal of the Japanese Circulation Society, 2022, 06-24, Volume: 86, Issue:7

    Topics: Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Japan; Prealbumin; Stroke Volume; Ventricular Function, Left

2022
What is this image? 2022 image 1 result: radiologic improvement of transthyretin cardiac amyloidosis after treatment with tafamidis.
    Journal of nuclear cardiology : official publication of the American Society of Nuclear Cardiology, 2022, Volume: 29, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Prealbumin

2022
Response by Elliott et al to Letter Regarding Article, "Long-Term Survival With Tafamidis in Patients With Transthyretin Amyloid Cardiomyopathy".
    Circulation. Heart failure, 2022, Volume: 15, Issue:7

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Prealbumin

2022
Letter by Baldovino et al Regarding Article, "Long-Term Survival With Tafamidis in Patients With Transthyretin Amyloid Cardiomyopathy".
    Circulation. Heart failure, 2022, Volume: 15, Issue:7

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Prealbumin

2022
Understanding Changes in Functional Capacity After TTR Stabilization in Patients With Transthyretin Cardiac Amyloidosis.
    Circulation. Heart failure, 2022, Volume: 15, Issue:7

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Prealbumin

2022
Redefining Prognosis of Transthyretin Cardiomyopathy in the Tafamidis Era.
    Journal of cardiac failure, 2022, Volume: 28, Issue:10

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart Failure; Humans; Prealbumin; Prognosis

2022
Tafamidis polyneuropathy amelioration requires modest increases in transthyretin stability even though increases in plasma native TTR and decreases in non-native TTR do not predict response.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2023, Volume: 30, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Male; Polyneuropathies; Prealbumin

2023
Regression of left ventricular hypertrophy after tafamidis therapy in a patient with transthyretin amyloidosis variant.
    The journal of medical investigation : JMI, 2022, Volume: 69, Issue:3.4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Hypertrophy, Left Ventricular; Prealbumin

2022
Relationship of binding-site occupancy, transthyretin stabilisation and disease modification in patients with tafamidis-treated transthyretin amyloid cardiomyopathy.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2023, Volume: 30, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Disease Progression; Humans; Prealbumin

2023
Tafamidis concentration required for transthyretin stabilisation in cerebrospinal fluid.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2023, Volume: 30, Issue:3

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Prealbumin

2023
Comparison between tafamidis and liver transplantation as first-line therapy for hereditary transthyretin amyloidosis.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2023, Volume: 30, Issue:3

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Liver Transplantation; Middle Aged; Prealbumin; Retrospective Studies

2023
New Drugs Treat Rare Heart Disease Caused by Transthyretin-Mediated Amyloidosis.
    The American journal of nursing, 2019, Volume: 119, Issue:9

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Heart Diseases; Humans

2019
Biophysical characterization and modulation of Transthyretin Ala97Ser.
    Annals of clinical and translational neurology, 2019, Volume: 6, Issue:10

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Binding Sites; Biophysical Phenomena; Calorimetry; Humans; Magnetic Resonance Spectroscopy; Mutation; Prealbumin

2019
Transthyretin Amyloidosis with Gastrointestinal Manifestation: a Case Report.
    Journal of gastrointestinal and liver diseases : JGLD, 2019, Sep-01, Volume: 28, Issue:3

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Chronic Disease; Diagnosis, Differential; Diarrhea; DNA Mutational Analysis; Genetic Predisposition to Disease; Humans; Male; Middle Aged; Mutation; Prealbumin; Predictive Value of Tests

2019
A Statement on the Appropriate Administration of Tafamidis in Patients With Transthyretin Cardiac Amyloidosis.
    Circulation journal : official journal of the Japanese Circulation Society, 2019, 12-25, Volume: 84, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans

2019
Advantages and Emerging Problems of Novel Treatments for Transthyretin Cardiac Amyloidosis.
    Circulation journal : official journal of the Japanese Circulation Society, 2019, 12-25, Volume: 84, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Prealbumin

2019
Tafamidis-A Pricey Therapy for a Not-So-Rare Condition.
    JAMA cardiology, 2020, 03-01, Volume: 5, Issue:3

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cost-Benefit Analysis; Drug Approval; Health Policy; Humans; Randomized Controlled Trials as Topic; United States

2020
Hereditary transthyretin amyloidosis caused by the rare Phe33Leu mutation.
    BMJ case reports, 2020, Jan-12, Volume: 13, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Combined Modality Therapy; Diagnosis, Differential; Heart Transplantation; Humans; Leucine; Male; Middle Aged; Mutation; Phenylalanine; Prealbumin

2020
Tafamidis: a selective transthyretin stabilizer to treat wild-type ATTR amyloidosis and hereditary ATTR amyloidosis with cardiomyopathy.
    Drugs of today (Barcelona, Spain : 1998), 2019, Volume: 55, Issue:12

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Prealbumin

2019
Cost-Effectiveness of Tafamidis Therapy for Transthyretin Amyloid Cardiomyopathy.
    Circulation, 2020, 04-14, Volume: 141, Issue:15

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Cost-Benefit Analysis; Female; Humans; Male; Quality of Life

2020
Initial Monthly Cost of Tafamidis-the Real Price for Patients.
    JAMA cardiology, 2020, 07-01, Volume: 5, Issue:7

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans

2020
Initial Monthly Cost of Tafamidis-the Real Price for Patients-Reply.
    JAMA cardiology, 2020, 07-01, Volume: 5, Issue:7

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans

2020
[Experience with tafamidis in a patient with transthyretin amyloidosis].
    Kardiologiia, 2020, Jan-20, Volume: 60, Issue:3

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Prealbumin

2020
Motor excitability measurements in early stage familial amyloid polyneuropathy: The influence of tafamidis treatment.
    Neurophysiologie clinique = Clinical neurophysiology, 2020, Volume: 50, Issue:3

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Female; Humans; Male; Median Nerve; Nerve Fibers; Neural Conduction; Neuroprotective Agents; Treatment Outcome

2020
Characteristics of Patients with Hereditary Transthyretin Amyloidosis and an Evaluation of the Safety of Tafamidis Meglumine in Japan: An Interim Analysis of an All-case Postmarketing Surveillance.
    Clinical therapeutics, 2020, Volume: 42, Issue:9

    Topics: Adolescent; Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Female; Humans; Japan; Male; Middle Aged; Young Adult

2020
Blinded potency comparison of transthyretin kinetic stabilisers by subunit exchange in human plasma.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2021, Volume: 28, Issue:1

    Topics: Amyloid; Amyloid Neuropathies, Familial; Benzoates; Benzoxazoles; Cardiomyopathies; Diflunisal; Humans; Kinetics; Prealbumin; Protein Aggregates; Protein Binding; Protein Multimerization; Protein Subunits; Pyrazoles; Tolcapone

2021
Conventional Molecular Dynamics and Metadynamics Simulation Studies of the Binding and Unbinding Mechanism of TTR Stabilizers AG10 and Tafamidis.
    ACS chemical neuroscience, 2020, 10-07, Volume: 11, Issue:19

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Molecular Dynamics Simulation; Prealbumin

2020
Response by Kazi et al to Letter Regarding Article, "Cost-Effectiveness of Tafamidis Therapy for Transthyretin Amyloid Cardiomyopathy".
    Circulation, 2020, 10-13, Volume: 142, Issue:15

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Cost-Benefit Analysis; Humans; Prealbumin

2020
Letter by Rozenbaum et al Regarding Article, "Cost-Effectiveness of Tafamidis Therapy for Transthyretin Amyloid Cardiomyopathy".
    Circulation, 2020, 10-13, Volume: 142, Issue:15

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Cost-Benefit Analysis; Humans; Prealbumin

2020
Natural history and impact of treatment with tafamidis on major cardiovascular outcome-free survival time in a cohort of patients with transthyretin amyloidosis.
    European journal of heart failure, 2021, Volume: 23, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; France; Heart Failure; Humans

2021
Population pharmacokinetic modelling and simulation of tafamidis in healthy subjects and patients with transthyretin amyloidosis.
    British journal of clinical pharmacology, 2021, Volume: 87, Issue:9

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Healthy Volunteers; Humans

2021
Estimating the annual economic burden for the management of patients with transthyretin amyloid polyneuropathy in Spain.
    Expert review of pharmacoeconomics & outcomes research, 2021, Volume: 21, Issue:5

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cost of Illness; Drug Costs; Health Care Costs; Hospitalization; Humans; Oligonucleotides; RNA, Small Interfering; Spain

2021
Modeling of Survival and Frequency of Cardiovascular-Related Hospitalization in Patients with Transthyretin Amyloid Cardiomyopathy Treated with Tafamidis.
    American journal of cardiovascular drugs : drugs, devices, and other interventions, 2021, Volume: 21, Issue:5

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Hospitalization; Humans; Models, Statistical; Survival Analysis

2021
[Update of tafamidis for the treatment of transthyretin cardiac amyloidosis].
    Zhonghua xin xue guan bing za zhi, 2021, Apr-24, Volume: 49, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Prealbumin

2021
False Positive 99mTc-Pyrophosphate Scanning Leading to Inappropriate Tafamidis Prescriptions.
    JACC. Cardiovascular imaging, 2021, Volume: 14, Issue:10

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Predictive Value of Tests; Prescriptions; Technetium Tc 99m Pyrophosphate

2021
Factors associated with changes in serum transthyretin after treatment with tafamidis and outcomes in transthyretin cardiac amyloidosis.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2021, Volume: 28, Issue:4

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Prealbumin

2021
Discredited legacy: Stigma and familial amyloid polyneuropathy in Northwestern Portugal.
    Social science & medicine (1982), 2017, Volume: 182

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Female; Genetic Diseases, Inborn; Humans; Male; Middle Aged; Portugal; Qualitative Research; Reproductive Behavior; Social Stigma; Surveys and Questionnaires

2017
Disruption of blood-nerve barriers in hereditary transthyretin (ATTR) amyloidosis.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2017, Volume: 24, Issue:sup1

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Cell Survival; Female; Humans; Male; Middle Aged; Mutation; Plasma

2017
Pharmacokinetics of tafamidis, a transthyretin amyloidosis drug, in rats.
    Xenobiotica; the fate of foreign compounds in biological systems, 2018, Volume: 48, Issue:8

    Topics: Amyloid Neuropathies, Familial; Animals; Benzoxazoles; Brain; Caco-2 Cells; Humans; Liver; Male; Microsomes, Liver; Organ Specificity; Rats; Rats, Sprague-Dawley

2018
Amyloid Polyneuropathy and Myocardial Amyloidosis 10 Years after Domino Liver Transplantation from a Patient with a Transthyretin Ser50Arg Mutation.
    Internal medicine (Tokyo, Japan), 2017, Dec-01, Volume: 56, Issue:23

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cysts; Humans; Liver Diseases; Liver Transplantation; Male; Middle Aged; Mutation; Prealbumin; Treatment Outcome

2017
Unwanted road to anaemia in transthyretin familial amyloid polyneuropathy may continue irrespective of tafamidis treatment.
    Annals of clinical biochemistry, 2018, Volume: 55, Issue:5

    Topics: Amyloid Neuropathies, Familial; Anemia; Benzoxazoles; Blood Chemical Analysis; Disease Progression; Female; Humans; Longitudinal Studies; Male; Middle Aged; Retrospective Studies

2018
Failure of Tafamidis to Halt Progression of Ala36Pro TTR Oculomeningovascular Amyloidosis.
    Journal of stroke and cerebrovascular diseases : the official journal of National Stroke Association, 2018, Volume: 27, Issue:9

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Blindness; Brain Ischemia; Cerebrovascular Disorders; Disease Progression; Eye Diseases; Female; Genetic Predisposition to Disease; Humans; Intracranial Hemorrhages; Magnetic Resonance Imaging; Mutation; Phenotype; Prealbumin; Siderosis; Treatment Failure; Ultrasonography

2018
Hereditary amyloidosis related to transthyretin V30M: disease progression in treated and untreated patients.
    European journal of neurology, 2018, Volume: 25, Issue:11

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Female; Humans; Liver Transplantation; Male; Middle Aged; Neural Conduction; Polyneuropathies; Time Factors; Treatment Outcome

2018
Cerebrospinal fluid and vitreous body exposure to orally administered tafamidis in hereditary ATTRV30M (p.TTRV50M) amyloidosis patients.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2018, Volume: 25, Issue:2

    Topics: Administration, Oral; Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Cerebrospinal Fluid; Chromatography, High Pressure Liquid; Female; Humans; Liver Transplantation; Male; Mutation; Prealbumin; Vitreous Body

2018
[What gnaws at the heart and gets on the nerves].
    Der Internist, 2018, Volume: 59, Issue:11

    Topics: Aged; Amyloid; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Drug Approval; Humans; Middle Aged; Mutation; Polyneuropathies; Prealbumin; Quality of Life

2018
Transthyretin Stabilizer Is Associated With Expanding Apical Sparing Area and Improving Global Cardiac Function in a Patient With Wild-Type Cardiac Amyloidosis.
    Circulation journal : official journal of the Japanese Circulation Society, 2019, 02-25, Volume: 83, Issue:3

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Heart; Humans; Magnetic Resonance Angiography; Male; Treatment Outcome

2019
Natural history and survival in stage 1 Val30Met transthyretin familial amyloid polyneuropathy.
    Neurology, 2018, 11-20, Volume: 91, Issue:21

    Topics: Adult; Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Female; Follow-Up Studies; Humans; Liver Transplantation; Male; Middle Aged

2018
Brazilian consensus for diagnosis, management and treatment of transthyretin familial amyloid polyneuropathy.
    Arquivos de neuro-psiquiatria, 2018, Volume: 76, Issue:9

    Topics: Amyloid Neuropathies, Familial; Animals; Benzoxazoles; Brazil; Cardiomyopathies; Diagnosis, Differential; Humans; Oligonucleotides; Randomized Controlled Trials as Topic; RNA, Small Interfering

2018
Monitoring treatment response to tafamidis by serial native T1 and extracellular volume in transthyretin amyloid cardiomyopathy.
    ESC heart failure, 2019, Volume: 6, Issue:1

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Biopsy; Cardiomyopathies; Electrocardiography; Follow-Up Studies; Humans; Magnetic Resonance Imaging, Cine; Male; Myocardium

2019
Hereditary cardiac amyloidosis associated with Pro24Ser transthyretin mutation: a case report.
    Journal of medical case reports, 2018, Dec-16, Volume: 12, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Diuretics; Echocardiography; Genes, Dominant; Humans; Male; Middle Aged; Mutation; Prealbumin; Radionuclide Imaging; Treatment Outcome

2018
Tafamidis for Transthyretin Amyloid Cardiomyopathy.
    The New England journal of medicine, 2019, 01-10, Volume: 380, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Prealbumin

2019
Tafamidis for Transthyretin Amyloid Cardiomyopathy.
    The New England journal of medicine, 2019, 01-10, Volume: 380, Issue:2

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Humans; Prealbumin

2019
Transthyretin deposition in the eye in the era of effective therapy for hereditary ATTRV30M amyloidosis.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2019, Volume: 26, Issue:1

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Eye Diseases; Humans; Mutation, Missense; Prealbumin; Protein Aggregation, Pathological

2019
Electrochemical skin conductance in hereditary amyloidosis related to transthyretin V30M - a promising tool to assess treatment efficacy?
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2018, Volume: 25, Issue:4

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Case-Control Studies; Electrochemical Techniques; Female; Follow-Up Studies; Galvanic Skin Response; Humans; Male; Middle Aged; Mutation; Neural Conduction; Prealbumin; Prognosis; Prospective Studies

2018
Tafamidis dramatically improved severe proteinuria in a patient with TTR V30M hereditary ATTR amyloidosis.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2019, Volume: 26, Issue:2

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Male; Middle Aged; Mutation, Missense; Prealbumin; Proteinuria; Treatment Outcome

2019
Letter to the editor concerning the article: "An indirect treatment comparison of the efficacy of patisiran and tafamidis for the treatment of hereditary transthyretin-mediated amyloidosis with polyneuropathy".
    Expert opinion on pharmacotherapy, 2019, Volume: 20, Issue:12

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Polyneuropathies; Prealbumin; RNA, Small Interfering

2019
Response to the letter to the editor on "an indirect treatment comparison of the efficacy of patisiran and tafamidis for the treatment of hereditary transthyretin-mediated amyloidosis with polyneuropathy".
    Expert opinion on pharmacotherapy, 2019, Volume: 20, Issue:12

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Polyneuropathies; Prealbumin; RNA, Small Interfering

2019
[The ATTR-ACT trial].
    Giornale italiano di cardiologia (2006), 2019, Volume: 20, Issue:6

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Multicenter Studies as Topic; Randomized Controlled Trials as Topic

2019
Predictive model of response to tafamidis in hereditary ATTR polyneuropathy.
    JCI insight, 2019, 06-20, Volume: 4, Issue:12

    Topics: Adult; Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Biomarkers; Cohort Studies; Demography; Female; Humans; Longitudinal Studies; Male; Middle Aged; Models, Biological; Prealbumin; Sex Factors; Treatment Outcome; Young Adult

2019
Real-world versus trial patients with transthyretin amyloid cardiomyopathy.
    European journal of heart failure, 2019, Volume: 21, Issue:11

    Topics: Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Angiotensin-Converting Enzyme Inhibitors; Benzoxazoles; Cardiomyopathies; Cardiovascular Agents; Clinical Trials as Topic; Diuretics; Female; Humans; Male; Rare Diseases

2019
Tafamidis for transthyretin familial amyloid polyneuropathy: a randomized, controlled trial.
    Neurology, 2013, Apr-09, Volume: 80, Issue:15

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Male; Neuroprotective Agents; Prealbumin

2013
Tafamidis (Vyndaqel): a light for FAP patients.
    ChemMedChem, 2013, Volume: 8, Issue:10

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Binding Sites; Drug Design; Humans; Mutation; Prealbumin; Protein Binding; Protein Structure, Tertiary

2013
[Newly developed drug therapies for familial amyloid polyneuropathy: diflunisal and tafamidis].
    Brain and nerve = Shinkei kenkyu no shinpo, 2014, Volume: 66, Issue:7

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Diflunisal; Humans; Liver Transplantation; Molecular Targeted Therapy; Prealbumin; Protein Multimerization

2014
A woman with a rare p.Glu74Gly transthyretin mutation presenting exclusively with a rapidly progressive neuropathy: a case report.
    Journal of medical case reports, 2014, Dec-04, Volume: 8

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Fatal Outcome; Female; Genetic Linkage; Glutamic Acid; Glycine; Humans; Liver Transplantation; Mutation, Missense; Pedigree; Prealbumin

2014
Effects of liver transplantation and tafamidis in hereditary transthyretin amyloidosis caused by transthyretin Leu55Pro mutation: a case report.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2015, Volume: 22, Issue:3

    Topics: Adult; Amino Acid Substitution; Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Hypesthesia; Liver Transplantation; Male; Muscle Weakness; Mutation; Neuroprotective Agents; Prealbumin

2015
Personalized medicine approach for optimizing the dose of tafamidis to potentially ameliorate wild-type transthyretin amyloidosis (cardiomyopathy).
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2015, Volume: 22, Issue:3

    Topics: Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Cardiomyopathies; Drug Dosage Calculations; Drug Monitoring; Escherichia coli; Gene Expression; Humans; Kinetics; Male; Neuroprotective Agents; Prealbumin; Precision Medicine; Protein Stability; Recombinant Proteins

2015
Monitoring effectiveness and safety of Tafamidis in transthyretin amyloidosis in Italy: a longitudinal multicenter study in a non-endemic area.
    Journal of neurology, 2016, Volume: 263, Issue:5

    Topics: Adult; Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Female; Follow-Up Studies; Humans; Italy; Longitudinal Studies; Male; Middle Aged; Mutation; Prealbumin; Prognosis; Severity of Illness Index; Treatment Outcome

2016
Preclinical evaluation of RNAi as a treatment for transthyretin-mediated amyloidosis.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2016, Volume: 23, Issue:2

    Topics: Amyloid Neuropathies, Familial; Animals; Anti-Inflammatory Agents, Non-Steroidal; Benzoxazoles; Disease Models, Animal; Drug Evaluation, Preclinical; Female; Gene Expression; Humans; Liver; Macaca fascicularis; Male; Mice; Mice, Transgenic; Prealbumin; RNA Interference; RNA, Messenger; RNA, Small Interfering

2016
[Presentations of transthyretin associated familial amyloid polyneuropathy in Argentina].
    Medicina, 2016, Volume: 76, Issue:2

    Topics: Adult; Amyloid Neuropathies, Familial; Argentina; Benzoxazoles; Fatal Outcome; Female; Humans; Liver Transplantation; Male; Middle Aged; Mutation; Prealbumin; Retrospective Studies

2016
Peripheral Blood Cell Gene Expression Diagnostic for Identifying Symptomatic Transthyretin Amyloidosis Patients: Male and Female Specific Signatures.
    Theranostics, 2016, Volume: 6, Issue:11

    Topics: Adult; Amyloid Neuropathies, Familial; Benzoxazoles; Biomarkers; Blood Cells; Cohort Studies; Female; Gene Expression; Gene Expression Profiling; Heterozygote; Humans; Inflammation; Male; Prealbumin; RNA; Sex Characteristics

2016
Tafamidis in hereditary ATTR amyloidosis - our experience on monitoring the ocular manifestations.
    Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2016, Volume: 23, Issue:4

    Topics: Amyloid; Amyloid Neuropathies, Familial; Benzoxazoles; Disease Progression; Female; Humans; Iris; Male; Middle Aged; Optic Disk; Prealbumin; Protein Aggregates; Retinal Pigment Epithelium; Vitreous Body

2016
Long-term treatment of transthyretin familial amyloid polyneuropathy with tafamidis: a clinical and neurophysiological study.
    Journal of neurology, 2017, Volume: 264, Issue:2

    Topics: Adult; Aged; Aged, 80 and over; Amyloid Neuropathies, Familial; Benzoxazoles; Body Mass Index; Disease Progression; Female; Follow-Up Studies; Hematologic Agents; Humans; Male; Middle Aged; Neural Conduction; Time Factors; Treatment Outcome

2017
Treatment of transthyretin familial amyloid polyneuropathy with tafamidis: a case report.
    Nihon Ronen Igakkai zasshi. Japanese journal of geriatrics, 2017, Volume: 54, Issue:1

    Topics: Aged; Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Male

2017
[Treatment of familial amyloid polyneuropathy].
    Presse medicale (Paris, France : 1983), 2012, Volume: 41, Issue:9 Pt 1

    Topics: Amyloid; Amyloid Neuropathies, Familial; Arrhythmias, Cardiac; Benzoxazoles; Early Diagnosis; Follow-Up Studies; Heart Transplantation; Humans; Kidney Transplantation; Liver Transplantation; Mutation; Prealbumin; Quality of Life; RNA Interference; RNA, Small Interfering

2012
A designer drug for amyloid polyneuropathy.
    Neurology, 2012, Aug-21, Volume: 79, Issue:8

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Male; Neuroprotective Agents; Prealbumin

2012
Is it better than it seems or just good enough? The tafamidis saga.
    Muscle & nerve, 2012, Volume: 46, Issue:6

    Topics: Amyloid Neuropathies, Familial; Benzoxazoles; Humans; Mutation; Neuroprotective Agents; Prealbumin

2012