alpha-aminopyridine has been researched along with ptc 124 in 8 studies
Timeframe | Studies, this research(%) | All Research% |
---|---|---|
pre-1990 | 0 (0.00) | 18.7374 |
1990's | 0 (0.00) | 18.2507 |
2000's | 1 (12.50) | 29.6817 |
2010's | 6 (75.00) | 24.3611 |
2020's | 1 (12.50) | 2.80 |
Authors | Studies |
---|---|
Retsch-Bogart, GZ | 1 |
Bertoncini, E; Colomb-Lippa, D | 1 |
Durieu, I; Durupt, S; Nove Josserand, R | 1 |
Doe, SJ; Lane, MA | 1 |
Carlier, J; Kupchick, T; Larder, A; McCarty, J; Powers, M; Thomas, J; Virant-Young, D; Woiderski, S | 1 |
Quon, BS; Rowe, SM | 1 |
Crawford, KJ; Downey, DG | 1 |
Eintracht, J; Forsythe, E; May-Simera, H; Moosajee, M | 1 |
5 review(s) available for alpha-aminopyridine and ptc 124
Article | Year |
---|---|
Update on new pulmonary therapies.
Topics: Aminophenols; Aminopyridines; Anti-Infective Agents; Anti-Inflammatory Agents; Benzodioxoles; Biomarkers; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Genetic Markers; Genetic Therapy; Humans; Mutation; Oxadiazoles; Quinolones; Respiratory System Agents; Saline Solution, Hypertonic | 2009 |
[Therapeutic update in cystic fibrosis].
Topics: Aminophenols; Aminopyridines; Benzodioxoles; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Humans; Mutation; Oxadiazoles; Quinolones | 2014 |
Cystic Fibrosis: A Novel Pharmacologic Approach to Cystic Fibrosis Transmembrane Regulator Modulation Therapy.
Topics: Aminophenols; Aminopyridines; Benzodioxoles; Chloride Channel Agonists; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; DNA; DNA Mutational Analysis; Humans; Mutation; Oxadiazoles; Quinolones | 2015 |
New and emerging targeted therapies for cystic fibrosis.
Topics: Aminophenols; Aminopyridines; Benzodioxoles; Clinical Trials as Topic; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Drug Discovery; Drug Therapy, Combination; Forced Expiratory Volume; Forecasting; Genetic Therapy; Homozygote; Humans; Molecular Targeted Therapy; Mutation; Oxadiazoles; Phosphodiesterase 5 Inhibitors; Practice Guidelines as Topic; Precision Medicine; Quinolones | 2016 |
Theratyping in cystic fibrosis.
Topics: Aminophenols; Aminopyridines; Benzodioxoles; Chloride Channel Agonists; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Drug Combinations; Gene Editing; Genetic Therapy; Genotype; Humans; Indoles; Mutation; Organoids; Oxadiazoles; Precision Medicine; Quinolones | 2018 |
3 other study(ies) available for alpha-aminopyridine and ptc 124
Article | Year |
---|---|
Pulmonology: CFTR modulators for cystic fibrosis.
Topics: Aminophenols; Aminopyridines; Benzodioxoles; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Humans; Lung; Mutation; Oxadiazoles; Quinolones | 2013 |
A new era in the treatment of cystic fibrosis.
Topics: Aminophenols; Aminopyridines; Benzodioxoles; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Genetic Therapy; Humans; Molecular Targeted Therapy; Mutation; Oxadiazoles; Quinolones | 2014 |
Translational readthrough of ciliopathy genes BBS2 and ALMS1 restores protein, ciliogenesis and function in patient fibroblasts.
Topics: Adolescent; Adult; Alstrom Syndrome; Aminopyridines; Bardet-Biedl Syndrome; Cell Cycle Proteins; Cells, Cultured; Codon, Nonsense; Fibroblasts; Humans; Male; Oxadiazoles; Proteins; Receptors, Somatostatin; Tumor Suppressor Proteins | 2021 |