chlorine and ptc 124
chlorine has been researched along with ptc 124 in 4 studies
Research
Studies (4)
Timeframe | Studies, this research(%) | All Research% |
---|---|---|
pre-1990 | 0 (0.00) | 18.7374 |
1990's | 0 (0.00) | 18.2507 |
2000's | 1 (25.00) | 29.6817 |
2010's | 3 (75.00) | 24.3611 |
2020's | 0 (0.00) | 2.80 |
Authors
Authors | Studies |
---|---|
Armoni, S; Aviram, M; Blau, H; Cohen, M; Elfring, GL; Hirawat, S; Kerem, B; Kerem, E; Miller, LL; Nissim-Rafinia, M; Northcutt, VJ; Rivlin, J; Shoseyov, D; Wilschanski, M; Yaakov, Y | 1 |
Kerem, B; Linde, L | 1 |
Roomans, GM | 1 |
Accurso, FJ; Ajayi, T; Barth, J; Branstrom, A; Bronsveld, I; De Boeck, K; Elborn, JS; Elfring, GL; Fajac, I; Kerem, E; Knoop, C; Konstan, MW; Malfroot, A; McColley, SA; Melotti, P; Peltz, SW; Quattrucci, S; Rietschel, E; Rosenbluth, DB; Rowe, SM; Sermet-Gaudelus, I; Spiegel, RJ; Walker, PA; Welch, EM; Wilschanski, M; Zeitlin, PL | 1 |
Reviews
1 review(s) available for chlorine and ptc 124
Article | Year |
---|---|
Pharmacological treatment of the basic defect in cystic fibrosis.
Topics: Chlorides; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Humans; Mutation; Nitric Oxide; Oxadiazoles; S-Nitrosoglutathione | 2014 |
Trials
2 trial(s) available for chlorine and ptc 124
Article | Year |
---|---|
Effectiveness of PTC124 treatment of cystic fibrosis caused by nonsense mutations: a prospective phase II trial.
Topics: Adolescent; Adult; Chlorides; Codon, Nonsense; Codon, Terminator; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Female; Humans; Male; Middle Aged; Oxadiazoles; Treatment Outcome | 2008 |
Ataluren for the treatment of nonsense-mutation cystic fibrosis: a randomised, double-blind, placebo-controlled phase 3 trial.
Topics: Acute Kidney Injury; Adolescent; Adult; Anti-Bacterial Agents; Child; Chlorides; Codon, Nonsense; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Disease Progression; Double-Blind Method; Female; Forced Expiratory Volume; Humans; Male; Middle Aged; Oxadiazoles; Sweat; Tobramycin; Young Adult | 2014 |
Other Studies
1 other study(ies) available for chlorine and ptc 124
Article | Year |
---|---|
Nonsense-mediated mRNA decay and cystic fibrosis.
Topics: Alleles; Animals; Blotting, Western; Cell Line, Tumor; Chlorides; Codon, Nonsense; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Genetic Techniques; Gentamicins; Humans; Nasal Mucosa; Oxadiazoles; Plasmids; RNA Helicases; RNA-Binding Proteins; RNA, Messenger; Trans-Activators; Transcription Factors; Transfection | 2011 |