chlorine and ptc 124

chlorine has been researched along with ptc 124 in 4 studies

Research

Studies (4)

TimeframeStudies, this research(%)All Research%
pre-19900 (0.00)18.7374
1990's0 (0.00)18.2507
2000's1 (25.00)29.6817
2010's3 (75.00)24.3611
2020's0 (0.00)2.80

Authors

AuthorsStudies
Armoni, S; Aviram, M; Blau, H; Cohen, M; Elfring, GL; Hirawat, S; Kerem, B; Kerem, E; Miller, LL; Nissim-Rafinia, M; Northcutt, VJ; Rivlin, J; Shoseyov, D; Wilschanski, M; Yaakov, Y1
Kerem, B; Linde, L1
Roomans, GM1
Accurso, FJ; Ajayi, T; Barth, J; Branstrom, A; Bronsveld, I; De Boeck, K; Elborn, JS; Elfring, GL; Fajac, I; Kerem, E; Knoop, C; Konstan, MW; Malfroot, A; McColley, SA; Melotti, P; Peltz, SW; Quattrucci, S; Rietschel, E; Rosenbluth, DB; Rowe, SM; Sermet-Gaudelus, I; Spiegel, RJ; Walker, PA; Welch, EM; Wilschanski, M; Zeitlin, PL1

Reviews

1 review(s) available for chlorine and ptc 124

ArticleYear
Pharmacological treatment of the basic defect in cystic fibrosis.
    Cell biology international, 2014, Volume: 38, Issue:11

    Topics: Chlorides; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Humans; Mutation; Nitric Oxide; Oxadiazoles; S-Nitrosoglutathione

2014

Trials

2 trial(s) available for chlorine and ptc 124

ArticleYear
Effectiveness of PTC124 treatment of cystic fibrosis caused by nonsense mutations: a prospective phase II trial.
    Lancet (London, England), 2008, Aug-30, Volume: 372, Issue:9640

    Topics: Adolescent; Adult; Chlorides; Codon, Nonsense; Codon, Terminator; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Female; Humans; Male; Middle Aged; Oxadiazoles; Treatment Outcome

2008
Ataluren for the treatment of nonsense-mutation cystic fibrosis: a randomised, double-blind, placebo-controlled phase 3 trial.
    The Lancet. Respiratory medicine, 2014, Volume: 2, Issue:7

    Topics: Acute Kidney Injury; Adolescent; Adult; Anti-Bacterial Agents; Child; Chlorides; Codon, Nonsense; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Disease Progression; Double-Blind Method; Female; Forced Expiratory Volume; Humans; Male; Middle Aged; Oxadiazoles; Sweat; Tobramycin; Young Adult

2014

Other Studies

1 other study(ies) available for chlorine and ptc 124

ArticleYear
Nonsense-mediated mRNA decay and cystic fibrosis.
    Methods in molecular biology (Clifton, N.J.), 2011, Volume: 741

    Topics: Alleles; Animals; Blotting, Western; Cell Line, Tumor; Chlorides; Codon, Nonsense; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Genetic Techniques; Gentamicins; Humans; Nasal Mucosa; Oxadiazoles; Plasmids; RNA Helicases; RNA-Binding Proteins; RNA, Messenger; Trans-Activators; Transcription Factors; Transfection

2011
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