Page last updated: 2024-08-21

alpha-aminopyridine and ptc 124

alpha-aminopyridine has been researched along with ptc 124 in 8 studies

Research

Studies (8)

TimeframeStudies, this research(%)All Research%
pre-19900 (0.00)18.7374
1990's0 (0.00)18.2507
2000's1 (12.50)29.6817
2010's6 (75.00)24.3611
2020's1 (12.50)2.80

Authors

AuthorsStudies
Retsch-Bogart, GZ1
Bertoncini, E; Colomb-Lippa, D1
Durieu, I; Durupt, S; Nove Josserand, R1
Doe, SJ; Lane, MA1
Carlier, J; Kupchick, T; Larder, A; McCarty, J; Powers, M; Thomas, J; Virant-Young, D; Woiderski, S1
Quon, BS; Rowe, SM1
Crawford, KJ; Downey, DG1
Eintracht, J; Forsythe, E; May-Simera, H; Moosajee, M1

Reviews

5 review(s) available for alpha-aminopyridine and ptc 124

ArticleYear
Update on new pulmonary therapies.
    Current opinion in pulmonary medicine, 2009, Volume: 15, Issue:6

    Topics: Aminophenols; Aminopyridines; Anti-Infective Agents; Anti-Inflammatory Agents; Benzodioxoles; Biomarkers; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Genetic Markers; Genetic Therapy; Humans; Mutation; Oxadiazoles; Quinolones; Respiratory System Agents; Saline Solution, Hypertonic

2009
[Therapeutic update in cystic fibrosis].
    La Revue de medecine interne, 2014, Volume: 35, Issue:6

    Topics: Aminophenols; Aminopyridines; Benzodioxoles; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Humans; Mutation; Oxadiazoles; Quinolones

2014
Cystic Fibrosis: A Novel Pharmacologic Approach to Cystic Fibrosis Transmembrane Regulator Modulation Therapy.
    The Journal of the American Osteopathic Association, 2015, Volume: 115, Issue:9

    Topics: Aminophenols; Aminopyridines; Benzodioxoles; Chloride Channel Agonists; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; DNA; DNA Mutational Analysis; Humans; Mutation; Oxadiazoles; Quinolones

2015
New and emerging targeted therapies for cystic fibrosis.
    BMJ (Clinical research ed.), 2016, Mar-30, Volume: 352

    Topics: Aminophenols; Aminopyridines; Benzodioxoles; Clinical Trials as Topic; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Drug Discovery; Drug Therapy, Combination; Forced Expiratory Volume; Forecasting; Genetic Therapy; Homozygote; Humans; Molecular Targeted Therapy; Mutation; Oxadiazoles; Phosphodiesterase 5 Inhibitors; Practice Guidelines as Topic; Precision Medicine; Quinolones

2016
Theratyping in cystic fibrosis.
    Current opinion in pulmonary medicine, 2018, Volume: 24, Issue:6

    Topics: Aminophenols; Aminopyridines; Benzodioxoles; Chloride Channel Agonists; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Drug Combinations; Gene Editing; Genetic Therapy; Genotype; Humans; Indoles; Mutation; Organoids; Oxadiazoles; Precision Medicine; Quinolones

2018

Other Studies

3 other study(ies) available for alpha-aminopyridine and ptc 124

ArticleYear
Pulmonology: CFTR modulators for cystic fibrosis.
    JAAPA : official journal of the American Academy of Physician Assistants, 2013, Volume: 26, Issue:2

    Topics: Aminophenols; Aminopyridines; Benzodioxoles; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Humans; Lung; Mutation; Oxadiazoles; Quinolones

2013
A new era in the treatment of cystic fibrosis.
    Clinical medicine (London, England), 2014, Volume: 14, Issue:1

    Topics: Aminophenols; Aminopyridines; Benzodioxoles; Cystic Fibrosis; Cystic Fibrosis Transmembrane Conductance Regulator; Genetic Therapy; Humans; Molecular Targeted Therapy; Mutation; Oxadiazoles; Quinolones

2014
Translational readthrough of ciliopathy genes BBS2 and ALMS1 restores protein, ciliogenesis and function in patient fibroblasts.
    EBioMedicine, 2021, Volume: 70

    Topics: Adolescent; Adult; Alstrom Syndrome; Aminopyridines; Bardet-Biedl Syndrome; Cell Cycle Proteins; Cells, Cultured; Codon, Nonsense; Fibroblasts; Humans; Male; Oxadiazoles; Proteins; Receptors, Somatostatin; Tumor Suppressor Proteins

2021