Page last updated: 2024-09-05

arimoclomol and Neurovisceral Storage Disease with Vertical Supranuclear Ophthalmoplegia

arimoclomol has been researched along with Neurovisceral Storage Disease with Vertical Supranuclear Ophthalmoplegia in 2 studies

Research

Studies (2)

Timeframe	Studies, this research(%)	All Research%
pre-1990	0 (0.00)	18.7374
1990's	0 (0.00)	18.2507
2000's	0 (0.00)	29.6817
2010's	1 (50.00)	24.3611
2020's	1 (50.00)	2.80

Authors

Authors	Studies
Andreasen, AK; Blaettler, T; Da Riol, RM; Day, S; Del Toro, M; Deodato, F; Gautschi, M; Geist, MA; Grunewald, S; Grønborg, S; Hansen, T; Harmatz, P; Havnsøe Torp Petersen, N; Héron, B; Í Dali, C; Ingemann, L; Kirkegaard, T; Maier, EM; Mengel, E; Patterson, MC; Roubertie, A; Santra, S; Tylki-Szymanska, A	1
Arenz, C; Atkins, J; Begley, D; Bornæs, C; Drndarski, S; Gray, J; Hinsby, A; Ingemann, L; Jäättelä, M; Jørgensen, SH; Kirkegaard, T; Klein, A; Morris, L; Olsen, OD; Petersen, NH; Platt, FM; Priestman, DA; Smith, DA; Wallom, KL; Williams, I	1

Trials

1 trial(s) available for arimoclomol and Neurovisceral Storage Disease with Vertical Supranuclear Ophthalmoplegia

Article	Year
Efficacy and safety of arimoclomol in Niemann-Pick disease type C: Results from a double-blind, randomised, placebo-controlled, multinational phase 2/3 trial of a novel treatment. Journal of inherited metabolic disease, 2021, Volume: 44, Issue:6 Topics: Adolescent; Child; Child, Preschool; Disease Progression; Double-Blind Method; Female; Humans; Hydroxylamines; Internationality; Male; Niemann-Pick Disease, Type C; Prospective Studies; Severity of Illness Index; Treatment Outcome; Young Adult	2021

Article

Year

Efficacy and safety of arimoclomol in Niemann-Pick disease type C: Results from a double-blind, randomised, placebo-controlled, multinational phase 2/3 trial of a novel treatment.

Journal of inherited metabolic disease, 2021, Volume: 44, Issue:6

Topics: Adolescent; Child; Child, Preschool; Disease Progression; Double-Blind Method; Female; Humans; Hydroxylamines; Internationality; Male; Niemann-Pick Disease, Type C; Prospective Studies; Severity of Illness Index; Treatment Outcome; Young Adult

2021

Other Studies

1 other study(ies) available for arimoclomol and Neurovisceral Storage Disease with Vertical Supranuclear Ophthalmoplegia

Article	Year
Heat shock protein-based therapy as a potential candidate for treating the sphingolipidoses. Science translational medicine, 2016, 09-07, Volume: 8, Issue:355 Topics: Administration, Intravenous; Animals; Blood-Brain Barrier; Bone Morphogenetic Proteins; Disease Models, Animal; Disease Progression; Fabry Disease; Fibroblasts; Glycosphingolipids; Heat-Shock Proteins; Humans; Hydroxylamines; Injections, Intraperitoneal; Intracellular Signaling Peptides and Proteins; Lysosomes; Niemann-Pick C1 Protein; Niemann-Pick Disease, Type C; Proteins; Recombinant Proteins; Sphingolipidoses; Tissue Distribution	2016

Article

Year

Heat shock protein-based therapy as a potential candidate for treating the sphingolipidoses.

Science translational medicine, 2016, 09-07, Volume: 8, Issue:355

Topics: Administration, Intravenous; Animals; Blood-Brain Barrier; Bone Morphogenetic Proteins; Disease Models, Animal; Disease Progression; Fabry Disease; Fibroblasts; Glycosphingolipids; Heat-Shock Proteins; Humans; Hydroxylamines; Injections, Intraperitoneal; Intracellular Signaling Peptides and Proteins; Lysosomes; Niemann-Pick C1 Protein; Niemann-Pick Disease, Type C; Proteins; Recombinant Proteins; Sphingolipidoses; Tissue Distribution

2016